JP2014519806A - 細胞内で自己会合し、RNAi活性を産生する組成物を使用した遺伝子発現を調節するための方法および成分 - Google Patents

細胞内で自己会合し、RNAi活性を産生する組成物を使用した遺伝子発現を調節するための方法および成分 Download PDF

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JP2014519806A
JP2014519806A JP2014506610A JP2014506610A JP2014519806A JP 2014519806 A JP2014519806 A JP 2014519806A JP 2014506610 A JP2014506610 A JP 2014506610A JP 2014506610 A JP2014506610 A JP 2014506610A JP 2014519806 A JP2014519806 A JP 2014519806A
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スミス,ラリー,ジェイ.
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スミス ホールディングス,エルエルシー
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JP2014506610A 2011-04-20 2012-04-20 細胞内で自己会合し、RNAi活性を産生する組成物を使用した遺伝子発現を調節するための方法および成分 Pending JP2014519806A (ja)

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Application Number Priority Date Filing Date Title
US201161477283P 2011-04-20 2011-04-20
US201161477291P 2011-04-20 2011-04-20
US61/477,291 2011-04-20
US61/477,283 2011-04-20
US201161477875P 2011-04-21 2011-04-21
US61/477,875 2011-04-21
PCT/US2012/034595 WO2012145729A2 (en) 2011-04-20 2012-04-20 Methods and compositions for modulating gene expression using components that self assemble in cells and produce rnai activity

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JP2014519806A true JP2014519806A (ja) 2014-08-21
JP2014519806A5 JP2014519806A5 (https=) 2015-07-30

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US (2) US20150038549A1 (https=)
EP (1) EP2699271A4 (https=)
JP (1) JP2014519806A (https=)
CN (1) CN104271740A (https=)
AU (1) AU2012245188A1 (https=)
BR (1) BR112013027070A2 (https=)
CA (1) CA2871089A1 (https=)
IL (1) IL228951A0 (https=)
RU (1) RU2013151301A (https=)
WO (1) WO2012145729A2 (https=)

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WO2015106128A2 (en) * 2014-01-09 2015-07-16 Alnylam Pharmaceuticals, Inc. MODIFIED RNAi AGENTS
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US20250297258A1 (en) * 2021-07-07 2025-09-25 Ractigen Therapeutics Oligonucleotide-based delivery vehicle for oligonucleotides agents and methods of use thereof
WO2024098061A2 (en) 2022-11-04 2024-05-10 Genkardia Inc. Oligonucleotide-based therapeutics targeting cyclin d2 for the treatment of heart failure
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NZ617944A (en) 2016-01-29
WO2012145729A3 (en) 2014-05-01
IL228951A0 (en) 2013-12-31
EP2699271A4 (en) 2015-10-07
CN104271740A (zh) 2015-01-07
AU2012245188A1 (en) 2013-12-05
CA2871089A1 (en) 2012-10-26
US20150038549A1 (en) 2015-02-05
US20160272972A1 (en) 2016-09-22
WO2012145729A2 (en) 2012-10-26
EP2699271A2 (en) 2014-02-26
RU2013151301A (ru) 2015-05-27
BR112013027070A2 (pt) 2019-09-24

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