JP2019528793A5 - - Google Patents
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- Publication number
- JP2019528793A5 JP2019528793A5 JP2019538714A JP2019538714A JP2019528793A5 JP 2019528793 A5 JP2019528793 A5 JP 2019528793A5 JP 2019538714 A JP2019538714 A JP 2019538714A JP 2019538714 A JP2019538714 A JP 2019538714A JP 2019528793 A5 JP2019528793 A5 JP 2019528793A5
- Authority
- JP
- Japan
- Prior art keywords
- vector
- polynucleotide
- adeno
- promoter
- associated virus
- Prior art date
- Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
- Granted
Links
Applications Claiming Priority (3)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| EP16382450 | 2016-09-30 | ||
| EP16382450.1 | 2016-09-30 | ||
| PCT/EP2017/074081 WO2018060097A1 (en) | 2016-09-30 | 2017-09-22 | Adenoassociated virus vectors for the treatment of mucopolysaccharidoses |
Publications (3)
| Publication Number | Publication Date |
|---|---|
| JP2019528793A JP2019528793A (ja) | 2019-10-17 |
| JP2019528793A5 true JP2019528793A5 (https=) | 2020-11-12 |
| JP7059285B2 JP7059285B2 (ja) | 2022-04-25 |
Family
ID=57123944
Family Applications (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2019538714A Expired - Fee Related JP7059285B2 (ja) | 2016-09-30 | 2017-09-22 | ムコ多糖症の治療のためのアデノ随伴ウイルスベクター |
Country Status (10)
| Country | Link |
|---|---|
| US (1) | US11338046B2 (https=) |
| EP (1) | EP3519569B1 (https=) |
| JP (1) | JP7059285B2 (https=) |
| CN (1) | CN109863243B (https=) |
| AR (1) | AR109752A1 (https=) |
| AU (1) | AU2017333336B2 (https=) |
| ES (1) | ES2859661T3 (https=) |
| PT (1) | PT3519569T (https=) |
| TW (1) | TW201814044A (https=) |
| WO (1) | WO2018060097A1 (https=) |
Families Citing this family (14)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| WO2012007458A1 (en) | 2010-07-12 | 2012-01-19 | Universidad Autónoma De Barcelona | Gene therapy composition for use in diabetes treatment |
| EP2692868A1 (en) | 2012-08-02 | 2014-02-05 | Universitat Autònoma De Barcelona | Adeno-associated viral (AAV) vectors useful for transducing adipose tissue |
| CN105377039A (zh) | 2013-05-15 | 2016-03-02 | 明尼苏达大学董事会 | 腺相关病毒介导的基因向中枢神经系统转移 |
| CA2960912A1 (en) | 2014-09-16 | 2016-03-24 | Universitat Autonoma De Barcelona | Adeno-associated viral vectors for the gene therapy of metabolic diseases |
| WO2016087678A1 (en) | 2014-12-05 | 2016-06-09 | Universitat Autònoma De Barcelona | Viral vectors for the treatment of diabetes |
| EP3242945B1 (en) | 2015-01-07 | 2021-09-01 | Universitat Autònoma de Barcelona | Single-vector gene construct comprising insulin and glucokinase genes |
| IL306098A (en) | 2017-05-24 | 2023-11-01 | Univ Barcelona Autonoma | Viral expression vectors containing the coding sequence for FIBROBLAST GROWTH FACTOR 21 (FGF21) |
| CA3096293A1 (en) | 2018-04-27 | 2019-10-31 | Rocket Pharmaceuticals, Ltd. | Gene therapy for cns degeneration |
| UA128788C2 (uk) * | 2018-05-30 | 2024-10-23 | Естеве Фармасьютікалз, С.А. | Вектор аденоасоційованого вірусу для лікування мукополісахаридозу типу iva |
| WO2020014523A1 (en) * | 2018-07-12 | 2020-01-16 | Rocket Pharmaceuticals, Ltd. | Gene therapy vectors for treatment of danon disease |
| EP3914720B9 (en) | 2019-07-10 | 2023-09-27 | Masonic Medical Research Laboratory | Vgll4 with ucp-1 cis-regulatory element and method of use thereof |
| CN111718947B (zh) * | 2020-06-18 | 2022-08-23 | 舒泰神（北京）生物制药股份有限公司 | 用于治疗ⅲa或ⅲb型粘多糖贮积症的腺相关病毒载体及用途 |
| JP2023538519A (ja) | 2020-08-07 | 2023-09-08 | スペースクラフト セブン リミテッド ライアビリティ カンパニー | Ａａｖベクターを使用したプラコフィリン－２（ｐｋｐ２）遺伝子治療 |
| CN114480454B (zh) * | 2020-10-27 | 2024-03-29 | 华东理工大学 | 用于治疗粘多糖贮积症ⅱ型的腺相关病毒载体、药物及其应用 |
Family Cites Families (10)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| US7232670B2 (en) * | 2001-09-28 | 2007-06-19 | St. Jude Children's Research Hospital | Targeting proteins to cells expressing mannose receptors via expression in insect cells |
| EP2325301B1 (en) * | 2003-02-11 | 2015-09-02 | Shire Human Genetic Therapies, Inc. | Diagnosis and treatment of multiple sulfatase deficiency and others using a formylglycine generating enzyme (FGE) |
| EP2394667A1 (en) * | 2010-06-10 | 2011-12-14 | Laboratorios Del Dr. Esteve, S.A. | Vectors and sequences for the treatment of diseases |
| CA2863964C (en) * | 2012-02-07 | 2021-10-26 | Global Bio Therapeutics Usa, Inc. | Compartmentalized method of nucleic acid delivery and compositions and uses thereof |
| CN105916990B (zh) * | 2013-08-02 | 2020-02-04 | 巴塞罗那自治大学 | 用于转导脂肪组织的腺相关病毒载体 |
| CN120174012A (zh) * | 2013-10-24 | 2025-06-20 | 优尼科Ip有限公司 | 用于基因治疗神经疾病的aav-5假型载体 |
| GB201322798D0 (en) * | 2013-12-20 | 2014-02-05 | Oxford Biomedica Ltd | Production system |
| AR100419A1 (es) * | 2014-05-14 | 2016-10-05 | Esteve Labor Dr | Vectores de virus adenoasociados para el tratamiento de trastornos de almacenamiento lisosómico |
| TN2017000353A1 (en) * | 2015-02-10 | 2019-01-16 | Genzyme Corp | Enhanced delivery of viral particles to the striatum and cortex |
| US9981021B1 (en) * | 2015-04-09 | 2018-05-29 | Kinetiq, Inc. | Subcutaneous therapeutic enzyme formulations, uses, and methods for generating thereof |
-
2017
- 2017-09-22 JP JP2019538714A patent/JP7059285B2/ja not_active Expired - Fee Related
- 2017-09-22 WO PCT/EP2017/074081 patent/WO2018060097A1/en not_active Ceased
- 2017-09-22 AU AU2017333336A patent/AU2017333336B2/en not_active Ceased
- 2017-09-22 PT PT177775418T patent/PT3519569T/pt unknown
- 2017-09-22 US US16/337,953 patent/US11338046B2/en active Active
- 2017-09-22 ES ES17777541T patent/ES2859661T3/es active Active
- 2017-09-22 CN CN201780060410.7A patent/CN109863243B/zh active Active
- 2017-09-22 EP EP17777541.8A patent/EP3519569B1/en active Active
- 2017-09-29 AR ARP170102704A patent/AR109752A1/es unknown
- 2017-09-30 TW TW106133935A patent/TW201814044A/zh unknown
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