JP2010509344A - ポンペ病を治療するための方法 - Google Patents
ポンペ病を治療するための方法 Download PDFInfo
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- JP2010509344A JP2010509344A JP2009536345A JP2009536345A JP2010509344A JP 2010509344 A JP2010509344 A JP 2010509344A JP 2009536345 A JP2009536345 A JP 2009536345A JP 2009536345 A JP2009536345 A JP 2009536345A JP 2010509344 A JP2010509344 A JP 2010509344A
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- A61K47/50—Medicinal preparations characterised by the non-active ingredients used, e.g. carriers or inert additives; Targeting or modifying agents chemically bound to the active ingredient the non-active ingredient being chemically bound to the active ingredient, e.g. polymer-drug conjugates
- A61K47/51—Medicinal preparations characterised by the non-active ingredients used, e.g. carriers or inert additives; Targeting or modifying agents chemically bound to the active ingredient the non-active ingredient being chemically bound to the active ingredient, e.g. polymer-drug conjugates the non-active ingredient being a modifying agent
- A61K47/62—Medicinal preparations characterised by the non-active ingredients used, e.g. carriers or inert additives; Targeting or modifying agents chemically bound to the active ingredient the non-active ingredient being chemically bound to the active ingredient, e.g. polymer-drug conjugates the non-active ingredient being a modifying agent the modifying agent being a protein, peptide or polyamino acid
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- A61P—SPECIFIC THERAPEUTIC ACTIVITY OF CHEMICAL COMPOUNDS OR MEDICINAL PREPARATIONS
- A61P43/00—Drugs for specific purposes, not provided for in groups A61P1/00-A61P41/00
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| US90018707P | 2007-02-07 | 2007-02-07 | |
| PCT/US2007/023881 WO2008063511A2 (en) | 2006-11-13 | 2007-11-13 | Methods for treating pompe disease |
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| JP2010509344A true JP2010509344A (ja) | 2010-03-25 |
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| EP (1) | EP2099523A2 (https=) |
| JP (1) | JP2010509344A (https=) |
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| CA (1) | CA2669347A1 (https=) |
| IL (1) | IL198692A0 (https=) |
| WO (1) | WO2008063511A2 (https=) |
Cited By (2)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| JP2014513952A (ja) * | 2011-04-22 | 2014-06-19 | ジェンザイム・コーポレーション | 促進されたプロセシングを備えた修飾された酸性アルファグルコシダーゼ |
| WO2023204202A1 (ja) * | 2022-04-19 | 2023-10-26 | Ｊｃｒファーマ株式会社 | マンノース－６－リン酸の数を減少させた糖蛋白質 |
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| EP2932982B1 (en) | 2005-05-17 | 2018-10-03 | Amicus Therapeutics, Inc. | A method for the treatment of pompe disease using 1-deoxynojirimycin and derivatives |
| WO2011028941A2 (en) | 2009-09-04 | 2011-03-10 | The United States Of America, As Represented By The Secretary Department Of Health & Human Services | Disabling autophagy as a treatment for lysosomal storage diseases |
| WO2012061597A1 (en) * | 2010-11-03 | 2012-05-10 | The United States Of America As Represented By The Secretary, Department Of Health And Human Services Office Of Technology Transfer, National Institutes Of Health | Alpha-glucosidase binders and methods of their use |
| KR20200032244A (ko) | 2012-03-07 | 2020-03-25 | 아미쿠스 세라퓨틱스, 인코포레이티드 | 폼페병의 치료를 위한 고농도 알파-글루코시다제 조성물 |
| EP2981551B1 (en) * | 2013-02-20 | 2020-06-03 | Valerion Therapeutics, LLC | Methods and compositions for treatment of pompe disease |
| WO2016054231A1 (en) | 2014-09-30 | 2016-04-07 | Amicus Therapeutics, Inc. | Highly potent acid alpha-glucosidase with enhanced carbohydrates |
| KR102510941B1 (ko) | 2015-12-30 | 2023-03-20 | 아미쿠스 세라퓨틱스, 인코포레이티드 | 폼페병 치료용의 강화된 산 알파-글루코시다제 |
| US10227577B2 (en) | 2016-03-30 | 2019-03-12 | Amicus Therapeutics, Inc. | Method for selection of high M6P recombinant proteins |
| IL325155A (en) | 2016-03-30 | 2026-02-01 | Amicus Therapeutics Inc | Formulations containing recombinant acid alpha-glucosidase |
| EP3624831B1 (en) | 2017-05-15 | 2023-03-29 | Amicus Therapeutics, Inc. | Recombinant human acid alpha-glucosidase |
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| CN114127275A (zh) * | 2019-04-30 | 2022-03-01 | 宾夕法尼亚州大学信托人 | 可用于治疗庞贝病的组合物 |
| EP3871687A1 (en) | 2020-02-27 | 2021-09-01 | eleva GmbH | Enzyme replacement therapy for treating pompe disease |
| KR20230010255A (ko) * | 2020-05-14 | 2023-01-18 | 더 트러스티스 오브 더 유니버시티 오브 펜실베니아 | 폼페병의 치료에 유용한 조성물 |
| TW202542190A (zh) | 2023-12-20 | 2025-11-01 | 美商戴納立製藥公司 | 包含酸性α—葡萄糖苷酶之融合蛋白及其方法 |
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Cited By (2)
| Publication number | Priority date | Publication date | Assignee | Title |
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| JP2014513952A (ja) * | 2011-04-22 | 2014-06-19 | ジェンザイム・コーポレーション | 促進されたプロセシングを備えた修飾された酸性アルファグルコシダーゼ |
| WO2023204202A1 (ja) * | 2022-04-19 | 2023-10-26 | Ｊｃｒファーマ株式会社 | マンノース－６－リン酸の数を減少させた糖蛋白質 |
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| WO2008063511A2 (en) | 2008-05-29 |
| US20120093794A1 (en) | 2012-04-19 |
| US20090117091A1 (en) | 2009-05-07 |
| CA2669347A1 (en) | 2008-05-29 |
| AU2007322123A1 (en) | 2008-05-29 |
| EP2099523A2 (en) | 2009-09-16 |
| WO2008063511A3 (en) | 2009-04-09 |
| IL198692A0 (en) | 2011-07-31 |
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