JP2004535801A5 - - Google Patents

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Publication number
JP2004535801A5
JP2004535801A5 JP2002592469A JP2002592469A JP2004535801A5 JP 2004535801 A5 JP2004535801 A5 JP 2004535801A5 JP 2002592469 A JP2002592469 A JP 2002592469A JP 2002592469 A JP2002592469 A JP 2002592469A JP 2004535801 A5 JP2004535801 A5 JP 2004535801A5
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JP
Japan
Prior art keywords
mck
promoter
amplify
upstream
downstream
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JP2002592469A
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English (en)
Japanese (ja)
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JP2004535801A (ja
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Priority claimed from PCT/US2002/016748 external-priority patent/WO2002095006A2/en
Publication of JP2004535801A publication Critical patent/JP2004535801A/ja
Publication of JP2004535801A5 publication Critical patent/JP2004535801A5/ja
Pending legal-status Critical Current

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JP2002592469A 2001-05-24 2002-05-22 筋特異的発現ベクター Pending JP2004535801A (ja)

Applications Claiming Priority (2)

Application Number Priority Date Filing Date Title
US29330401P 2001-05-24 2001-05-24
PCT/US2002/016748 WO2002095006A2 (en) 2001-05-24 2002-05-22 Muscle-specific expression vectors

Publications (2)

Publication Number Publication Date
JP2004535801A JP2004535801A (ja) 2004-12-02
JP2004535801A5 true JP2004535801A5 (enExample) 2006-01-05

Family

ID=23128549

Family Applications (1)

Application Number Title Priority Date Filing Date
JP2002592469A Pending JP2004535801A (ja) 2001-05-24 2002-05-22 筋特異的発現ベクター

Country Status (7)

Country Link
US (2) US20030100526A1 (enExample)
EP (2) EP1390490B1 (enExample)
JP (1) JP2004535801A (enExample)
AT (1) ATE428777T1 (enExample)
CA (1) CA2448120A1 (enExample)
DE (1) DE60231975D1 (enExample)
WO (1) WO2002095006A2 (enExample)

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CN120665951A (zh) 2018-02-07 2025-09-19 吉尼松公司 杂合调控元件
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MX2020012077A (es) 2018-05-15 2021-03-09 Voyager Therapeutics Inc Composiciones y metodos para el tratamiento de la enfermedad de parkinson.
WO2019222329A1 (en) 2018-05-15 2019-11-21 Voyager Therapeutics, Inc. Compositions and methods for delivery of aav
EP3807404A1 (en) 2018-06-13 2021-04-21 Voyager Therapeutics, Inc. Engineered 5' untranslated regions (5' utr) for aav production
WO2020010042A1 (en) 2018-07-02 2020-01-09 Voyager Therapeutics, Inc. Treatment of amyotrophic lateral sclerosis and disorders associated with the spinal cord
TW202035689A (zh) 2018-10-04 2020-10-01 美商航海家醫療公司 測量病毒載體粒子的效價及強度之方法
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US20210371470A1 (en) 2018-10-12 2021-12-02 Voyager Therapeutics, Inc. Compositions and methods for delivery of aav
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AU2019381460A1 (en) 2018-11-16 2021-06-17 Astellas Pharma Inc. Method for treating muscular dystrophy by targeting Utrophin gene
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US20220333133A1 (en) 2019-09-03 2022-10-20 Voyager Therapeutics, Inc. Vectorized editing of nucleic acids to correct overt mutations
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TW202325263A (zh) 2021-09-14 2023-07-01 美商雷納嘉德醫療管理公司 非環狀脂質及其使用方法
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EP4493705A1 (en) * 2022-03-16 2025-01-22 Rutgers, the State University of New Jersey Controlled muscle-specific gene delivery
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WO1999055564A1 (en) * 1998-04-24 1999-11-04 Univ Florida Materials and methods for gene therapy
WO2001083695A2 (en) * 2000-04-28 2001-11-08 Xiao Xiao Dna sequences encoding dystrophin minigenes and methods of use thereof
WO2001083703A2 (en) * 2000-05-04 2001-11-08 California Institute Of Technology Checkpoint-activating oligonucleotides

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