EA038966B1 - Лентивирусный вектор для генной терапии, способ его получения и его применение - Google Patents
Лентивирусный вектор для генной терапии, способ его получения и его применение Download PDFInfo
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- EA038966B1 EA038966B1 EA201692361A EA201692361A EA038966B1 EA 038966 B1 EA038966 B1 EA 038966B1 EA 201692361 A EA201692361 A EA 201692361A EA 201692361 A EA201692361 A EA 201692361A EA 038966 B1 EA038966 B1 EA 038966B1
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| JP2018174874A (ja) * | 2017-04-19 | 2018-11-15 | 国立大学法人 東京医科歯科大学 | 上皮細胞の水分泌機能測定方法 |
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| EP3775236A1 (en) | 2018-04-12 | 2021-02-17 | Krystal Biotech, LLC | Compositions and methods for the treatment of autosomal recessive congenital ichthyosis |
| MX2020011257A (es) | 2018-04-27 | 2021-01-15 | Krystal Biotech Inc | Ácidos nucleicos recombinantes que codifican una o más proteínas cosméticas para usos estéticos. |
| WO2020009444A1 (ko) * | 2018-07-02 | 2020-01-09 | 서울대학교산학협력단 | 세포융합 기술을 이용한 유전자 및 세포 치료제 및 이의 용도 |
| CN112384247B (zh) * | 2018-07-02 | 2024-09-27 | 库拉米斯公司 | 利用细胞融合技术的基因及细胞治疗剂以及其的用途 |
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| CN113454105A (zh) | 2019-02-08 | 2021-09-28 | 克里斯托生物技术股份有限公司 | 用于递送cftr多肽的组合物和方法 |
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| CN112575034B (zh) * | 2019-09-29 | 2023-04-25 | 济南赛尔生物科技股份有限公司 | 一种治疗a型血友病的产品及应用 |
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| US20230190871A1 (en) | 2020-05-20 | 2023-06-22 | Sana Biotechnology, Inc. | Methods and compositions for treatment of viral infections |
| EP4162036A1 (en) | 2020-06-09 | 2023-04-12 | Inozyme Pharma, Inc. | Soluble enpp1 or enpp3 proteins and uses thereof |
| JP2023537565A (ja) * | 2020-06-24 | 2023-09-04 | バイオベラティブ セラピューティクス インコーポレイテッド | タンパク質を発現するように改変されたレンチウイルスベクターの調製物から遊離第ｖｉｉｉ因子を除去する方法 |
| WO2022047316A1 (en) | 2020-08-28 | 2022-03-03 | Sana Biotechnology, Inc. | Modified anti-viral binding agents |
| CA3191743A1 (en) * | 2020-09-16 | 2022-03-24 | Generation Bio Co. | Non-viral dna vectors and uses thereof for expressing fviii therapeutics |
| GB202100688D0 (en) * | 2021-01-19 | 2021-03-03 | Autolus Ltd | Process |
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| WO2024044655A1 (en) | 2022-08-24 | 2024-02-29 | Sana Biotechnology, Inc. | Delivery of heterologous proteins |
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| WO2024057315A1 (en) | 2022-09-15 | 2024-03-21 | Yeda Research And Development Co. Ltd. | Compositions and methods for virotherapy |
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| LT3145949T (lt) | 2020-08-25 |
| JP2017521049A (ja) | 2017-08-03 |
| CA2947125C (en) | 2023-02-28 |
| GB201409089D0 (en) | 2014-07-02 |
| US20170096684A1 (en) | 2017-04-06 |
| SMT202000360T1 (it) | 2020-09-10 |
| EP3145949A1 (en) | 2017-03-29 |
| PT3145949T (pt) | 2020-07-13 |
| CA2947125A1 (en) | 2015-11-26 |
| DK3145949T3 (da) | 2020-06-29 |
| EP3145949B1 (en) | 2020-04-08 |
| JP6637444B2 (ja) | 2020-01-29 |
| CY1123413T1 (el) | 2021-12-31 |
| ES2805045T3 (es) | 2021-02-10 |
| PL3145949T3 (pl) | 2021-01-25 |
| AU2015263150A1 (en) | 2016-11-10 |
| HUE051269T2 (hu) | 2021-03-01 |
| AU2015263150B2 (en) | 2020-04-16 |
| SI3145949T1 (sl) | 2020-08-31 |
| WO2015177501A1 (en) | 2015-11-26 |
| EA201692361A1 (ru) | 2017-05-31 |
| GB2526339A (en) | 2015-11-25 |
| HRP20200930T1 (hr) | 2020-09-18 |
| US10704061B2 (en) | 2020-07-07 |
| ME03789B (me) | 2021-04-20 |
| RS60586B1 (sr) | 2020-08-31 |
| UA122127C2 (uk) | 2020-09-25 |
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