EA201991309A1 - Способы модуляции сплайсинга рнк - Google Patents

Способы модуляции сплайсинга рнк

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Publication number
EA201991309A1
EA201991309A1 EA201991309A EA201991309A EA201991309A1 EA 201991309 A1 EA201991309 A1 EA 201991309A1 EA 201991309 A EA201991309 A EA 201991309A EA 201991309 A EA201991309 A EA 201991309A EA 201991309 A1 EA201991309 A1 EA 201991309A1
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Eurasian Patent Office
Prior art keywords
methods
rems
another aspect
gene
intronic
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EA201991309A
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English (en)
Russian (ru)
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  • Health & Medical Sciences (AREA)
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  • Crystallography & Structural Chemistry (AREA)
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EA201991309A 2016-11-28 2017-11-27 Способы модуляции сплайсинга рнк EA201991309A1 (ru)

Applications Claiming Priority (2)

Application Number Priority Date Filing Date Title
US201662426619P 2016-11-28 2016-11-28
PCT/US2017/063323 WO2018098446A1 (en) 2016-11-28 2017-11-27 Methods for modulating rna splicing

Publications (1)

Publication Number Publication Date
EA201991309A1 true EA201991309A1 (ru) 2019-11-29

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EA201991309A EA201991309A1 (ru) 2016-11-28 2017-11-27 Способы модуляции сплайсинга рнк

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US (2) US11702646B2 (https=)
EP (1) EP3544435A4 (https=)
JP (2) JP2019535789A (https=)
CN (1) CN110352007A (https=)
AU (1) AU2017363369A1 (https=)
CA (1) CA3043755A1 (https=)
EA (1) EA201991309A1 (https=)
MX (1) MX2019005588A (https=)
WO (1) WO2018098446A1 (https=)

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EP4249472A3 (en) 2015-05-30 2023-12-13 PTC Therapeutics, Inc. Methods for modulating rna splicing
EA201991309A1 (ru) 2016-11-28 2019-11-29 Способы модуляции сплайсинга рнк
KR20200017476A (ko) 2017-06-14 2020-02-18 피티씨 테라퓨틱스, 인크. Rna 스플라이싱의 변경 방법
WO2019028440A1 (en) 2017-08-04 2019-02-07 Skyhawk Therapeutics, Inc. METHODS AND COMPOSITIONS FOR MODULATING SPLICING
US20210355509A1 (en) * 2018-08-07 2021-11-18 The Children's Hospital Of Philadelphia Alternative splicing regulation of gene expression and therapeutic methods
EP3864161A4 (en) * 2018-10-09 2022-11-23 The University of North Carolina at Chapel Hill Regulated gene editing system
WO2020163248A1 (en) 2019-02-04 2020-08-13 Skyhawk Therapeutics, Inc. Methods and compositions for modulating splicing
CN114126613A (zh) 2019-02-05 2022-03-01 斯基霍克疗法公司 用于调节剪接的方法和组合物
EP3920915A4 (en) 2019-02-05 2022-10-05 Skyhawk Therapeutics, Inc. METHODS AND COMPOSITIONS FOR MODULATING SPLICE
WO2020163544A1 (en) 2019-02-06 2020-08-13 Skyhawk Therapeutics, Inc. Methods and compositions for modulating splicing
CN113661162A (zh) 2019-02-06 2021-11-16 斯基霍克疗法公司 用于调节剪接的方法和组合物
US11129829B2 (en) 2019-06-17 2021-09-28 Skyhawk Therapeutics, Inc. Methods for modulating splicing
EP4004213A1 (en) 2019-07-25 2022-06-01 Novartis AG Regulatable expression systems
EP4017979A4 (en) * 2019-08-19 2024-03-27 Stoke Therapeutics, Inc. COMPOSITIONS AND METHODS FOR MODULATING PROTEIN SPLICING AND EXPRESSION
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