JP2020520643A5 - - Google Patents
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- Publication number
- JP2020520643A5 JP2020520643A5 JP2019563548A JP2019563548A JP2020520643A5 JP 2020520643 A5 JP2020520643 A5 JP 2020520643A5 JP 2019563548 A JP2019563548 A JP 2019563548A JP 2019563548 A JP2019563548 A JP 2019563548A JP 2020520643 A5 JP2020520643 A5 JP 2020520643A5
- Authority
- JP
- Japan
- Prior art keywords
- item
- expression cassette
- factor
- transgene
- cassette according
- Prior art date
- Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
- Granted
Links
Priority Applications (2)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| JP2022152422A JP2022173348A (ja) | 2017-05-19 | 2022-09-26 | 高活性制御エレメント |
| JP2023211093A JP2024015408A (ja) | 2017-05-19 | 2023-12-14 | 高活性制御エレメント |
Applications Claiming Priority (3)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| US201762508968P | 2017-05-19 | 2017-05-19 | |
| US62/508,968 | 2017-05-19 | ||
| PCT/US2018/033515 WO2018213786A1 (en) | 2017-05-19 | 2018-05-18 | High activity regulatory elements |
Related Child Applications (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2022152422A Division JP2022173348A (ja) | 2017-05-19 | 2022-09-26 | 高活性制御エレメント |
Publications (3)
| Publication Number | Publication Date |
|---|---|
| JP2020520643A JP2020520643A (ja) | 2020-07-16 |
| JP2020520643A5 true JP2020520643A5 (OSRAM) | 2021-07-26 |
| JP7315475B2 JP7315475B2 (ja) | 2023-07-26 |
Family
ID=64274721
Family Applications (3)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2019563548A Active JP7315475B2 (ja) | 2017-05-19 | 2018-05-18 | 高活性制御エレメント |
| JP2022152422A Pending JP2022173348A (ja) | 2017-05-19 | 2022-09-26 | 高活性制御エレメント |
| JP2023211093A Pending JP2024015408A (ja) | 2017-05-19 | 2023-12-14 | 高活性制御エレメント |
Family Applications After (2)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2022152422A Pending JP2022173348A (ja) | 2017-05-19 | 2022-09-26 | 高活性制御エレメント |
| JP2023211093A Pending JP2024015408A (ja) | 2017-05-19 | 2023-12-14 | 高活性制御エレメント |
Country Status (11)
| Country | Link |
|---|---|
| US (2) | US12104175B2 (OSRAM) |
| EP (1) | EP3624858A4 (OSRAM) |
| JP (3) | JP7315475B2 (OSRAM) |
| KR (2) | KR102636351B1 (OSRAM) |
| CN (2) | CN118956965A (OSRAM) |
| AU (1) | AU2018269050A1 (OSRAM) |
| BR (1) | BR112019024222A2 (OSRAM) |
| CA (1) | CA3063464A1 (OSRAM) |
| MA (1) | MA49153A (OSRAM) |
| TW (1) | TWI811219B (OSRAM) |
| WO (1) | WO2018213786A1 (OSRAM) |
Families Citing this family (16)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| GB201420139D0 (en) | 2014-11-12 | 2014-12-24 | Ucl Business Plc | Factor IX gene therapy |
| CN118956965A (zh) | 2017-05-19 | 2024-11-15 | 编码治疗公司 | 高活性调控元件 |
| JP7401432B2 (ja) | 2017-12-01 | 2023-12-19 | エンコーデッド セラピューティクス， インコーポレイテッド | 操作されたｄｎａ結合タンパク質 |
| GB201813528D0 (en) | 2018-08-20 | 2018-10-03 | Ucl Business Plc | Factor IX encoding nucleotides |
| US10842885B2 (en) | 2018-08-20 | 2020-11-24 | Ucl Business Ltd | Factor IX encoding nucleotides |
| EP3914719A4 (en) * | 2019-01-24 | 2023-04-05 | Valorisation-HSJ, Limited Partnership | Cell-specific transcriptional regulatory sequences and uses thereof |
| WO2020210633A1 (en) * | 2019-04-12 | 2020-10-15 | Encoded Therapeutics, Inc. | Compositions and methods for administration of therapeutics |
| WO2020243651A1 (en) | 2019-05-29 | 2020-12-03 | Encoded Therapeutics, Inc. | Compositions and methods for selective gene regulation |
| CA3147875A1 (en) | 2019-07-19 | 2021-01-28 | Flagship Pioneering Innovations Vi, Llc | Recombinase compositions and methods of use |
| CN113088519B (zh) * | 2019-12-23 | 2024-02-02 | 苏州华毅乐健生物科技有限公司 | 一种分离的核酸分子及其应用 |
| BR112022015921A2 (pt) * | 2020-02-14 | 2022-10-04 | Ultragenyx Pharmaceutical Inc | Terapia gênica para tratar o transtorno de deficiência de cdkl5 |
| EP4150051A4 (en) * | 2020-04-27 | 2025-05-21 | The Trustees of The University of Pennsylvania | COMPOSITIONS FOR THE TREATMENT OF CDKL5 DEFICIENCY DISORDER (CDD) |
| CA3224482A1 (en) * | 2021-08-05 | 2023-02-09 | Brian Kaspar | Adeno-associated virus particles and methods of use thereof |
| EP4602061A1 (en) * | 2022-10-11 | 2025-08-20 | MeiraGTx UK II Limited | Atp7b gene therapy |
| CN117925624B (zh) * | 2024-03-22 | 2024-05-31 | 上海凌医生物科技有限公司 | 一种金属响应调控元件 |
| CN117947035A (zh) * | 2024-03-25 | 2024-04-30 | 上海凌医生物科技有限公司 | 一种增强基因表达的启动子 |
Family Cites Families (13)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| DE60034478T2 (de) * | 1999-11-16 | 2008-01-10 | Genzyme Corp., Cambridge | Vektoren und transgene mit regulatorischen elementen zur genverabreichung in leber |
| US6436703B1 (en) * | 2000-03-31 | 2002-08-20 | Hyseq, Inc. | Nucleic acids and polypeptides |
| EP1783645A1 (en) * | 2005-11-08 | 2007-05-09 | Actigenics | Methods for the identification of microRNA and their applications in research and human health |
| US20090018031A1 (en) * | 2006-12-07 | 2009-01-15 | Switchgear Genomics | Transcriptional regulatory elements of biological pathways tools, and methods |
| GB0911870D0 (en) | 2009-07-08 | 2009-08-19 | Ucl Business Plc | Optimised coding sequence and promoter |
| WO2013033627A2 (en) * | 2011-09-01 | 2013-03-07 | The Regents Of The University Of California | Diagnosis and treatment of arthritis using epigenetics |
| KR102057540B1 (ko) * | 2012-02-17 | 2019-12-19 | 더 칠드런스 호스피탈 오브 필라델피아 | 세포, 기관 및 조직으로의 유전자 전이를 위한 ａａｖ 벡터 조성물 및 방법 |
| US11065311B2 (en) | 2012-10-25 | 2021-07-20 | Denovo Biopharma Llc | Retroviral vector with mini-promoter cassette |
| JP6865167B2 (ja) * | 2014-12-17 | 2021-04-28 | フンダシオン パラ ラ インベスティガシオン メディカ アプリカダ | ウィルソン病の処置に使用するための核酸構築物及び遺伝子治療ベクター |
| TWI707951B (zh) * | 2015-04-08 | 2020-10-21 | 美商健臻公司 | 過大腺相關載體之製造 |
| CN118956965A (zh) | 2017-05-19 | 2024-11-15 | 编码治疗公司 | 高活性调控元件 |
| JP7401432B2 (ja) * | 2017-12-01 | 2023-12-19 | エンコーデッド セラピューティクス， インコーポレイテッド | 操作されたｄｎａ結合タンパク質 |
| MA55087A (fr) * | 2019-02-28 | 2022-01-05 | Encoded Therapeutics Inc | Compositions et procédés de traitement de laminopathies |
-
2018
- 2018-05-18 CN CN202411101805.5A patent/CN118956965A/zh active Pending
- 2018-05-18 CA CA3063464A patent/CA3063464A1/en active Pending
- 2018-05-18 CN CN201880048355.4A patent/CN110944674B/zh not_active Expired - Fee Related
- 2018-05-18 EP EP18803184.3A patent/EP3624858A4/en not_active Withdrawn
- 2018-05-18 JP JP2019563548A patent/JP7315475B2/ja active Active
- 2018-05-18 KR KR1020197037368A patent/KR102636351B1/ko active Active
- 2018-05-18 MA MA049153A patent/MA49153A/fr unknown
- 2018-05-18 BR BR112019024222-8A patent/BR112019024222A2/pt not_active Application Discontinuation
- 2018-05-18 WO PCT/US2018/033515 patent/WO2018213786A1/en not_active Ceased
- 2018-05-18 KR KR1020247004550A patent/KR20240024326A/ko not_active Ceased
- 2018-05-18 TW TW107117128A patent/TWI811219B/zh active
- 2018-05-18 AU AU2018269050A patent/AU2018269050A1/en not_active Abandoned
-
2019
- 2019-11-18 US US16/687,426 patent/US12104175B2/en active Active
-
2022
- 2022-09-26 JP JP2022152422A patent/JP2022173348A/ja active Pending
-
2023
- 2023-12-14 JP JP2023211093A patent/JP2024015408A/ja active Pending
-
2024
- 2024-08-01 US US18/792,310 patent/US20240376441A1/en not_active Abandoned
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