JP2019535789A - Ｒｎａスプライシングを調節する方法 - Google Patents

Ｒｎａスプライシングを調節する方法 Download PDF

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JP2019535789A
JP2019535789A JP2019528527A JP2019528527A JP2019535789A JP 2019535789 A JP2019535789 A JP 2019535789A JP 2019528527 A JP2019528527 A JP 2019528527A JP 2019528527 A JP2019528527 A JP 2019528527A JP 2019535789 A JP2019535789 A JP 2019535789A
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alkyl
amino
alkoxy
hydroxy
heterocyclyl
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JP2019535789A5 (https=
Inventor
ブハッタチャリイヤ アヌラドハ
ブハッタチャリイヤ アヌラドハ
ダッカ アマル
ダッカ アマル
エッフェンバーガー カースティン
エッフェンバーガー カースティン
ガッベタ ビジャヤラクシュミ
ガッベタ ビジャヤラクシュミ
リ ウェンチェング
リ ウェンチェング
ナリシュキン ニコライ
ナリシュキン ニコライ
トロッタ クリストファー
トロッタ クリストファー
ウィエディンガー カリ
ウィエディンガー カリ
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PTC Therapeutics Inc
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PTC Therapeutics Inc
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Publication of JP2019535789A publication Critical patent/JP2019535789A/ja
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Priority to JP2022108509A priority Critical patent/JP2022153413A/ja
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JP2019528527A 2016-11-28 2017-11-27 Ｒｎａスプライシングを調節する方法 Pending JP2019535789A (ja)

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US201662426619P 2016-11-28 2016-11-28
US62/426,619 2016-11-28
PCT/US2017/063323 WO2018098446A1 (en) 2016-11-28 2017-11-27 Methods for modulating rna splicing

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EP (1) EP3544435A4 (https=)
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CN (1) CN110352007A (https=)
AU (1) AU2017363369A1 (https=)
CA (1) CA3043755A1 (https=)
EA (1) EA201991309A1 (https=)
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