JP2019528793A5 - - Google Patents
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- Publication number
- JP2019528793A5 JP2019528793A5 JP2019538714A JP2019538714A JP2019528793A5 JP 2019528793 A5 JP2019528793 A5 JP 2019528793A5 JP 2019538714 A JP2019538714 A JP 2019538714A JP 2019538714 A JP2019538714 A JP 2019538714A JP 2019528793 A5 JP2019528793 A5 JP 2019528793A5
- Authority
- JP
- Japan
- Prior art keywords
- vector
- polynucleotide
- adeno
- promoter
- associated virus
- Prior art date
- Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
- Granted
Links
Applications Claiming Priority (3)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| EP16382450 | 2016-09-30 | ||
| EP16382450.1 | 2016-09-30 | ||
| PCT/EP2017/074081 WO2018060097A1 (en) | 2016-09-30 | 2017-09-22 | Adenoassociated virus vectors for the treatment of mucopolysaccharidoses |
Publications (3)
| Publication Number | Publication Date |
|---|---|
| JP2019528793A JP2019528793A (ja) | 2019-10-17 |
| JP2019528793A5 true JP2019528793A5 (https=) | 2020-11-12 |
| JP7059285B2 JP7059285B2 (ja) | 2022-04-25 |
Family
ID=57123944
Family Applications (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2019538714A Expired - Fee Related JP7059285B2 (ja) | 2016-09-30 | 2017-09-22 | ムコ多糖症の治療のためのアデノ随伴ウイルスベクター |
Country Status (10)
| Country | Link |
|---|---|
| US (1) | US11338046B2 (https=) |
| EP (1) | EP3519569B1 (https=) |
| JP (1) | JP7059285B2 (https=) |
| CN (1) | CN109863243B (https=) |
| AR (1) | AR109752A1 (https=) |
| AU (1) | AU2017333336B2 (https=) |
| ES (1) | ES2859661T3 (https=) |
| PT (1) | PT3519569T (https=) |
| TW (1) | TW201814044A (https=) |
| WO (1) | WO2018060097A1 (https=) |
Families Citing this family (14)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| EP2605798A1 (en) | 2010-07-12 | 2013-06-26 | Universidad Autònoma de Barcelona | Gene therapy composition for use in diabetes treatment |
| EP2692868A1 (en) | 2012-08-02 | 2014-02-05 | Universitat Autònoma De Barcelona | Adeno-associated viral (AAV) vectors useful for transducing adipose tissue |
| CN115120746A (zh) | 2013-05-15 | 2022-09-30 | 明尼苏达大学董事会 | 腺相关病毒介导的基因向中枢神经系统转移 |
| EP3194430A1 (en) | 2014-09-16 | 2017-07-26 | Universitat Autònoma De Barcelona | Adeno-associated viral vectors for the gene therapy of metabolic diseases |
| US11085055B2 (en) | 2014-12-05 | 2021-08-10 | Universitat Autonoma De Barcelona | Viral vectors for the treatment of diabetes |
| US11033638B2 (en) | 2015-01-07 | 2021-06-15 | Universität Autonoma De Barcelona | Single-vector gene construct comprising insulin and glucokinase genes |
| IL270882B2 (en) | 2017-05-24 | 2024-02-01 | Univ Barcelona Autonoma | Viral expression vectors containing the coding sequence for FIBROBLAST GROWTH FACTOR 21 (FGF21 |
| MX2020011386A (es) | 2018-04-27 | 2021-01-29 | Spacecraft Seven Llc | Terapia genica para la degeneracion del snc. |
| MX2020012911A (es) * | 2018-05-30 | 2021-02-26 | Esteve Pharmaceuticals Sa | Vectores de virus adenoasociados para el tratamiento de mucopolisacaridosis tipo iv a. |
| KR102918544B1 (ko) * | 2018-07-12 | 2026-01-27 | 로켓 파마슈티컬스, 리미티드 | 다논병을 치료하기 위한 유전자 요법 벡터 |
| ES2948620T3 (es) | 2019-07-10 | 2023-09-14 | Masonic Medical Res Laboratory | Vgll4 con elemento regulador CIS de UCP-1 y método de uso del mismo |
| CN111718947B (zh) * | 2020-06-18 | 2022-08-23 | 舒泰神（北京）生物制药股份有限公司 | 用于治疗ⅲa或ⅲb型粘多糖贮积症的腺相关病毒载体及用途 |
| KR20230043869A (ko) | 2020-08-07 | 2023-03-31 | 스페이스크래프트 세븐, 엘엘씨 | Aav 벡터를 사용한 플라코필린-2(pkp2) 유전자 요법 |
| CN114480454B (zh) * | 2020-10-27 | 2024-03-29 | 华东理工大学 | 用于治疗粘多糖贮积症ⅱ型的腺相关病毒载体、药物及其应用 |
Family Cites Families (10)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| US7232670B2 (en) * | 2001-09-28 | 2007-06-19 | St. Jude Children's Research Hospital | Targeting proteins to cells expressing mannose receptors via expression in insect cells |
| CA2515708A1 (en) * | 2003-02-11 | 2004-08-26 | Transkaryotic Therapies, Inc. | Diagnosis and treatment of multiple sulfatase deficiency and other sulfatase deficiencies |
| EP2394667A1 (en) | 2010-06-10 | 2011-12-14 | Laboratorios Del Dr. Esteve, S.A. | Vectors and sequences for the treatment of diseases |
| JP6188728B2 (ja) | 2012-02-07 | 2017-08-30 | グローバル・バイオ・セラピューティクス・インコーポレイテッドＧｌｏｂａｌ Ｂｉｏ Ｔｈｅｒａｐｅｕｔｉｃｓ，Ｉｎｃ． | 核酸送達の区画化方法ならびにその組成物および使用 |
| CN105916990B (zh) * | 2013-08-02 | 2020-02-04 | 巴塞罗那自治大学 | 用于转导脂肪组织的腺相关病毒载体 |
| CN105745326A (zh) * | 2013-10-24 | 2016-07-06 | 优尼科Ip有限公司 | 用于基因治疗神经疾病的aav-5假型载体 |
| GB201322798D0 (en) * | 2013-12-20 | 2014-02-05 | Oxford Biomedica Ltd | Production system |
| CA2947468C (en) | 2014-05-14 | 2022-10-25 | Laboratorios Del Dr. Esteve S.A. | Adenoassociated virus vectors for the treatment of lysosomal storage disorders |
| CN107530447A (zh) * | 2015-02-10 | 2018-01-02 | 建新公司 | 病毒颗粒至纹状体和皮质的增强递送 |
| US9981021B1 (en) * | 2015-04-09 | 2018-05-29 | Kinetiq, Inc. | Subcutaneous therapeutic enzyme formulations, uses, and methods for generating thereof |
-
2017
- 2017-09-22 US US16/337,953 patent/US11338046B2/en active Active
- 2017-09-22 WO PCT/EP2017/074081 patent/WO2018060097A1/en not_active Ceased
- 2017-09-22 JP JP2019538714A patent/JP7059285B2/ja not_active Expired - Fee Related
- 2017-09-22 ES ES17777541T patent/ES2859661T3/es active Active
- 2017-09-22 AU AU2017333336A patent/AU2017333336B2/en not_active Ceased
- 2017-09-22 PT PT177775418T patent/PT3519569T/pt unknown
- 2017-09-22 EP EP17777541.8A patent/EP3519569B1/en active Active
- 2017-09-22 CN CN201780060410.7A patent/CN109863243B/zh active Active
- 2017-09-29 AR ARP170102704A patent/AR109752A1/es unknown
- 2017-09-30 TW TW106133935A patent/TW201814044A/zh unknown
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