JP2013509168A5 - - Google Patents
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- Publication number
- JP2013509168A5 JP2013509168A5 JP2012535849A JP2012535849A JP2013509168A5 JP 2013509168 A5 JP2013509168 A5 JP 2013509168A5 JP 2012535849 A JP2012535849 A JP 2012535849A JP 2012535849 A JP2012535849 A JP 2012535849A JP 2013509168 A5 JP2013509168 A5 JP 2013509168A5
- Authority
- JP
- Japan
- Prior art keywords
- nucleic acid
- expression cassette
- vector
- seq
- acid expression
- Prior art date
- Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
- Granted
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Applications Claiming Priority (3)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| EP09174519 | 2009-10-29 | ||
| EP09174519.0 | 2009-10-29 | ||
| PCT/EP2010/066474 WO2011051450A1 (en) | 2009-10-29 | 2010-10-29 | Cardiac-specific nucleic acid regulatory elements and methods and use thereof |
Publications (3)
| Publication Number | Publication Date |
|---|---|
| JP2013509168A JP2013509168A (ja) | 2013-03-14 |
| JP2013509168A5 true JP2013509168A5 (enExample) | 2013-12-19 |
| JP5823969B2 JP5823969B2 (ja) | 2015-11-25 |
Family
ID=43414855
Family Applications (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2012535849A Expired - Fee Related JP5823969B2 (ja) | 2009-10-29 | 2010-10-29 | 心臓特異的核酸調節因子ならびにこの方法および使用 |
Country Status (6)
| Country | Link |
|---|---|
| US (1) | US9353164B2 (enExample) |
| EP (1) | EP2494058B1 (enExample) |
| JP (1) | JP5823969B2 (enExample) |
| AU (1) | AU2010311376B2 (enExample) |
| CA (1) | CA2778945A1 (enExample) |
| WO (1) | WO2011051450A1 (enExample) |
Families Citing this family (17)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| AU2010311376B2 (en) | 2009-10-29 | 2014-07-03 | Life Sciences Research Partners Vzw | Cardiac-specific nucleic acid regulatory elements and methods and use thereof |
| US8859517B2 (en) | 2011-08-08 | 2014-10-14 | Fondazione Salvatore Maugeri Clinica Del Lavoro E Della Riabilitazione | Method of gene transfer for the treatment of recessive catecholaminergic polymorphic ventricular tachycardia (CPVT) |
| US20130136729A1 (en) * | 2011-11-11 | 2013-05-30 | University of Virginia Patent Foundation, d/b/a University of Virginia Licensing & Ventures Group | Compositions and methods for targeting and treating diseases and injuries using adeno-associated virus vectors |
| WO2014077863A1 (en) * | 2012-11-19 | 2014-05-22 | Nature Technology Corporation | Replicative minicircle vectors with improved expression |
| CA2932624C (en) * | 2013-12-09 | 2023-03-28 | Texas Heart Institute | Treating cardiac conditions using shrna or sirna targeting salvador (sav1) |
| WO2015110449A1 (en) * | 2014-01-21 | 2015-07-30 | Vrije Universiteit Brussel | Muscle-specific nucleic acid regulatory elements and methods and use thereof |
| US10570183B2 (en) | 2016-04-19 | 2020-02-25 | The Board Of Regents Of The University Of Texas System | Use of a small native peptide activator of SERCA pump for treatment of heart failure and other disorders characterized by cytosolic calcium overload |
| WO2018178067A1 (en) | 2017-03-27 | 2018-10-04 | Vrije Universiteit Brussel | Diaphragm-specific nucleic acid regulatory elements and methods and use thereof |
| CN113166767B (zh) * | 2018-09-05 | 2025-03-28 | 马克思-德布鲁克-分子医学中心亥姆霍兹联合会 | 用于工程合成顺式调控dna的方法 |
| WO2020084162A1 (en) | 2018-10-26 | 2020-04-30 | Vrije Universiteit Brussel | Liver-specific nucleic acid regulatory elements and methods and use thereof |
| WO2021116138A1 (en) * | 2019-12-09 | 2021-06-17 | Ucl Business Ltd | Gene therapy composition and treatment for myh7-linked cardiomyopathy |
| AU2020412375A1 (en) * | 2019-12-24 | 2022-06-30 | AskBio Inc. | Regulatory nucleic acid sequences |
| EP4087489B1 (en) | 2020-01-08 | 2025-05-14 | Vitruvia Holdings Inc. | Methods and computing system for processing ultrasound image to determine health of subdermal tissue |
| CN115298307A (zh) | 2020-02-18 | 2022-11-04 | 布鲁塞尔自由大学 | 核酸调节元件的新组合及其方法和用途 |
| JP2024502257A (ja) * | 2020-12-21 | 2024-01-18 | フレイエ ユニヴェルシテイト ブリュッセル | 心筋細胞由来核酸調節エレメント並びにその方法及び使用 |
| JP2024523707A (ja) | 2021-07-08 | 2024-06-28 | テナヤ セラピューティクス， インコーポレイテッド | 遺伝子治療のための最適化された発現カセット |
| AR126660A1 (es) | 2021-07-28 | 2023-11-01 | Univ Brussel Vrije | Mejorando la eficacia de la terapia génica dirigida a músculos |
Family Cites Families (11)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| FR2797273B1 (fr) * | 1999-08-06 | 2004-01-02 | Pasteur Institut | Polynucleotides dirigeant l'activation de l'expression d'un gene dans le coeur et ses applications a la therapie genique |
| AU2001234470A1 (en) * | 2000-01-14 | 2001-07-24 | Beth Israel Deaconess Medical Center | Cardiac-cell specific enhancer elements and uses thereof |
| ATE373095T1 (de) * | 2000-07-14 | 2007-09-15 | Univ Michigan | Mutierte muskelspezifische enhancer |
| US20050004058A1 (en) * | 2000-12-07 | 2005-01-06 | Patrick Benoit | Sequences upstream of the carp gene, vectors containing them and uses thereof |
| US7714100B2 (en) * | 2004-01-27 | 2010-05-11 | Compugen Ltd | Nucleotide and amino acid sequences, and assays and methods of use thereof for diagnosis of cardiac disease |
| US20060068496A1 (en) * | 2004-07-29 | 2006-03-30 | Kelly James H | Differentiation of stem cells |
| US20080081354A1 (en) * | 2006-10-02 | 2008-04-03 | Cardiac Pacemakers, Inc. | Devices, vectors and methods for inducible ischemia cardioprotection |
| US8383601B2 (en) | 2006-10-30 | 2013-02-26 | Thomas Jefferson University | Tissue specific gene therapy treatment |
| WO2008126083A2 (en) * | 2007-04-11 | 2008-10-23 | Technion Research & Development Foundation Ltd. | Methods for identification and selection of human embryonic stem cell derived cells |
| DK2282764T3 (da) | 2008-04-22 | 2019-10-14 | Vib Vzw | Leverspecifikke nukleinsyreregulerende elementer samt fremgangsmåder og anvendelser heraf |
| AU2010311376B2 (en) | 2009-10-29 | 2014-07-03 | Life Sciences Research Partners Vzw | Cardiac-specific nucleic acid regulatory elements and methods and use thereof |
-
2010
- 2010-10-29 AU AU2010311376A patent/AU2010311376B2/en not_active Ceased
- 2010-10-29 US US13/504,614 patent/US9353164B2/en not_active Expired - Fee Related
- 2010-10-29 EP EP10771459.4A patent/EP2494058B1/en not_active Not-in-force
- 2010-10-29 WO PCT/EP2010/066474 patent/WO2011051450A1/en not_active Ceased
- 2010-10-29 JP JP2012535849A patent/JP5823969B2/ja not_active Expired - Fee Related
- 2010-10-29 CA CA2778945A patent/CA2778945A1/en not_active Abandoned
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