JP2019537576A5 - - Google Patents
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- Publication number
- JP2019537576A5 JP2019537576A5 JP2019522377A JP2019522377A JP2019537576A5 JP 2019537576 A5 JP2019537576 A5 JP 2019537576A5 JP 2019522377 A JP2019522377 A JP 2019522377A JP 2019522377 A JP2019522377 A JP 2019522377A JP 2019537576 A5 JP2019537576 A5 JP 2019537576A5
- Authority
- JP
- Japan
- Prior art keywords
- aav
- particle according
- aav particle
- disease
- particles
- Prior art date
- Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
- Pending
Links
Priority Applications (1)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| JP2022169285A JP2023002721A (ja) | 2016-11-04 | 2022-10-21 | 神経変性疾患を処置するための遺伝子移入用組成物、遺伝子導入法、及び遺伝子導入の使用 |
Applications Claiming Priority (3)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| US201662418033P | 2016-11-04 | 2016-11-04 | |
| US62/418,033 | 2016-11-04 | ||
| PCT/US2017/059986 WO2018085688A1 (en) | 2016-11-04 | 2017-11-03 | Gene transfer compositions, methods and uses for treating neurodegenerative diseases |
Related Child Applications (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2022169285A Division JP2023002721A (ja) | 2016-11-04 | 2022-10-21 | 神経変性疾患を処置するための遺伝子移入用組成物、遺伝子導入法、及び遺伝子導入の使用 |
Publications (2)
| Publication Number | Publication Date |
|---|---|
| JP2019537576A JP2019537576A (ja) | 2019-12-26 |
| JP2019537576A5 true JP2019537576A5 (enExample) | 2020-12-03 |
Family
ID=62075988
Family Applications (2)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2019522377A Pending JP2019537576A (ja) | 2016-11-04 | 2017-11-03 | 神経変性疾患を処置するための遺伝子移入用組成物、遺伝子導入法、及び遺伝子導入の使用 |
| JP2022169285A Pending JP2023002721A (ja) | 2016-11-04 | 2022-10-21 | 神経変性疾患を処置するための遺伝子移入用組成物、遺伝子導入法、及び遺伝子導入の使用 |
Family Applications After (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2022169285A Pending JP2023002721A (ja) | 2016-11-04 | 2022-10-21 | 神経変性疾患を処置するための遺伝子移入用組成物、遺伝子導入法、及び遺伝子導入の使用 |
Country Status (9)
| Country | Link |
|---|---|
| US (1) | US20190269797A1 (enExample) |
| EP (1) | EP3534892A4 (enExample) |
| JP (2) | JP2019537576A (enExample) |
| CN (1) | CN110198712A (enExample) |
| AU (1) | AU2017355502B2 (enExample) |
| BR (1) | BR112019009074A2 (enExample) |
| CA (1) | CA3041548A1 (enExample) |
| MX (1) | MX2019005266A (enExample) |
| WO (1) | WO2018085688A1 (enExample) |
Families Citing this family (11)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| US9818239B2 (en) | 2015-08-20 | 2017-11-14 | Zendrive, Inc. | Method for smartphone-based accident detection |
| ES3065816T3 (en) | 2017-06-07 | 2026-05-08 | Regeneron Pharma | Compositions and methods for internalizing enzymes |
| EP3698340A4 (en) | 2017-10-20 | 2021-07-14 | Zendrive, Inc. | PROCEDURE AND SYSTEM FOR VEHICLE ASSOCIATED COMMUNICATION |
| CN112040985A (zh) | 2018-02-07 | 2020-12-04 | 瑞泽恩制药公司 | 用于递送治疗性蛋白质的方法和组合物 |
| BR112020023145A2 (pt) | 2018-05-17 | 2021-02-02 | Regeneron Pharmaceuticals, Inc. | anticorpo anti-cd63 ou fragmento de ligação ao antígeno do mesmo, molécula de ligação ao antígeno biespecífica, proteína terapêutica de múltiplos domínios, polinucleotídeo composição farmacêutica, e, composto |
| SG11202103102WA (en) | 2018-09-26 | 2021-04-29 | California Inst Of Techn | Adeno-associated virus compositions for targeted gene therapy |
| IL327339A (en) * | 2018-11-14 | 2026-05-01 | Regenxbio Inc | Gene therapy for neural ceroid lipofuscinosis |
| CN113891712A (zh) * | 2019-02-01 | 2022-01-04 | 星火治疗有限公司 | 用于晚期婴儿神经元蜡样脂褐质沉积症2型的aav载体治疗方法 |
| EP4042297A4 (en) | 2019-12-03 | 2023-11-22 | Zendrive, Inc. | METHOD AND SYSTEM FOR DETERMINING THE RISK OF A ROUTE |
| WO2021180118A1 (en) * | 2020-03-11 | 2021-09-16 | Shanghai Belief-Delivery Biomed Co., Ltd. | Novel use of aspirin compound in increasing nucleic acid expression |
| WO2025231406A1 (en) * | 2024-05-02 | 2025-11-06 | The Children's Hospital Of Philadelphia | Methods to increase transduction of ependyma cells in brain |
Family Cites Families (12)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| AU2003221745A1 (en) * | 2002-04-19 | 2003-11-03 | University Of Florida | rAAV VECTOR-BASED COMPOSITIONS AND METHODS FOR THE PREVENTION AND TREATMENT OF MAMMALIAN DISEASES |
| US20040258666A1 (en) * | 2003-05-01 | 2004-12-23 | Passini Marco A. | Gene therapy for neurometabolic disorders |
| KR20070004637A (ko) * | 2004-01-22 | 2007-01-09 | 가부시키가이샤 디나벡크 겐큐쇼 | 바이러스 벡터의 제조방법 |
| ES2700048T3 (es) * | 2006-02-08 | 2019-02-13 | Genzyme Corp | Terapia génica par la enfermedad de Niemann-Pick tipo A |
| PT3252161T (pt) * | 2007-06-06 | 2022-02-01 | Genzyme Corp | Terapia genética para doenças do armazenamento lisossomal |
| CA2832151C (en) * | 2011-03-31 | 2021-06-15 | University Of Iowa Research Foundation | Methods and compositions for treating brain diseases |
| PT3024498T (pt) * | 2013-07-22 | 2020-03-06 | Childrens Hospital Philadelphia | Variante aav e composições, métodos e usos para transferência genética em células, órgãos e tecidos |
| PT3024497T (pt) * | 2013-07-26 | 2021-08-23 | Univ Iowa Res Found | Métodos e composições para o tratamento de doenças cerebrais |
| WO2015060722A1 (en) * | 2013-10-24 | 2015-04-30 | Uniqure Ip B.V. | Aav-5 pseudotyped vector for gene therapy for neurological diseases |
| IL245703B (en) * | 2013-11-20 | 2022-07-01 | Univ Iowa Res Found | Methods and compositions for treating amyloid deposits |
| SG11201803218PA (en) * | 2015-10-23 | 2018-05-30 | Univ Iowa Res Found | Methods for treating neurodegenerative diseases using gene therapy to delay disease onset and progression while providing cognitive protection |
| BR112019023303A2 (pt) * | 2017-05-11 | 2020-06-16 | The Trustees Of The University Of Pennsylvania | Terapia de gene para lipofuscinoses ceroides neuronais |
-
2017
- 2017-11-03 AU AU2017355502A patent/AU2017355502B2/en not_active Ceased
- 2017-11-03 CN CN201780067919.4A patent/CN110198712A/zh active Pending
- 2017-11-03 MX MX2019005266A patent/MX2019005266A/es unknown
- 2017-11-03 US US16/344,298 patent/US20190269797A1/en active Pending
- 2017-11-03 WO PCT/US2017/059986 patent/WO2018085688A1/en not_active Ceased
- 2017-11-03 EP EP17867272.1A patent/EP3534892A4/en not_active Withdrawn
- 2017-11-03 BR BR112019009074-6A patent/BR112019009074A2/pt not_active IP Right Cessation
- 2017-11-03 JP JP2019522377A patent/JP2019537576A/ja active Pending
- 2017-11-03 CA CA3041548A patent/CA3041548A1/en active Pending
-
2022
- 2022-10-21 JP JP2022169285A patent/JP2023002721A/ja active Pending
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