CN112424347A - 治疗酸性鞘磷脂酶缺乏症的药物组合物 - Google Patents
治疗酸性鞘磷脂酶缺乏症的药物组合物 Download PDFInfo
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- CN112424347A CN112424347A CN201980048133.7A CN201980048133A CN112424347A CN 112424347 A CN112424347 A CN 112424347A CN 201980048133 A CN201980048133 A CN 201980048133A CN 112424347 A CN112424347 A CN 112424347A
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| TW202403043A (zh) | 2022-03-18 | 2024-01-16 | 美商健臻公司 | 重組人類酸性鞘磷脂酶醫藥組合物及方法 |
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| CN101431960A (zh) * | 2006-01-20 | 2009-05-13 | 建新公司 | 用于溶酶体贮积症的脑室内酶输注系统 |
| WO2010148337A1 (en) * | 2009-06-18 | 2010-12-23 | Wyeth Llc | Lyophilized formulations for small modular immunopharmaceuticals |
| CN103260637A (zh) * | 2010-06-25 | 2013-08-21 | 夏尔人类遗传性治疗公司 | 乙酰肝素n-硫酸酯酶cns递送的方法和组合物 |
| WO2017149199A1 (en) * | 2016-02-29 | 2017-09-08 | Faron Pharmaceuticals Oy | A lyophilised pharmaceutical formulation and its use |
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| US5773278A (en) | 1991-05-03 | 1998-06-30 | Mount Sinai Medical Center | Acid sphingomyelinase gene |
| ES2351786T3 (es) * | 2001-11-13 | 2011-02-10 | Genentech, Inc. | Formulaciones con ligando apo2/trail y usos de las mismas. |
| WO2004112826A1 (en) | 2003-06-20 | 2004-12-29 | Ares Trading Sa | Freeze-dried fsh / lh formulations |
| JP2007514661A (ja) * | 2003-11-25 | 2007-06-07 | マウント シナイ スクール オブ メディスン オブ ニューヨーク ユニバーシティー | ニーマンピック病のシャペロンに基づく治療方法 |
| HRP20120994T1 (hr) | 2006-02-07 | 2012-12-31 | Shire Human Genetic Therapies, Inc. | Stabilizirana smjesa glukocerebrozidaze |
| MX2008011842A (es) * | 2006-03-13 | 2008-10-02 | Encysive Pharmaceuticals Inc | Procedimientos y composiciones para el tratamiento de insuficiencia cardiaca diastolica. |
| CN102943106A (zh) * | 2006-03-13 | 2013-02-27 | 珀金埃尔默健康科学股份有限公司 | 用于质谱法检测的底物和内标 |
| SI3998078T1 (sl) | 2009-08-28 | 2026-02-27 | Genzyme Corporation | Encimsko nadomestno zdravljenje z naraščajočim odmerkom za zdravljenje pomanjkanja kisle sfingomielinaze |
| WO2012134240A2 (ko) * | 2011-03-31 | 2012-10-04 | (주)메디톡스 | 보툴리눔 독소의 동결건조제제 |
| JP6480154B2 (ja) | 2014-11-06 | 2019-03-06 | 持田製薬株式会社 | エタネルセプトの凍結乾燥製剤 |
| KR20250025051A (ko) * | 2017-08-24 | 2025-02-20 | 사노피 | 산성 스핑고미엘린분해효소 결핍증 환자에서의 비정상적 골병태의 치료 |
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| CN101431960A (zh) * | 2006-01-20 | 2009-05-13 | 建新公司 | 用于溶酶体贮积症的脑室内酶输注系统 |
| WO2010148337A1 (en) * | 2009-06-18 | 2010-12-23 | Wyeth Llc | Lyophilized formulations for small modular immunopharmaceuticals |
| CN103260637A (zh) * | 2010-06-25 | 2013-08-21 | 夏尔人类遗传性治疗公司 | 乙酰肝素n-硫酸酯酶cns递送的方法和组合物 |
| WO2017149199A1 (en) * | 2016-02-29 | 2017-09-08 | Faron Pharmaceuticals Oy | A lyophilised pharmaceutical formulation and its use |
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| EP3802805A1 (en) | 2021-04-14 |
| UY38238A (es) | 2019-12-31 |
| WO2019227029A1 (en) | 2019-11-28 |
| PY1939780A (es) | 2019-12-04 |
| JP2021525083A (ja) | 2021-09-24 |
| IL278964A (en) | 2021-01-31 |
| AU2025205577A1 (en) | 2025-08-07 |
| US20210145941A1 (en) | 2021-05-20 |
| MX2025002733A (es) | 2025-04-02 |
| JP7497300B2 (ja) | 2024-06-10 |
| JP7832245B2 (ja) | 2026-03-17 |
| CO2020014399A2 (es) | 2020-12-10 |
| CA3101688A1 (en) | 2019-11-28 |
| AU2019275109C1 (en) | 2025-11-13 |
| MX2020012700A (es) | 2021-04-28 |
| BR112020023829A2 (pt) | 2021-05-11 |
| JP2024069459A (ja) | 2024-05-21 |
| AU2019275109B2 (en) | 2025-04-17 |
| AU2019275109A1 (en) | 2021-01-21 |
| SG11202011488WA (en) | 2020-12-30 |
| KR20210015903A (ko) | 2021-02-10 |
| KR102852946B1 (ko) | 2025-09-02 |
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