HK1243727B - 用於治療血紅蛋白病的bcl11a調節 - Google Patents

用於治療血紅蛋白病的bcl11a調節

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Publication number
HK1243727B
HK1243727B HK18102648.2A HK18102648A HK1243727B HK 1243727 B HK1243727 B HK 1243727B HK 18102648 A HK18102648 A HK 18102648A HK 1243727 B HK1243727 B HK 1243727B
Authority
HK
Hong Kong
Prior art keywords
bcl11a
hemoglobinopathies
modulation
treatment
Prior art date
Application number
HK18102648.2A
Other languages
English (en)
Inventor
Stuart H Orkin
Vijay G Sankaran
Original Assignee
Childrens Medical Ct Corp
Harvard College
Priority date (The priority date is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the date listed.)
Filing date
Publication date
Application filed by Childrens Medical Ct Corp, Harvard College filed Critical Childrens Medical Ct Corp
Publication of HK1243727B publication Critical patent/HK1243727B/zh

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HK18102648.2A 2008-09-15 2018-02-23 用於治療血紅蛋白病的bcl11a調節 HK1243727B (zh)

Applications Claiming Priority (2)

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US9701708P 2008-09-15 2008-09-15
US22257109P 2009-07-02 2009-07-02

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HK1243727B true HK1243727B (zh) 2020-01-10

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Country Link
US (5) US8383604B2 (zh)
EP (2) EP3208339B1 (zh)
BR (1) BRPI0919017A2 (zh)
CA (1) CA2737180C (zh)
DK (1) DK2334794T3 (zh)
ES (2) ES2738980T3 (zh)
HK (1) HK1243727B (zh)
MX (2) MX2011002731A (zh)
PT (1) PT2334794T (zh)
WO (1) WO2010030963A2 (zh)
ZA (1) ZA201101964B (zh)

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