JP2020534788A - アデノ随伴ウイルスカプシド変異体及びその使用方法 - Google Patents

アデノ随伴ウイルスカプシド変異体及びその使用方法 Download PDF

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JP2020534788A
JP2020534788A JP2019562303A JP2019562303A JP2020534788A JP 2020534788 A JP2020534788 A JP 2020534788A JP 2019562303 A JP2019562303 A JP 2019562303A JP 2019562303 A JP2019562303 A JP 2019562303A JP 2020534788 A JP2020534788 A JP 2020534788A
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aav
amino acids
virion
raav
fold
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デビッド ブイ． シャッファー
デビッド ブイ． シャッファー
デビッド スティーブン オハラ
デビッド スティーブン オハラ
フィリップ エー． ロメロ
フィリップ エー． ロメロ
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University of California
University of California Los Angeles UCLA
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University of California San Diego UCSD
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    • C12N2750/00011—Details
    • C12N2750/14011—Parvoviridae
    • C12N2750/14111—Dependovirus, e.g. adenoassociated viruses
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    • C12N2800/00—Nucleic acids vectors
    • C12N2800/30—Vector systems comprising sequences for excision in presence of a recombinase, e.g. loxP or FRT

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JP2019562303A 2017-08-28 2018-08-22 アデノ随伴ウイルスカプシド変異体及びその使用方法 Withdrawn JP2020534788A (ja)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US201762551133P 2017-08-28 2017-08-28
US62/551,133 2017-08-28
PCT/US2018/047561 WO2019046069A1 (en) 2017-08-28 2018-08-22 ADENO-ASSOCIATED VIRUS CAPSID VARIANTS AND METHODS OF USE

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JP2020534788A true JP2020534788A (ja) 2020-12-03
JP2020534788A5 JP2020534788A5 (https=) 2021-09-30

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US (1) US11680249B2 (https=)
EP (1) EP3676373A4 (https=)
JP (1) JP2020534788A (https=)
KR (1) KR20200039617A (https=)
CN (1) CN110709511A (https=)
AU (1) AU2018324477A1 (https=)
BR (1) BR112020003571A2 (https=)
CA (1) CA3059995A1 (https=)
MX (1) MX2020001997A (https=)
WO (1) WO2019046069A1 (https=)

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