ES2599401T3 - Tratamiento de glucogenosis de tipo II - Google Patents
Tratamiento de glucogenosis de tipo II Download PDFInfo
- Publication number
- ES2599401T3 ES2599401T3 ES14167882.1T ES14167882T ES2599401T3 ES 2599401 T3 ES2599401 T3 ES 2599401T3 ES 14167882 T ES14167882 T ES 14167882T ES 2599401 T3 ES2599401 T3 ES 2599401T3
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- Prior art keywords
- glucosidase
- human
- gaa
- glycogenosis
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Classifications
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- A61P3/08—Drugs for disorders of the metabolism for glucose homeostasis
- A61P3/10—Drugs for disorders of the metabolism for glucose homeostasis for hyperglycaemia, e.g. antidiabetics
-
- A—HUMAN NECESSITIES
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- A61P37/00—Drugs for immunological or allergic disorders
- A61P37/02—Immunomodulators
- A61P37/06—Immunosuppressants, e.g. drugs for graft rejection
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- A—HUMAN NECESSITIES
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- A—HUMAN NECESSITIES
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- A—HUMAN NECESSITIES
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- A61P9/00—Drugs for disorders of the cardiovascular system
- A61P9/02—Non-specific cardiovascular stimulants, e.g. drugs for syncope, antihypotensives
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- A61P9/00—Drugs for disorders of the cardiovascular system
- A61P9/04—Inotropic agents, i.e. stimulants of cardiac contraction; Drugs for heart failure
-
- C—CHEMISTRY; METALLURGY
- C12—BIOCHEMISTRY; BEER; SPIRITS; WINE; VINEGAR; MICROBIOLOGY; ENZYMOLOGY; MUTATION OR GENETIC ENGINEERING
- C12Y—ENZYMES
- C12Y302/00—Hydrolases acting on glycosyl compounds, i.e. glycosylases (3.2)
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Landscapes
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- Life Sciences & Earth Sciences (AREA)
- Chemical & Material Sciences (AREA)
- Engineering & Computer Science (AREA)
- Bioinformatics & Cheminformatics (AREA)
- General Health & Medical Sciences (AREA)
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- Animal Behavior & Ethology (AREA)
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- Nuclear Medicine, Radiotherapy & Molecular Imaging (AREA)
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- General Chemical & Material Sciences (AREA)
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- Diabetes (AREA)
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- Biochemistry (AREA)
- Hematology (AREA)
- Obesity (AREA)
- Emergency Medicine (AREA)
- Physical Education & Sports Medicine (AREA)
- Orthopedic Medicine & Surgery (AREA)
- Neurology (AREA)
- Endocrinology (AREA)
- Hospice & Palliative Care (AREA)
- Transplantation (AREA)
- Medicines That Contain Protein Lipid Enzymes And Other Medicines (AREA)
- Pharmaceuticals Containing Other Organic And Inorganic Compounds (AREA)
- Saccharide Compounds (AREA)
- Medicines Containing Material From Animals Or Micro-Organisms (AREA)
Applications Claiming Priority (2)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| US21923700P | 2000-07-18 | 2000-07-18 | |
| US219237P | 2000-07-18 |
Publications (1)
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|---|---|
| ES2599401T3 true ES2599401T3 (es) | 2017-02-01 |
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| ES16178390T Expired - Lifetime ES2700865T3 (es) | 2000-07-18 | 2001-07-10 | Tratamiento de glucogenosis de tipo II |
| ES07001091.3T Expired - Lifetime ES2523024T3 (es) | 2000-07-18 | 2001-07-10 | Tratamiento de glucogenosis de tipo II |
| ES01951000T Expired - Lifetime ES2277931T3 (es) | 2000-07-18 | 2001-07-10 | Tratamiento de la glucogenesis de tipo ii. |
| ES18194771T Expired - Lifetime ES2799882T3 (es) | 2000-07-18 | 2001-07-10 | Tratamiento de glucogenosis de tipo II |
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| Application Number | Title | Priority Date | Filing Date |
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| ES16178390T Expired - Lifetime ES2700865T3 (es) | 2000-07-18 | 2001-07-10 | Tratamiento de glucogenosis de tipo II |
| ES07001091.3T Expired - Lifetime ES2523024T3 (es) | 2000-07-18 | 2001-07-10 | Tratamiento de glucogenosis de tipo II |
| ES01951000T Expired - Lifetime ES2277931T3 (es) | 2000-07-18 | 2001-07-10 | Tratamiento de la glucogenesis de tipo ii. |
| ES18194771T Expired - Lifetime ES2799882T3 (es) | 2000-07-18 | 2001-07-10 | Tratamiento de glucogenosis de tipo II |
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| Country | Link |
|---|---|
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| EP (4) | EP3449934B1 (enExample) |
| JP (10) | JP5113312B2 (enExample) |
| AT (1) | ATE355075T1 (enExample) |
| AU (3) | AU7194101A (enExample) |
| BR (1) | BR0113006A (enExample) |
| CA (1) | CA2416492C (enExample) |
| CY (2) | CY1120977T1 (enExample) |
| DE (1) | DE60126947T2 (enExample) |
| DK (5) | DK1782825T3 (enExample) |
| ES (5) | ES2599401T3 (enExample) |
| LT (3) | LT2767291T (enExample) |
| MX (1) | MXPA03000474A (enExample) |
| PT (5) | PT3108895T (enExample) |
| SI (3) | SI3108895T1 (enExample) |
| TW (1) | TWI280882B (enExample) |
| WO (1) | WO2002005841A1 (enExample) |
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| Publication number | Priority date | Publication date | Assignee | Title |
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| US7056712B2 (en) * | 2000-07-18 | 2006-06-06 | Duke University | Treatment of glycogen storage disease type II |
| US7629309B2 (en) * | 2002-05-29 | 2009-12-08 | Zystor Therapeutics, Inc. | Targeted therapeutic proteins |
| US20040005309A1 (en) * | 2002-05-29 | 2004-01-08 | Symbiontics, Inc. | Targeted therapeutic proteins |
| EP1436316B1 (en) * | 2001-04-30 | 2008-01-23 | ZyStor Therapeutics , Inc. | Subcellular targeting of therapeutic proteins |
| US7560424B2 (en) | 2001-04-30 | 2009-07-14 | Zystor Therapeutics, Inc. | Targeted therapeutic proteins |
| US6981964B2 (en) | 2001-05-22 | 2006-01-03 | Boston Scientific Scimed, Inc. | Draining bodily fluids with a stent |
| US20030072761A1 (en) * | 2001-10-16 | 2003-04-17 | Lebowitz Jonathan | Methods and compositions for targeting proteins across the blood brain barrier |
| US6733536B1 (en) | 2002-10-22 | 2004-05-11 | Scimed Life Systems | Male urethral stent device |
| PT1587923E (pt) | 2003-01-22 | 2011-12-07 | Univ Duke | Construções melhoradas para a expressão de polipéptidos lisossomais |
| US7442372B2 (en) | 2003-08-29 | 2008-10-28 | Biomarin Pharmaceutical Inc. | Delivery of therapeutic compounds to the brain and other tissues |
| US7129049B2 (en) * | 2003-12-22 | 2006-10-31 | Regents Of The University Of Minnesota | Method of detecting equine glycogen storage disease IV |
| DE602005020745D1 (de) * | 2004-02-10 | 2010-06-02 | Zystor Therapeutics Inc | Saure alpha-glukosidase und fragmente davon |
| US20050208090A1 (en) * | 2004-03-18 | 2005-09-22 | Medtronic, Inc. | Methods and systems for treatment of neurological diseases of the central nervous system |
| EP1773401B1 (en) * | 2004-06-21 | 2013-01-02 | Medtronic, Inc. | Medical systems and methods for delivering compositions to cells |
| AU2007322123A1 (en) * | 2006-11-13 | 2008-05-29 | Biomarin Pharmaceutical Inc. | Methods for treating Pompe disease |
| WO2009075815A1 (en) | 2007-12-07 | 2009-06-18 | Duke University | Immunomodulating gene therapy |
| WO2009137721A2 (en) | 2008-05-07 | 2009-11-12 | Zystor Therapeutics, Inc. | Lysosomal targeting peptides and uses thereof |
| US9050333B2 (en) | 2008-07-08 | 2015-06-09 | Duke University | Method of treating glycogen storage disease type III with human acid α-glucosidase |
| US8785168B2 (en) | 2009-06-17 | 2014-07-22 | Biomarin Pharmaceutical Inc. | Formulations for lysosomal enzymes |
| US8809282B2 (en) | 2010-05-06 | 2014-08-19 | Duke University | Method of reducing titers of antibodies specific for a therapeutic agent |
| JP2016514096A (ja) | 2013-02-20 | 2016-05-19 | バレリオン セラピューティクス， エルエルシー | ポンぺ病の処置のための方法および組成物 |
| JP2016523835A (ja) * | 2013-05-15 | 2016-08-12 | リージェンツ オブ ザ ユニバーシティ オブ ミネソタ | 中枢神経系へのアデノ随伴ウイルスを介した遺伝子導入 |
| JP6851964B2 (ja) | 2014-09-30 | 2021-03-31 | アミカス セラピューティックス インコーポレイテッド | 炭水化物が増大している非常に強力な酸性アルファ−グルコシダーゼ |
| WO2016178431A1 (ja) * | 2015-05-07 | 2016-11-10 | 国立大学法人 東京大学 | ポリイオンコンプレックス型ポリマーソームを用いたナノリアクタとその製造方法 |
| EP3344337A4 (en) * | 2015-08-31 | 2019-03-06 | Duke University | METHOD AND COMPOSITIONS FOR TREATING CYTOPLASMATIC GLYCOGEN MEMORY DISEASES |
| US10940125B2 (en) | 2015-09-18 | 2021-03-09 | Duke University | Methods and compositions for the treatment of steatosis-associated disorders |
| IL299470B2 (en) | 2015-12-30 | 2026-05-01 | Amicus Therapeutics Inc | Improved acid alpha-glucosidase for the treatment of Pompe disease |
| KR102618519B1 (ko) | 2016-03-30 | 2023-12-28 | 아미쿠스 세라퓨틱스, 인코포레이티드 | 재조합 산 알파-글루코시다제를 포함하는 제형 |
| CA3019354A1 (en) | 2016-03-30 | 2017-10-05 | Amicus Therapeutics, Inc. | Method for selection of high m6p recombinant proteins |
| US11253612B2 (en) | 2016-04-15 | 2022-02-22 | The Trustees Of The University Of Pennsylvania | Gene therapy for treating mucopolysaccharidosis type II |
| CN119113091A (zh) | 2017-05-15 | 2024-12-13 | 阿米库斯治疗学公司 | 重组人类酸性α-葡萄糖苷酶 |
| EP3684938A1 (en) | 2017-09-22 | 2020-07-29 | The Trustees of the University of Pennsylvania | Gene therapy for treating mucopolysaccharidosis type ii |
| WO2020163480A1 (en) * | 2019-02-05 | 2020-08-13 | Amicus Therapeutics, Inc. | Recombinant human acid alpha-glucosidase and uses thereof |
| IT202300005733A1 (it) * | 2023-03-27 | 2024-09-27 | St Microelectronics Int Nv | Circuito di comunicazione, sistema e procedimento corrispondenti |
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| US3063911A (en) * | 1961-04-03 | 1962-11-13 | Taisho Pharmaceutical Co Ltd | Acid-stable digestive enzyme preparation and process of making same |
| US5464778A (en) | 1989-03-08 | 1995-11-07 | Board Of Regents Of The University Of Oklahoma | Glycoprotein ligand for P-selectin and methods of use thereof |
| US5356804A (en) * | 1990-10-24 | 1994-10-18 | Mount Sinai School Of Medicine Of The City Of New York | Cloning and expression of biologically active human α-galactosidase A |
| US6118045A (en) | 1995-08-02 | 2000-09-12 | Pharming B.V. | Lysosomal proteins produced in the milk of transgenic animals |
| WO1999058691A2 (en) | 1998-05-13 | 1999-11-18 | Harbor-Ucla | Recombinant (alpha)-l-iduronidase, methods for producing and purifying the same and methods for treating diseases caused by deficiencies thereof |
| DK2020438T3 (en) | 1998-12-07 | 2018-07-23 | Genzyme Corp | Treatment of Pompe disease |
| US6534300B1 (en) | 1999-09-14 | 2003-03-18 | Genzyme Glycobiology Research Institute, Inc. | Methods for producing highly phosphorylated lysosomal hydrolases |
| US7056712B2 (en) * | 2000-07-18 | 2006-06-06 | Duke University | Treatment of glycogen storage disease type II |
| US7629309B2 (en) | 2002-05-29 | 2009-12-08 | Zystor Therapeutics, Inc. | Targeted therapeutic proteins |
| DE602005020745D1 (de) * | 2004-02-10 | 2010-06-02 | Zystor Therapeutics Inc | Saure alpha-glukosidase und fragmente davon |
| US8470552B2 (en) | 2009-10-12 | 2013-06-25 | Keck Graduate Institute | Strategy to reduce lactic acid production and control PH in animal cell culture |
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2001
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- 2001-07-10 EP EP18194771.4A patent/EP3449934B1/en not_active Expired - Lifetime
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- 2001-07-10 PT PT181947714T patent/PT3449934T/pt unknown
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- 2001-07-10 DK DK07001091.3T patent/DK1782825T3/da active
- 2001-07-10 PT PT01951000T patent/PT1301201E/pt unknown
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- 2001-07-10 PT PT70010913T patent/PT1782825E/pt unknown
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- 2001-07-10 DK DK14167882.1T patent/DK2767291T3/en active
- 2001-07-10 DK DK16178390.7T patent/DK3108895T3/en active
- 2001-07-10 EP EP16178390.7A patent/EP3108895B1/en not_active Expired - Lifetime
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- 2001-07-10 EP EP01951000A patent/EP1301201B1/en not_active Revoked
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- 2001-07-10 DK DK01951000T patent/DK1301201T3/da active
- 2001-07-10 SI SI200131073T patent/SI3449934T1/sl unknown
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2005
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2007
- 2007-08-13 US US11/889,457 patent/US20080175833A1/en not_active Abandoned
- 2007-12-03 JP JP2007312804A patent/JP2008081507A/ja active Pending
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2009
- 2009-10-22 US US12/604,267 patent/US20100254966A1/en not_active Abandoned
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2010
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2011
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2012
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2013
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2014
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2016
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-
2017
- 2017-05-19 JP JP2017099515A patent/JP2017137357A/ja active Pending
- 2017-10-17 JP JP2017201250A patent/JP2018002749A/ja active Pending
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2018
- 2018-01-19 US US15/876,086 patent/US10792341B2/en not_active Expired - Fee Related
- 2018-09-13 JP JP2018171154A patent/JP2018199721A/ja active Pending
- 2018-12-07 CY CY181101308T patent/CY1120977T1/el unknown
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2019
- 2019-11-08 JP JP2019202851A patent/JP2020019822A/ja active Pending
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2020
- 2020-06-24 CY CY20201100587T patent/CY1123084T1/el unknown
- 2020-07-27 US US16/940,054 patent/US20210169996A1/en not_active Abandoned
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