ES2639066T3 - Oligonucleótidos de modulación de ARN con características mejoradas para el tratamiento de trastornos neuromusculares - Google Patents

Oligonucleótidos de modulación de ARN con características mejoradas para el tratamiento de trastornos neuromusculares Download PDF

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ES2639066T3
ES2639066T3 ES13720617.3T ES13720617T ES2639066T3 ES 2639066 T3 ES2639066 T3 ES 2639066T3 ES 13720617 T ES13720617 T ES 13720617T ES 2639066 T3 ES2639066 T3 ES 2639066T3
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oligonucleotide
nucleotides
seq
preferred
rna
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Peter Christian De Visser
Susan Allegonda Maria MULDERS
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Biomarin Technologies BV
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Biomarin Technologies BV
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    • C12N15/113—Non-coding nucleic acids modulating the expression of genes, e.g. antisense oligonucleotides; Antisense DNA or RNA; Triplex- forming oligonucleotides; Catalytic nucleic acids, e.g. ribozymes; Nucleic acids used in co-suppression or gene silencing
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ES13720617.3T 2012-04-23 2013-04-23 Oligonucleótidos de modulación de ARN con características mejoradas para el tratamiento de trastornos neuromusculares Active ES2639066T3 (es)

Applications Claiming Priority (5)

Application Number Priority Date Filing Date Title
US201261636914P 2012-04-23 2012-04-23
US201261636914P 2012-04-23
EP12165139 2012-04-23
EP12165139 2012-04-23
PCT/NL2013/050306 WO2013162363A1 (en) 2012-04-23 2013-04-23 RNA modulating oligonucleotides with improved characteristics for the treatment of neuromuscular disorders

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ES13720617.3T Active ES2639066T3 (es) 2012-04-23 2013-04-23 Oligonucleótidos de modulación de ARN con características mejoradas para el tratamiento de trastornos neuromusculares
ES19194127T Active ES2983421T3 (es) 2012-04-23 2013-04-23 Oligonucleótidos moduladores de ARN con características mejoradas para el tratamiento de trastornos neuromusculares

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ES19194127T Active ES2983421T3 (es) 2012-04-23 2013-04-23 Oligonucleótidos moduladores de ARN con características mejoradas para el tratamiento de trastornos neuromusculares

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US (5) US9745576B2 (https=)
EP (4) EP2841578B1 (https=)
JP (5) JP6174678B2 (https=)
CN (2) CN110025628B (https=)
AU (1) AU2013253074C1 (https=)
BR (1) BR112014026285B1 (https=)
CA (2) CA2870697C (https=)
DK (1) DK2841578T3 (https=)
ES (2) ES2639066T3 (https=)
HR (1) HRP20171254T1 (https=)
HU (1) HUE033431T2 (https=)
LT (1) LT2841578T (https=)
NZ (1) NZ700561A (https=)
PL (2) PL2841578T3 (https=)
PT (1) PT2841578T (https=)
RS (1) RS56319B1 (https=)
SI (1) SI2841578T1 (https=)
SM (1) SMT201700339T1 (https=)
WO (1) WO2013162363A1 (https=)

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