JP2010509344A - ポンペ病を治療するための方法 - Google Patents
ポンペ病を治療するための方法 Download PDFInfo
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- JP2010509344A JP2010509344A JP2009536345A JP2009536345A JP2010509344A JP 2010509344 A JP2010509344 A JP 2010509344A JP 2009536345 A JP2009536345 A JP 2009536345A JP 2009536345 A JP2009536345 A JP 2009536345A JP 2010509344 A JP2010509344 A JP 2010509344A
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- A61K47/50—Medicinal preparations characterised by the non-active ingredients used, e.g. carriers or inert additives; Targeting or modifying agents chemically bound to the active ingredient the non-active ingredient being chemically bound to the active ingredient, e.g. polymer-drug conjugates
- A61K47/51—Medicinal preparations characterised by the non-active ingredients used, e.g. carriers or inert additives; Targeting or modifying agents chemically bound to the active ingredient the non-active ingredient being chemically bound to the active ingredient, e.g. polymer-drug conjugates the non-active ingredient being a modifying agent
- A61K47/62—Medicinal preparations characterised by the non-active ingredients used, e.g. carriers or inert additives; Targeting or modifying agents chemically bound to the active ingredient the non-active ingredient being chemically bound to the active ingredient, e.g. polymer-drug conjugates the non-active ingredient being a modifying agent the modifying agent being a protein, peptide or polyamino acid
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- A61P43/00—Drugs for specific purposes, not provided for in groups A61P1/00-A61P41/00
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| US90018707P | 2007-02-07 | 2007-02-07 | |
| PCT/US2007/023881 WO2008063511A2 (en) | 2006-11-13 | 2007-11-13 | Methods for treating pompe disease |
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| JP2010509344A true JP2010509344A (ja) | 2010-03-25 |
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| EP (1) | EP2099523A2 (https=) |
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| CA (1) | CA2669347A1 (https=) |
| IL (1) | IL198692A0 (https=) |
| WO (1) | WO2008063511A2 (https=) |
Cited By (2)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| JP2014513952A (ja) * | 2011-04-22 | 2014-06-19 | ジェンザイム・コーポレーション | 促進されたプロセシングを備えた修飾された酸性アルファグルコシダーゼ |
| WO2023204202A1 (ja) * | 2022-04-19 | 2023-10-26 | Ｊｃｒファーマ株式会社 | マンノース－６－リン酸の数を減少させた糖蛋白質 |
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| EP3782655A1 (en) | 2005-05-17 | 2021-02-24 | Amicus Therapeutics, Inc. | A method for the treatment of pompe disease using 1-deoxynojirimycin and derivatives |
| US8536148B2 (en) | 2009-09-04 | 2013-09-17 | The United States Of America, As Represented By The Secretary, Department Of Health And Human Services | Disabling autophagy as a treatment for lysosomal storage diseases |
| WO2012061597A1 (en) * | 2010-11-03 | 2012-05-10 | The United States Of America As Represented By The Secretary, Department Of Health And Human Services Office Of Technology Transfer, National Institutes Of Health | Alpha-glucosidase binders and methods of their use |
| KR20230066482A (ko) | 2012-03-07 | 2023-05-15 | 아미쿠스 세라퓨틱스, 인코포레이티드 | 폼페병의 치료를 위한 고농도 알파-글루코시다제 조성물 |
| AU2014218854B2 (en) * | 2013-02-20 | 2019-01-24 | Valerion Therapeutics, Llc | Methods and compositions for treatment of Pompe disease |
| CN114540327B (zh) | 2014-09-30 | 2026-03-24 | 阿米库斯治疗学公司 | 具有增强的碳水化合物的高强度酸性α-葡糖苷酶 |
| KR20250007693A (ko) | 2015-12-30 | 2025-01-14 | 아미쿠스 세라퓨틱스, 인코포레이티드 | 폼페병 치료용의 강화된 산 알파-글루코시다제 |
| CA3019354A1 (en) | 2016-03-30 | 2017-10-05 | Amicus Therapeutics, Inc. | Method for selection of high m6p recombinant proteins |
| AU2017239641A1 (en) | 2016-03-30 | 2018-10-18 | Amicus Therapeutics, Inc. | Formulations comprising recombinant acid alpha-glucosidase |
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Cited By (2)
| Publication number | Priority date | Publication date | Assignee | Title |
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| JP2014513952A (ja) * | 2011-04-22 | 2014-06-19 | ジェンザイム・コーポレーション | 促進されたプロセシングを備えた修飾された酸性アルファグルコシダーゼ |
| WO2023204202A1 (ja) * | 2022-04-19 | 2023-10-26 | Ｊｃｒファーマ株式会社 | マンノース－６－リン酸の数を減少させた糖蛋白質 |
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| EP2099523A2 (en) | 2009-09-16 |
| CA2669347A1 (en) | 2008-05-29 |
| US20090117091A1 (en) | 2009-05-07 |
| US20120093794A1 (en) | 2012-04-19 |
| AU2007322123A1 (en) | 2008-05-29 |
| IL198692A0 (en) | 2011-07-31 |
| WO2008063511A2 (en) | 2008-05-29 |
| WO2008063511A3 (en) | 2009-04-09 |
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