HUE033431T2 - RNA modulating oligonucleotides with improved characteristics in the treatment of neuromuscular disorders - Google Patents

RNA modulating oligonucleotides with improved characteristics in the treatment of neuromuscular disorders Download PDF

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Publication number
HUE033431T2
HUE033431T2 HUE13720617A HUE13720617A HUE033431T2 HU E033431 T2 HUE033431 T2 HU E033431T2 HU E13720617 A HUE13720617 A HU E13720617A HU E13720617 A HUE13720617 A HU E13720617A HU E033431 T2 HUE033431 T2 HU E033431T2
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misc
feature
methylcytosine
oligonucleotide
nucleotides
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HUE13720617A
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English (en)
Hungarian (hu)
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Visser Peter Christian De
Susan Allegonda Maria Mulders
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Biomarin Tech Bv
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Publication of HUE033431T2 publication Critical patent/HUE033431T2/en

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    • C12N15/113—Non-coding nucleic acids modulating the expression of genes, e.g. antisense oligonucleotides; Antisense DNA or RNA; Triplex- forming oligonucleotides; Catalytic nucleic acids, e.g. ribozymes; Nucleic acids used in co-suppression or gene silencing
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    • A61P21/00—Drugs for disorders of the muscular or neuromuscular system
    • A61P21/02—Muscle relaxants, e.g. for tetanus or cramps
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HUE13720617A 2012-04-23 2013-04-23 RNA modulating oligonucleotides with improved characteristics in the treatment of neuromuscular disorders HUE033431T2 (en)

Applications Claiming Priority (2)

Application Number Priority Date Filing Date Title
US201261636914P 2012-04-23 2012-04-23
EP12165139 2012-04-23

Publications (1)

Publication Number Publication Date
HUE033431T2 true HUE033431T2 (en) 2017-11-28

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HUE13720617A HUE033431T2 (en) 2012-04-23 2013-04-23 RNA modulating oligonucleotides with improved characteristics in the treatment of neuromuscular disorders

Country Status (19)

Country Link
US (5) US9745576B2 (OSRAM)
EP (4) EP2841578B1 (OSRAM)
JP (5) JP6174678B2 (OSRAM)
CN (2) CN104271741A (OSRAM)
AU (1) AU2013253074C1 (OSRAM)
BR (1) BR112014026285B1 (OSRAM)
CA (2) CA2870697C (OSRAM)
DK (1) DK2841578T3 (OSRAM)
ES (2) ES2639066T3 (OSRAM)
HR (1) HRP20171254T1 (OSRAM)
HU (1) HUE033431T2 (OSRAM)
LT (1) LT2841578T (OSRAM)
NZ (1) NZ700561A (OSRAM)
PL (2) PL3604536T3 (OSRAM)
PT (1) PT2841578T (OSRAM)
RS (1) RS56319B1 (OSRAM)
SI (1) SI2841578T1 (OSRAM)
SM (1) SMT201700339T1 (OSRAM)
WO (1) WO2013162363A1 (OSRAM)

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