JP2021500864A - Ｔｔｒ遺伝子編集およびａｔｔｒアミロイドーシスの治療用の組成物および方法 - Google Patents

Ｔｔｒ遺伝子編集およびａｔｔｒアミロイドーシスの治療用の組成物および方法 Download PDF

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JP2021500864A
JP2021500864A JP2020517500A JP2020517500A JP2021500864A JP 2021500864 A JP2021500864 A JP 2021500864A JP 2020517500 A JP2020517500 A JP 2020517500A JP 2020517500 A JP2020517500 A JP 2020517500A JP 2021500864 A JP2021500864 A JP 2021500864A
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composition
sequence selected
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composition according
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マヘンドラ プラカシュ カンジョリア，アルティ
マヘンドラ プラカシュ カンジョリア，アルティ
オダテ，ショブ
リン サイツァー，ジェシカ
リン サイツァー，ジェシカ
マイケル レスカーボ，レイナルド
マイケル レスカーボ，レイナルド
ストラップス，ウォルター
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インテリア セラピューティクス，インコーポレイテッド
インテリア セラピューティクス，インコーポレイテッド
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Publication of JP2021500864A publication Critical patent/JP2021500864A/ja
Publication of JP2021500864A5 publication Critical patent/JP2021500864A5/ja
Priority to JP2022194564A priority Critical patent/JP7707140B2/ja
Priority to JP2025112164A priority patent/JP2025163016A/ja
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JP2020517500A 2017-09-29 2018-09-28 Ｔｔｒ遺伝子編集およびａｔｔｒアミロイドーシスの治療用の組成物および方法 Pending JP2021500864A (ja)

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Application Number Priority Date Filing Date Title
JP2022194564A JP7707140B2 (ja) 2017-09-29 2022-12-06 Ｔｔｒ遺伝子編集およびａｔｔｒアミロイドーシスの治療用の組成物および方法
JP2025112164A JP2025163016A (ja) 2017-09-29 2025-07-02 Ｔｔｒ遺伝子編集およびａｔｔｒアミロイドーシスの治療用の組成物および方法

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US201762566236P 2017-09-29 2017-09-29
US62/566,236 2017-09-29
US201862671902P 2018-05-15 2018-05-15
US62/671,902 2018-05-15
PCT/US2018/053382 WO2019067872A1 (en) 2017-09-29 2018-09-28 COMPOSITIONS AND METHODS FOR EDITING THE TTR GENE AND TREATING AMYLOID DOSE ATTR

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JP2022194564A Active JP7707140B2 (ja) 2017-09-29 2022-12-06 Ｔｔｒ遺伝子編集およびａｔｔｒアミロイドーシスの治療用の組成物および方法
JP2025112164A Pending JP2025163016A (ja) 2017-09-29 2025-07-02 Ｔｔｒ遺伝子編集およびａｔｔｒアミロイドーシスの治療用の組成物および方法

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JP2025112164A Pending JP2025163016A (ja) 2017-09-29 2025-07-02 Ｔｔｒ遺伝子編集およびａｔｔｒアミロイドーシスの治療用の組成物および方法

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US (4) US20200248180A1 (https=)
EP (1) EP3688161A1 (https=)
JP (3) JP2021500864A (https=)
KR (1) KR20200058509A (https=)
CN (2) CN118530993A (https=)
AU (2) AU2018338787C1 (https=)
BR (1) BR112020005287A2 (https=)
CA (1) CA3077251A1 (https=)
CO (1) CO2020005116A2 (https=)
IL (3) IL311170B1 (https=)
MX (2) MX2020003608A (https=)
MY (1) MY203849A (https=)
PH (1) PH12020550364A1 (https=)
SG (1) SG11202002565YA (https=)
TW (1) TWI904069B (https=)
WO (1) WO2019067872A1 (https=)

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