JP2019519511A5 - - Google Patents
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- JP2019519511A5 JP2019519511A5 JP2018560776A JP2018560776A JP2019519511A5 JP 2019519511 A5 JP2019519511 A5 JP 2019519511A5 JP 2018560776 A JP2018560776 A JP 2018560776A JP 2018560776 A JP2018560776 A JP 2018560776A JP 2019519511 A5 JP2019519511 A5 JP 2019519511A5
- Authority
- JP
- Japan
- Prior art keywords
- hours
- glycero
- mrna
- pharmaceutical composition
- phosphocholine
- Prior art date
- Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
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Priority Applications (1)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| JP2023002608A JP2023055716A (ja) | 2016-05-18 | 2023-01-11 | Ｉｉ型シトルリン血症の治療のためのシトリンをコードするポリヌクレオチド |
Applications Claiming Priority (3)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| US201662338479P | 2016-05-18 | 2016-05-18 | |
| US62/338,479 | 2016-05-18 | ||
| PCT/US2017/033421 WO2017201349A1 (en) | 2016-05-18 | 2017-05-18 | Polynucleotides encoding citrin for the treatment of citrullinemia type 2 |
Related Child Applications (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2023002608A Division JP2023055716A (ja) | 2016-05-18 | 2023-01-11 | Ｉｉ型シトルリン血症の治療のためのシトリンをコードするポリヌクレオチド |
Publications (3)
| Publication Number | Publication Date |
|---|---|
| JP2019519511A JP2019519511A (ja) | 2019-07-11 |
| JP2019519511A5 true JP2019519511A5 (https=) | 2020-07-02 |
| JP7210287B2 JP7210287B2 (ja) | 2023-01-23 |
Family
ID=59009788
Family Applications (2)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2018560776A Active JP7210287B2 (ja) | 2016-05-18 | 2017-05-18 | Ｉｉ型シトルリン血症の治療のためのシトリンをコードするポリヌクレオチド |
| JP2023002608A Pending JP2023055716A (ja) | 2016-05-18 | 2023-01-11 | Ｉｉ型シトルリン血症の治療のためのシトリンをコードするポリヌクレオチド |
Family Applications After (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2023002608A Pending JP2023055716A (ja) | 2016-05-18 | 2023-01-11 | Ｉｉ型シトルリン血症の治療のためのシトリンをコードするポリヌクレオチド |
Country Status (9)
| Country | Link |
|---|---|
| US (2) | US10993918B2 (https=) |
| EP (1) | EP3458081B1 (https=) |
| JP (2) | JP7210287B2 (https=) |
| AU (2) | AU2017268396B2 (https=) |
| CA (1) | CA3024625A1 (https=) |
| MA (1) | MA45036A (https=) |
| MY (1) | MY201498A (https=) |
| SG (1) | SG11201810162PA (https=) |
| WO (1) | WO2017201349A1 (https=) |
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| EP3388834B1 (en) | 2013-03-15 | 2020-04-15 | Translate Bio, Inc. | Synergistic enhancement of the delivery of nucleic acids via blended formulations |
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| HUE060907T2 (hu) | 2014-06-25 | 2023-04-28 | Acuitas Therapeutics Inc | Új lipidek és lipid nanorészecske formulációk nukleinsavak bevitelére |
| JP6948313B6 (ja) | 2015-09-17 | 2022-01-14 | モデルナティエックス インコーポレイテッド | 治療剤の細胞内送達のための化合物および組成物 |
| HRP20230209T1 (hr) | 2015-10-28 | 2023-04-14 | Acuitas Therapeutics Inc. | Novi lipidi i lipidne formulacije nanočestica za isporuku nukleinskih kiselina |
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| JP2019519601A (ja) | 2016-05-18 | 2019-07-11 | モダーナティエックス・インコーポレイテッドＭｏｄｅｒｎａＴＸ， Ｉｎｃ． | 急性間欠性ポルフィリン症の治療のためのポルホビリノゲン脱アミノ酵素をコードするポリヌクレオチド |
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-
2017
- 2017-05-18 MA MA045036A patent/MA45036A/fr unknown
- 2017-05-18 AU AU2017268396A patent/AU2017268396B2/en not_active Ceased
- 2017-05-18 WO PCT/US2017/033421 patent/WO2017201349A1/en not_active Ceased
- 2017-05-18 CA CA3024625A patent/CA3024625A1/en active Pending
- 2017-05-18 MY MYPI2018001974A patent/MY201498A/en unknown
- 2017-05-18 EP EP17728001.3A patent/EP3458081B1/en active Active
- 2017-05-18 SG SG11201810162PA patent/SG11201810162PA/en unknown
- 2017-05-18 JP JP2018560776A patent/JP7210287B2/ja active Active
- 2017-05-18 US US16/302,360 patent/US10993918B2/en active Active
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2021
- 2021-01-21 US US17/154,325 patent/US12239742B2/en active Active
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2023
- 2023-01-11 JP JP2023002608A patent/JP2023055716A/ja active Pending
- 2023-08-16 AU AU2023216799A patent/AU2023216799A1/en not_active Abandoned
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