JP2018532403A5 - - Google Patents

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Publication number
JP2018532403A5
JP2018532403A5 JP2018516030A JP2018516030A JP2018532403A5 JP 2018532403 A5 JP2018532403 A5 JP 2018532403A5 JP 2018516030 A JP2018516030 A JP 2018516030A JP 2018516030 A JP2018516030 A JP 2018516030A JP 2018532403 A5 JP2018532403 A5 JP 2018532403A5
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JP
Japan
Prior art keywords
composition
item
tissue
guide rna
genome
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Pending
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JP2018516030A
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English (en)
Japanese (ja)
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JP2018532403A (ja
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Priority claimed from PCT/US2016/053960 external-priority patent/WO2017058793A1/en
Publication of JP2018532403A publication Critical patent/JP2018532403A/ja
Publication of JP2018532403A5 publication Critical patent/JP2018532403A5/ja
Pending legal-status Critical Current

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JP2018516030A 2015-09-29 2016-09-27 送達方法および組成物 Pending JP2018532403A (ja)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US201562234340P 2015-09-29 2015-09-29
US62/234,340 2015-09-29
PCT/US2016/053960 WO2017058793A1 (en) 2015-09-29 2016-09-27 Delivery methods and compositions

Publications (2)

Publication Number Publication Date
JP2018532403A JP2018532403A (ja) 2018-11-08
JP2018532403A5 true JP2018532403A5 (enExample) 2019-10-31

Family

ID=58408949

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JP2018516030A Pending JP2018532403A (ja) 2015-09-29 2016-09-27 送達方法および組成物

Country Status (8)

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US (1) US20170087224A1 (enExample)
EP (1) EP3355954A4 (enExample)
JP (1) JP2018532403A (enExample)
CN (1) CN108601883A (enExample)
AU (1) AU2016332704A1 (enExample)
CA (1) CA2999922A1 (enExample)
HK (1) HK1258900A1 (enExample)
WO (1) WO2017058793A1 (enExample)

Families Citing this family (44)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
WO2013066438A2 (en) 2011-07-22 2013-05-10 President And Fellows Of Harvard College Evaluation and improvement of nuclease cleavage specificity
US20150044192A1 (en) 2013-08-09 2015-02-12 President And Fellows Of Harvard College Methods for identifying a target site of a cas9 nuclease
US9359599B2 (en) 2013-08-22 2016-06-07 President And Fellows Of Harvard College Engineered transcription activator-like effector (TALE) domains and uses thereof
US9340799B2 (en) 2013-09-06 2016-05-17 President And Fellows Of Harvard College MRNA-sensing switchable gRNAs
US9388430B2 (en) 2013-09-06 2016-07-12 President And Fellows Of Harvard College Cas9-recombinase fusion proteins and uses thereof
US9526784B2 (en) 2013-09-06 2016-12-27 President And Fellows Of Harvard College Delivery system for functional nucleases
US20150166984A1 (en) 2013-12-12 2015-06-18 President And Fellows Of Harvard College Methods for correcting alpha-antitrypsin point mutations
WO2016022363A2 (en) 2014-07-30 2016-02-11 President And Fellows Of Harvard College Cas9 proteins including ligand-dependent inteins
SG10202104041PA (en) 2015-10-23 2021-06-29 Harvard College Nucleobase editors and uses thereof
CN109788979B (zh) 2016-06-27 2022-04-19 盖能适治疗股份有限公司 发生器和具有电极的导管以及用于治疗肺通道的方法
US12403305B2 (en) 2016-06-27 2025-09-02 Galvanize Therapeutics, Inc. Immunostimulation in the treatment of viral infection
KR20250103795A (ko) 2016-08-03 2025-07-07 프레지던트 앤드 펠로우즈 오브 하바드 칼리지 아데노신 핵염기 편집제 및 그의 용도
US11661590B2 (en) 2016-08-09 2023-05-30 President And Fellows Of Harvard College Programmable CAS9-recombinase fusion proteins and uses thereof
WO2018039438A1 (en) 2016-08-24 2018-03-01 President And Fellows Of Harvard College Incorporation of unnatural amino acids into proteins using base editing
SG11201903089RA (en) 2016-10-14 2019-05-30 Harvard College Aav delivery of nucleobase editors
WO2018119359A1 (en) 2016-12-23 2018-06-28 President And Fellows Of Harvard College Editing of ccr5 receptor gene to protect against hiv infection
EP3592381A1 (en) 2017-03-09 2020-01-15 President and Fellows of Harvard College Cancer vaccine
US11898179B2 (en) 2017-03-09 2024-02-13 President And Fellows Of Harvard College Suppression of pain by gene editing
WO2018165629A1 (en) 2017-03-10 2018-09-13 President And Fellows Of Harvard College Cytosine to guanine base editor
WO2018176009A1 (en) 2017-03-23 2018-09-27 President And Fellows Of Harvard College Nucleobase editors comprising nucleic acid programmable dna binding proteins
WO2018209320A1 (en) 2017-05-12 2018-11-15 President And Fellows Of Harvard College Aptazyme-embedded guide rnas for use with crispr-cas9 in genome editing and transcriptional activation
CN111801345A (zh) 2017-07-28 2020-10-20 哈佛大学的校长及成员们 使用噬菌体辅助连续进化(pace)的进化碱基编辑器的方法和组合物
EP3676376B1 (en) 2017-08-30 2025-01-15 President and Fellows of Harvard College High efficiency base editors comprising gam
US11795443B2 (en) 2017-10-16 2023-10-24 The Broad Institute, Inc. Uses of adenosine base editors
WO2019118949A1 (en) 2017-12-15 2019-06-20 The Broad Institute, Inc. Systems and methods for predicting repair outcomes in genetic engineering
CN118383863A (zh) 2017-12-26 2024-07-26 盖能适治疗股份有限公司 用于各种应用的能量输送的优化
US12157760B2 (en) 2018-05-23 2024-12-03 The Broad Institute, Inc. Base editors and uses thereof
EP3820495A4 (en) 2018-07-09 2022-07-20 The Broad Institute Inc. RNA-PROGRAMMABLE EPIGENETIC RNA MODIFIERS AND THEIR USES
WO2020015279A1 (zh) * 2018-07-17 2020-01-23 杭州观梓健康科技有限公司 一种在干细胞中进行基因定向敲入的方法
WO2020092453A1 (en) 2018-10-29 2020-05-07 The Broad Institute, Inc. Nucleobase editors comprising geocas9 and uses thereof
WO2020102532A1 (en) * 2018-11-15 2020-05-22 President And Fellows Of Harvard College Genetically engineered skin cells for the systemic in vivo treatment of deficient enzymes, factors or proteins
US12351837B2 (en) 2019-01-23 2025-07-08 The Broad Institute, Inc. Supernegatively charged proteins and uses thereof
EP3942043A2 (en) 2019-03-19 2022-01-26 The Broad Institute, Inc. Methods and compositions for editing nucleotide sequences
US12098429B2 (en) * 2019-03-25 2024-09-24 The Chinese University Of Hong Kong Determining linear and circular forms of circulating nucleic acids
KR20210151789A (ko) * 2019-04-08 2021-12-14 벨라니디 테크놀로지스 엘엘씨 마이크로규모 내지 나노규모의 환경을 감지, 검출 및 유효화하기 위한 시스템, 장치 및 방법
WO2020214842A1 (en) 2019-04-17 2020-10-22 The Broad Institute, Inc. Adenine base editors with reduced off-target effects
AU2020257266A1 (en) 2019-04-18 2021-11-11 Galvanize Therapeutics, Inc. Devices, systems and methods for the treatment of abnormal tissue
US12435330B2 (en) 2019-10-10 2025-10-07 The Broad Institute, Inc. Methods and compositions for prime editing RNA
BR112022022603A2 (pt) 2020-05-08 2023-01-17 Broad Inst Inc Métodos e composições para edição simultânea de ambas as fitas de sequência alvo de nucleotídeos de fita dupla
AU2021281307A1 (en) 2020-05-29 2022-12-15 Georgia Tech Research Corporation Devices, systems, and methods for facilitating tissue delivery of drug
WO2022031797A1 (en) * 2020-08-04 2022-02-10 Galary, Inc. Pulsed electric field transfer of molecules to cells while in the body
CN116829691A (zh) * 2020-08-04 2023-09-29 盖能适治疗股份有限公司 分子到体内细胞的脉冲电场转移
CN112807273B (zh) * 2021-02-23 2022-06-17 浙江大学 一种治疗炎症性皮肤病的基因编辑微针及其应用
JP2023094496A (ja) * 2021-12-23 2023-07-05 委子 陌間 抗菌・ウイルス治療薬の製造方法

Family Cites Families (9)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
US6713291B2 (en) * 1999-01-28 2004-03-30 Alan D. King Electrodes coated with treating agent and uses thereof
EP1432799A2 (en) * 2001-07-17 2004-06-30 Anne Josephine Milner Silencing of gene expression by sirna
WO2011097036A1 (en) * 2010-02-08 2011-08-11 Sangamo Biosciences, Inc. Engineered cleavage half-domains
WO2011109735A2 (en) * 2010-03-05 2011-09-09 Cornell University Ultrasound-assisted convection enhanced delivery of compounds in vivo with a transducer cannula assembly
RU2016128077A (ru) * 2013-12-12 2018-12-06 Те Брод Инститьют Инк. Доставка, применение и применения в терапии систем и композиций crispr-cas для лечения обусловленных hbv и вирусных заболеваний и нарушений
EP3107999A4 (en) * 2014-02-18 2017-10-04 Duke University Compositions for the inactivation of virus replication and methods of making and using the same
KR20170005494A (ko) * 2014-05-30 2017-01-13 더 보드 어브 트러스티스 어브 더 리랜드 스탠포드 주니어 유니버시티 잠복 바이러스 감염에 대한 치료제를 전달하는 조성물 및 방법
CA3000155A1 (en) * 2015-05-29 2016-12-08 Agenovir Corporation Compositions and methods for cell targeted hpv treatment
WO2017147446A1 (en) * 2016-02-25 2017-08-31 Agenovir Corporation Viral and oncoviral nuclease treatment

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