JP2011511090A5 - - Google Patents

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Publication number
JP2011511090A5
JP2011511090A5 JP2010546007A JP2010546007A JP2011511090A5 JP 2011511090 A5 JP2011511090 A5 JP 2011511090A5 JP 2010546007 A JP2010546007 A JP 2010546007A JP 2010546007 A JP2010546007 A JP 2010546007A JP 2011511090 A5 JP2011511090 A5 JP 2011511090A5
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JP
Japan
Prior art keywords
pharmaceutical composition
cells
growth factor
layer
eye
Prior art date
Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
Ceased
Application number
JP2010546007A
Other languages
English (en)
Japanese (ja)
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JP2011511090A (ja
Filing date
Publication date
Application filed filed Critical
Priority claimed from PCT/US2009/033275 external-priority patent/WO2009100253A1/en
Publication of JP2011511090A publication Critical patent/JP2011511090A/ja
Publication of JP2011511090A5 publication Critical patent/JP2011511090A5/ja
Ceased legal-status Critical Current

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JP2010546007A 2008-02-07 2009-02-05 治療用タンパク質をコードする発現ベクターの硝子体内投与による光受容体のレスキュー方法 Ceased JP2011511090A (ja)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US2699008P 2008-02-07 2008-02-07
US9322808P 2008-08-29 2008-08-29
PCT/US2009/033275 WO2009100253A1 (en) 2008-02-07 2009-02-05 Rescue of photoreceptors by intravitreal administation of an expression vector encoding a therapeutic protein

Publications (2)

Publication Number Publication Date
JP2011511090A JP2011511090A (ja) 2011-04-07
JP2011511090A5 true JP2011511090A5 (https=) 2013-03-28

Family

ID=40939054

Family Applications (1)

Application Number Title Priority Date Filing Date
JP2010546007A Ceased JP2011511090A (ja) 2008-02-07 2009-02-05 治療用タンパク質をコードする発現ベクターの硝子体内投与による光受容体のレスキュー方法

Country Status (7)

Country Link
US (2) US8242093B2 (https=)
EP (1) EP2247258A4 (https=)
JP (1) JP2011511090A (https=)
CN (1) CN101980668A (https=)
AU (1) AU2009212309B2 (https=)
CA (1) CA2713755A1 (https=)
WO (1) WO2009100253A1 (https=)

Families Citing this family (12)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
CN101980668A (zh) * 2008-02-07 2011-02-23 赛拉基因公司 通过玻璃体内施用编码治疗用蛋白质的表达载体救援光感器
GB201103062D0 (en) * 2011-02-22 2011-04-06 Isis Innovation Method
US9902933B2 (en) * 2011-02-25 2018-02-27 Riken Method of producing retinal pigment epithelial cell sheet
EP2872183B1 (en) * 2012-07-11 2018-09-26 The Trustees Of The University Of Pennsylvania Aav-mediated gene therapy for rpgr x-linked retinal degeneration
US20160256571A1 (en) * 2013-09-30 2016-09-08 Sanofi Invention
KR102281881B1 (ko) * 2013-12-06 2021-07-27 엥스띠뛰 나씨오날 드 라 쌍떼 에 드 라 흐쉐르슈 메디깔 (인쎄름) 대상체의 망막 색소 상피에서 목적 폴리뉴클레오티드를 발현시키기 위한 방법 및 약학적 조성물
CN107635584B (zh) * 2015-04-09 2022-06-17 康奈尔大学 基因治疗以预防对过敏原的反应
WO2017093566A1 (en) * 2015-12-04 2017-06-08 Universite Pierre Et Marie Curie (Paris 6) Promoters and uses thereof
WO2017187272A1 (en) * 2016-04-29 2017-11-02 Gensight Biologics Sa Optogenetic visual restoration using chrimson
PL239642B1 (pl) * 2018-08-16 2021-12-20 Pomorski Univ Medyczny W Szczecinie Kompozycja do doszklistkowego podawania białka leczniczego
IL302164A (en) * 2020-10-22 2023-06-01 Visgenx Inc Elovl2 constructs for human gene therapy
WO2024123461A1 (en) * 2022-12-05 2024-06-13 The United States Of America, As Represented By The Secretary, Department Of Health And Human Services Pigment epithelium-derived factor peptides and use for treating retinal degeneration

Family Cites Families (14)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
US5932479A (en) 1988-09-26 1999-08-03 Auburn University Genetic engineering of plant chloroplasts
JP2002512627A (ja) * 1997-06-11 2002-04-23 アコーダ セラピーティックス Cns神経再生組成物及びその使用方法
EP1154691A4 (en) 1999-01-05 2004-07-07 Massachusetts Eye & Ear Infirm TARGETED ADMINISTRATION OF REGULATED RELEASE MEDICINE TO RETINA AND CHOROID THROUGH SCLEROTIC
US6943153B1 (en) * 1999-03-15 2005-09-13 The Regents Of The University Of California Use of recombinant gene delivery vectors for treating or preventing diseases of the eye
AU3755900A (en) * 1999-03-15 2000-10-04 Chiron Corporation Use of recombinant gene delivery vectors for treating or preventing diseases of the eye
WO2001064850A1 (en) 2000-02-29 2001-09-07 Auburn University Genetic engineering of drought tolerance via a plastid genome
EP1274846A4 (en) 2000-03-01 2004-09-29 Univ Auburn PLASTIDE TRANSFORMATION VECTOR FOR THE EXPRESSION OF HUMAN PROTEINS IN PLANTS
US7354760B2 (en) 2001-12-26 2008-04-08 University Of Central Florida Research Foundation, Inc. Expression of protective antigens in transgenic chloroplasts
AU2003253781A1 (en) 2002-07-03 2004-01-23 University Of Central Florida Expression of human interferon in transgenic chloroplasts
WO2006101634A1 (en) 2005-02-17 2006-09-28 The Regents Of The University Of California Müller cell specific gene therapy
US20060188481A1 (en) 2005-02-22 2006-08-24 Saitama Medical School Methods for prophylactically or therapeutically treating an animal for an ocular-related disorder
CA2598029A1 (en) 2005-02-24 2006-10-05 The Scripps Research Institute Isolated myeloid-like bone marrow cell populations and methods of treatment therewith
US20080274143A1 (en) 2005-05-27 2008-11-06 Henry Daniell Chloroplasts Engineering to Express Pharmaceutical Proteins
CN101980668A (zh) * 2008-02-07 2011-02-23 赛拉基因公司 通过玻璃体内施用编码治疗用蛋白质的表达载体救援光感器

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