GB202013940D0 - Regulatory nucleic acid sequences - Google Patents

Regulatory nucleic acid sequences

Info

Publication number
GB202013940D0
GB202013940D0 GBGB2013940.8A GB202013940A GB202013940D0 GB 202013940 D0 GB202013940 D0 GB 202013940D0 GB 202013940 A GB202013940 A GB 202013940A GB 202013940 D0 GB202013940 D0 GB 202013940D0
Authority
GB
United Kingdom
Prior art keywords
nucleic acid
acid sequences
regulatory nucleic
regulatory
sequences
Prior art date
Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
Ceased
Application number
GBGB2013940.8A
Other languages
English (en)
Current Assignee (The listed assignees may be inaccurate. Google has not performed a legal analysis and makes no representation or warranty as to the accuracy of the list.)
AskBio UK Ltd
Original Assignee
Synpromics Ltd
Priority date (The priority date is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the date listed.)
Filing date
Publication date
Application filed by Synpromics Ltd filed Critical Synpromics Ltd
Priority to GBGB2013940.8A priority Critical patent/GB202013940D0/en
Publication of GB202013940D0 publication Critical patent/GB202013940D0/en
Priority to US18/024,211 priority patent/US20230321279A1/en
Priority to AU2021336754A priority patent/AU2021336754A1/en
Priority to CA3193489A priority patent/CA3193489A1/en
Priority to CN202180072951.8A priority patent/CN116457026A/zh
Priority to JP2023514994A priority patent/JP2023540545A/ja
Priority to PCT/GB2021/052273 priority patent/WO2022049385A1/en
Priority to EP21778528.6A priority patent/EP4208207A1/en
Ceased legal-status Critical Current

Links

Classifications

    • A—HUMAN NECESSITIES
    • A61—MEDICAL OR VETERINARY SCIENCE; HYGIENE
    • A61K—PREPARATIONS FOR MEDICAL, DENTAL OR TOILETRY PURPOSES
    • A61K48/00—Medicinal preparations containing genetic material which is inserted into cells of the living body to treat genetic diseases; Gene therapy
    • A61K48/005—Medicinal preparations containing genetic material which is inserted into cells of the living body to treat genetic diseases; Gene therapy characterised by an aspect of the 'active' part of the composition delivered, i.e. the nucleic acid delivered
    • A61K48/0058—Nucleic acids adapted for tissue specific expression, e.g. having tissue specific promoters as part of a contruct
    • C—CHEMISTRY; METALLURGY
    • C07—ORGANIC CHEMISTRY
    • C07K—PEPTIDES
    • C07K14/00—Peptides having more than 20 amino acids; Gastrins; Somatostatins; Melanotropins; Derivatives thereof
    • C07K14/435—Peptides having more than 20 amino acids; Gastrins; Somatostatins; Melanotropins; Derivatives thereof from animals; from humans
    • C07K14/46—Peptides having more than 20 amino acids; Gastrins; Somatostatins; Melanotropins; Derivatives thereof from animals; from humans from vertebrates
    • C07K14/47—Peptides having more than 20 amino acids; Gastrins; Somatostatins; Melanotropins; Derivatives thereof from animals; from humans from vertebrates from mammals
    • C—CHEMISTRY; METALLURGY
    • C12—BIOCHEMISTRY; BEER; SPIRITS; WINE; VINEGAR; MICROBIOLOGY; ENZYMOLOGY; MUTATION OR GENETIC ENGINEERING
    • C12N—MICROORGANISMS OR ENZYMES; COMPOSITIONS THEREOF; PROPAGATING, PRESERVING, OR MAINTAINING MICROORGANISMS; MUTATION OR GENETIC ENGINEERING; CULTURE MEDIA
    • C12N15/00—Mutation or genetic engineering; DNA or RNA concerning genetic engineering, vectors, e.g. plasmids, or their isolation, preparation or purification; Use of hosts therefor
    • C12N15/09—Recombinant DNA-technology
    • C12N15/63—Introduction of foreign genetic material using vectors; Vectors; Use of hosts therefor; Regulation of expression
    • C12N15/79—Vectors or expression systems specially adapted for eukaryotic hosts
    • C12N15/85—Vectors or expression systems specially adapted for eukaryotic hosts for animal cells
    • C12N15/86—Viral vectors
    • C—CHEMISTRY; METALLURGY
    • C12—BIOCHEMISTRY; BEER; SPIRITS; WINE; VINEGAR; MICROBIOLOGY; ENZYMOLOGY; MUTATION OR GENETIC ENGINEERING
    • C12N—MICROORGANISMS OR ENZYMES; COMPOSITIONS THEREOF; PROPAGATING, PRESERVING, OR MAINTAINING MICROORGANISMS; MUTATION OR GENETIC ENGINEERING; CULTURE MEDIA
    • C12N9/00—Enzymes; Proenzymes; Compositions thereof; Processes for preparing, activating, inhibiting, separating or purifying enzymes
    • C12N9/0004—Oxidoreductases (1.)
    • C12N9/0071—Oxidoreductases (1.) acting on paired donors with incorporation of molecular oxygen (1.14)
    • C—CHEMISTRY; METALLURGY
    • C12—BIOCHEMISTRY; BEER; SPIRITS; WINE; VINEGAR; MICROBIOLOGY; ENZYMOLOGY; MUTATION OR GENETIC ENGINEERING
    • C12Y—ENZYMES
    • C12Y114/00—Oxidoreductases acting on paired donors, with incorporation or reduction of molecular oxygen (1.14)
    • C12Y114/14—Oxidoreductases acting on paired donors, with incorporation or reduction of molecular oxygen (1.14) with reduced flavin or flavoprotein as one donor, and incorporation of one atom of oxygen (1.14.14)
    • C—CHEMISTRY; METALLURGY
    • C12—BIOCHEMISTRY; BEER; SPIRITS; WINE; VINEGAR; MICROBIOLOGY; ENZYMOLOGY; MUTATION OR GENETIC ENGINEERING
    • C12N—MICROORGANISMS OR ENZYMES; COMPOSITIONS THEREOF; PROPAGATING, PRESERVING, OR MAINTAINING MICROORGANISMS; MUTATION OR GENETIC ENGINEERING; CULTURE MEDIA
    • C12N2750/00—MICROORGANISMS OR ENZYMES; COMPOSITIONS THEREOF; PROPAGATING, PRESERVING, OR MAINTAINING MICROORGANISMS; MUTATION OR GENETIC ENGINEERING; CULTURE MEDIA ssDNA viruses
    • C12N2750/00011—Details
    • C12N2750/14011—Parvoviridae
    • C12N2750/14111—Dependovirus, e.g. adenoassociated viruses
    • C12N2750/14141—Use of virus, viral particle or viral elements as a vector
    • C12N2750/14143—Use of virus, viral particle or viral elements as a vector viral genome or elements thereof as genetic vector
    • C—CHEMISTRY; METALLURGY
    • C12—BIOCHEMISTRY; BEER; SPIRITS; WINE; VINEGAR; MICROBIOLOGY; ENZYMOLOGY; MUTATION OR GENETIC ENGINEERING
    • C12N—MICROORGANISMS OR ENZYMES; COMPOSITIONS THEREOF; PROPAGATING, PRESERVING, OR MAINTAINING MICROORGANISMS; MUTATION OR GENETIC ENGINEERING; CULTURE MEDIA
    • C12N2830/00—Vector systems having a special element relevant for transcription
    • C12N2830/008—Vector systems having a special element relevant for transcription cell type or tissue specific enhancer/promoter combination

Landscapes

  • Health & Medical Sciences (AREA)
  • Life Sciences & Earth Sciences (AREA)
  • Chemical & Material Sciences (AREA)
  • Genetics & Genomics (AREA)
  • Engineering & Computer Science (AREA)
  • Organic Chemistry (AREA)
  • Zoology (AREA)
  • Bioinformatics & Cheminformatics (AREA)
  • Wood Science & Technology (AREA)
  • Biotechnology (AREA)
  • Biomedical Technology (AREA)
  • Biochemistry (AREA)
  • General Health & Medical Sciences (AREA)
  • Molecular Biology (AREA)
  • General Engineering & Computer Science (AREA)
  • Medicinal Chemistry (AREA)
  • Microbiology (AREA)
  • Biophysics (AREA)
  • Animal Behavior & Ethology (AREA)
  • Physics & Mathematics (AREA)
  • Plant Pathology (AREA)
  • Virology (AREA)
  • Veterinary Medicine (AREA)
  • Public Health (AREA)
  • Pharmacology & Pharmacy (AREA)
  • Epidemiology (AREA)
  • Toxicology (AREA)
  • Proteomics, Peptides & Aminoacids (AREA)
  • Gastroenterology & Hepatology (AREA)
  • Micro-Organisms Or Cultivation Processes Thereof (AREA)
  • Medicines That Contain Protein Lipid Enzymes And Other Medicines (AREA)
  • Medicines Containing Material From Animals Or Micro-Organisms (AREA)
  • Pharmaceuticals Containing Other Organic And Inorganic Compounds (AREA)
GBGB2013940.8A 2020-09-04 2020-09-04 Regulatory nucleic acid sequences Ceased GB202013940D0 (en)

Priority Applications (8)

Application Number Priority Date Filing Date Title
GBGB2013940.8A GB202013940D0 (en) 2020-09-04 2020-09-04 Regulatory nucleic acid sequences
US18/024,211 US20230321279A1 (en) 2020-09-04 2021-09-03 Regulatory nucleic acid sequences
AU2021336754A AU2021336754A1 (en) 2020-09-04 2021-09-03 Regulatory nucleic acid sequences
CA3193489A CA3193489A1 (en) 2020-09-04 2021-09-03 Regulatory nucleic acid sequences
CN202180072951.8A CN116457026A (zh) 2020-09-04 2021-09-03 调节核酸序列
JP2023514994A JP2023540545A (ja) 2020-09-04 2021-09-03 調節核酸配列
PCT/GB2021/052273 WO2022049385A1 (en) 2020-09-04 2021-09-03 Regulatory nucleic acid sequences
EP21778528.6A EP4208207A1 (en) 2020-09-04 2021-09-03 Regulatory nucleic acid sequences

Applications Claiming Priority (1)

Application Number Priority Date Filing Date Title
GBGB2013940.8A GB202013940D0 (en) 2020-09-04 2020-09-04 Regulatory nucleic acid sequences

Publications (1)

Publication Number Publication Date
GB202013940D0 true GB202013940D0 (en) 2020-10-21

Family

ID=72841262

Family Applications (1)

Application Number Title Priority Date Filing Date
GBGB2013940.8A Ceased GB202013940D0 (en) 2020-09-04 2020-09-04 Regulatory nucleic acid sequences

Country Status (8)

Country Link
US (1) US20230321279A1 (enExample)
EP (1) EP4208207A1 (enExample)
JP (1) JP2023540545A (enExample)
CN (1) CN116457026A (enExample)
AU (1) AU2021336754A1 (enExample)
CA (1) CA3193489A1 (enExample)
GB (1) GB202013940D0 (enExample)
WO (1) WO2022049385A1 (enExample)

Families Citing this family (1)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
CN119256090A (zh) * 2022-03-25 2025-01-03 阿斯克肋匹奥生物制药公司 用于治疗帕金森病的方法和组合物

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Also Published As

Publication number Publication date
CA3193489A1 (en) 2022-03-10
JP2023540545A (ja) 2023-09-25
WO2022049385A1 (en) 2022-03-10
US20230321279A1 (en) 2023-10-12
AU2021336754A1 (en) 2023-04-06
EP4208207A1 (en) 2023-07-12
CN116457026A (zh) 2023-07-18

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