DK2961420T3 - Fremgangsmåder og sammensætninger til forebyggelsen eller behandlingen af barth syndrom - Google Patents
Fremgangsmåder og sammensætninger til forebyggelsen eller behandlingen af barth syndrom Download PDFInfo
- Publication number
- DK2961420T3 DK2961420T3 DK14756991.7T DK14756991T DK2961420T3 DK 2961420 T3 DK2961420 T3 DK 2961420T3 DK 14756991 T DK14756991 T DK 14756991T DK 2961420 T3 DK2961420 T3 DK 2961420T3
- Authority
- DK
- Denmark
- Prior art keywords
- prevention
- compositions
- treatment
- methods
- barth syndrome
- Prior art date
Links
Classifications
-
- A—HUMAN NECESSITIES
- A61—MEDICAL OR VETERINARY SCIENCE; HYGIENE
- A61K—PREPARATIONS FOR MEDICAL, DENTAL OR TOILETRY PURPOSES
- A61K38/00—Medicinal preparations containing peptides
- A61K38/04—Peptides having up to 20 amino acids in a fully defined sequence; Derivatives thereof
- A61K38/06—Tripeptides
-
- A—HUMAN NECESSITIES
- A61—MEDICAL OR VETERINARY SCIENCE; HYGIENE
- A61K—PREPARATIONS FOR MEDICAL, DENTAL OR TOILETRY PURPOSES
- A61K38/00—Medicinal preparations containing peptides
- A61K38/04—Peptides having up to 20 amino acids in a fully defined sequence; Derivatives thereof
- A61K38/07—Tetrapeptides
-
- A—HUMAN NECESSITIES
- A61—MEDICAL OR VETERINARY SCIENCE; HYGIENE
- A61K—PREPARATIONS FOR MEDICAL, DENTAL OR TOILETRY PURPOSES
- A61K45/00—Medicinal preparations containing active ingredients not provided for in groups A61K31/00 - A61K41/00
- A61K45/06—Mixtures of active ingredients without chemical characterisation, e.g. antiphlogistics and cardiaca
-
- A—HUMAN NECESSITIES
- A61—MEDICAL OR VETERINARY SCIENCE; HYGIENE
- A61P—SPECIFIC THERAPEUTIC ACTIVITY OF CHEMICAL COMPOUNDS OR MEDICINAL PREPARATIONS
- A61P11/00—Drugs for disorders of the respiratory system
-
- A—HUMAN NECESSITIES
- A61—MEDICAL OR VETERINARY SCIENCE; HYGIENE
- A61P—SPECIFIC THERAPEUTIC ACTIVITY OF CHEMICAL COMPOUNDS OR MEDICINAL PREPARATIONS
- A61P21/00—Drugs for disorders of the muscular or neuromuscular system
-
- A—HUMAN NECESSITIES
- A61—MEDICAL OR VETERINARY SCIENCE; HYGIENE
- A61P—SPECIFIC THERAPEUTIC ACTIVITY OF CHEMICAL COMPOUNDS OR MEDICINAL PREPARATIONS
- A61P43/00—Drugs for specific purposes, not provided for in groups A61P1/00-A61P41/00
-
- A—HUMAN NECESSITIES
- A61—MEDICAL OR VETERINARY SCIENCE; HYGIENE
- A61P—SPECIFIC THERAPEUTIC ACTIVITY OF CHEMICAL COMPOUNDS OR MEDICINAL PREPARATIONS
- A61P7/00—Drugs for disorders of the blood or the extracellular fluid
-
- A—HUMAN NECESSITIES
- A61—MEDICAL OR VETERINARY SCIENCE; HYGIENE
- A61P—SPECIFIC THERAPEUTIC ACTIVITY OF CHEMICAL COMPOUNDS OR MEDICINAL PREPARATIONS
- A61P9/00—Drugs for disorders of the cardiovascular system
-
- A—HUMAN NECESSITIES
- A61—MEDICAL OR VETERINARY SCIENCE; HYGIENE
- A61P—SPECIFIC THERAPEUTIC ACTIVITY OF CHEMICAL COMPOUNDS OR MEDICINAL PREPARATIONS
- A61P9/00—Drugs for disorders of the cardiovascular system
- A61P9/04—Inotropic agents, i.e. stimulants of cardiac contraction; Drugs for heart failure
Landscapes
- Health & Medical Sciences (AREA)
- Life Sciences & Earth Sciences (AREA)
- Veterinary Medicine (AREA)
- Animal Behavior & Ethology (AREA)
- Chemical & Material Sciences (AREA)
- Public Health (AREA)
- General Health & Medical Sciences (AREA)
- Medicinal Chemistry (AREA)
- Pharmacology & Pharmacy (AREA)
- Bioinformatics & Cheminformatics (AREA)
- Engineering & Computer Science (AREA)
- Epidemiology (AREA)
- Organic Chemistry (AREA)
- Chemical Kinetics & Catalysis (AREA)
- General Chemical & Material Sciences (AREA)
- Nuclear Medicine, Radiotherapy & Molecular Imaging (AREA)
- Proteomics, Peptides & Aminoacids (AREA)
- Immunology (AREA)
- Gastroenterology & Hepatology (AREA)
- Cardiology (AREA)
- Heart & Thoracic Surgery (AREA)
- Hospice & Palliative Care (AREA)
- Orthopedic Medicine & Surgery (AREA)
- Physical Education & Sports Medicine (AREA)
- Diabetes (AREA)
- Hematology (AREA)
- Pulmonology (AREA)
- Neurology (AREA)
- Medicines That Contain Protein Lipid Enzymes And Other Medicines (AREA)
- Peptides Or Proteins (AREA)
Applications Claiming Priority (4)
Application Number | Priority Date | Filing Date | Title |
---|---|---|---|
US201361771534P | 2013-03-01 | 2013-03-01 | |
US201361771642P | 2013-03-01 | 2013-03-01 | |
US201361839753P | 2013-06-26 | 2013-06-26 | |
PCT/US2014/019622 WO2014134554A1 (en) | 2013-03-01 | 2014-02-28 | Methods and compositions for the prevention or treatment of barth syndrome |
Publications (1)
Publication Number | Publication Date |
---|---|
DK2961420T3 true DK2961420T3 (da) | 2019-10-07 |
Family
ID=51428869
Family Applications (1)
Application Number | Title | Priority Date | Filing Date |
---|---|---|---|
DK14756991.7T DK2961420T3 (da) | 2013-03-01 | 2014-02-28 | Fremgangsmåder og sammensætninger til forebyggelsen eller behandlingen af barth syndrom |
Country Status (9)
Country | Link |
---|---|
US (5) | US9687519B2 (da) |
EP (2) | EP2961420B1 (da) |
JP (4) | JP6518197B2 (da) |
CN (3) | CN115990241A (da) |
CA (1) | CA2916880C (da) |
DK (1) | DK2961420T3 (da) |
ES (1) | ES2750258T3 (da) |
HU (1) | HUE046924T2 (da) |
WO (1) | WO2014134554A1 (da) |
Families Citing this family (8)
Publication number | Priority date | Publication date | Assignee | Title |
---|---|---|---|---|
CN105517533A (zh) | 2013-03-01 | 2016-04-20 | 康德生物医疗技术公司 | 治疗线粒体疾病的方法 |
DK2961420T3 (da) * | 2013-03-01 | 2019-10-07 | Stealth Biotherapeutics Corp | Fremgangsmåder og sammensætninger til forebyggelsen eller behandlingen af barth syndrom |
CA2916977A1 (en) | 2013-06-26 | 2014-12-31 | Stealth Biotherapeutics Corp | Methods and compositions for detecting and diagnosing diseases and conditions |
US9550981B2 (en) | 2014-01-22 | 2017-01-24 | University Of Washington | Modified tafazzin proteins and methods of making and using the same |
EP3230308B1 (en) * | 2014-12-12 | 2019-05-01 | University of Washington | Methods for treating and preventing cardiomyopathy |
WO2018104172A1 (en) | 2016-12-06 | 2018-06-14 | Centre National De La Recherche Scientifique (Cnrs) | Compounds for treating barth syndrome |
WO2018187400A1 (en) | 2017-04-05 | 2018-10-11 | Stealth Biotherapeutics Corp. | Crystalline salt forms of boc-d-arg-dmt-lys-(boc)-phe-nh2 |
US10676506B2 (en) | 2018-01-26 | 2020-06-09 | Stealth Biotherapeutics Corp. | Crystalline bis- and tris-hydrochloride salt of elamipretide |
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US5858784A (en) | 1991-12-17 | 1999-01-12 | The Regents Of The University Of California | Expression of cloned genes in the lung by aerosol- and liposome-based delivery |
US5674534A (en) | 1992-06-11 | 1997-10-07 | Alkermes, Inc. | Composition for sustained release of non-aggregated erythropoietin |
US5716644A (en) | 1992-06-11 | 1998-02-10 | Alkermes, Inc. | Composition for sustained release of non-aggregated erythropoietin |
US5989463A (en) | 1997-09-24 | 1999-11-23 | Alkermes Controlled Therapeutics, Inc. | Methods for fabricating polymer-based controlled release devices |
US6245740B1 (en) | 1998-12-23 | 2001-06-12 | Amgen Inc. | Polyol:oil suspensions for the sustained release of proteins |
US7435578B2 (en) | 2001-08-06 | 2008-10-14 | Vanderbilt University | Device and methods for monitoring the status of at least one cell |
BRPI0105509B8 (pt) | 2001-11-05 | 2021-05-25 | Univ Minas Gerais | formulações do peptídeo angiotensina-(1-7) usando as ciclodextrinas, lipossomas e o polímero plga |
EP3144009A1 (en) | 2003-02-04 | 2017-03-22 | Cornell Research Foundation, Inc. | Uses of aromatic-cationic peptide |
CN101440124B (zh) | 2003-02-04 | 2012-07-18 | 科内尔研究基金会 | 用于防止线粒体通透性改变的方法 |
WO2004069866A1 (en) * | 2003-02-10 | 2004-08-19 | Autogen Research Pty Ltd | Therapeutic molecules |
WO2005023274A1 (en) | 2003-09-05 | 2005-03-17 | Yissum Research Development Company Of The Hebrew University Of Jerusalem | Treatment and prevention of inflammatory disease and mitochondrial dysfunction with high dose selenium |
CA2554166C (en) | 2004-01-23 | 2014-07-29 | Cornell Research Foundation, Inc. | Methods for reducing oxidative damage |
US8500720B2 (en) | 2005-05-09 | 2013-08-06 | Medtronic, Inc | Method and apparatus for treatment of cardiac disorders |
US20070265216A1 (en) * | 2005-10-05 | 2007-11-15 | Gross Richard W | Enhanced medical treatment in diabetic cardiomyopathy |
US20090298848A1 (en) * | 2006-04-18 | 2009-12-03 | Cortendo Invest Ab, | Methods and Compositions for Treating Barth Syndrome, Cardiomyopathy, Mitochondrial Diseases and Other Conditions |
EP2641617A1 (en) | 2007-05-02 | 2013-09-25 | THE McLEAN HOSPITAL CORPORATION | Methods and compositions for mitochondrial replacement therapy |
US20080318909A1 (en) | 2007-06-14 | 2008-12-25 | Sparagna Genevieve C | Use Of Linoleic Compounds Against Heart Failure |
US20090143279A1 (en) | 2007-06-15 | 2009-06-04 | Vamsi Krishna Mootha | Methods and compositions for treating metabolic disorders |
CN101951936A (zh) | 2008-02-26 | 2011-01-19 | 康奈尔大学 | 用于防止和治疗急性肾损伤的方法 |
WO2009149307A2 (en) | 2008-06-04 | 2009-12-10 | San Diego State University Research Foundation | Compositions and methods for restoring mitochondrial electron transfer function |
KR101593158B1 (ko) | 2008-08-07 | 2016-02-12 | 입센 파마 에스.에이.에스. | N-말단이 변형된 포도당 의존적인 인슐린 분비 자극성 폴리펩타이드(gip)의 유사체 |
CN102573881A (zh) | 2009-03-20 | 2012-07-11 | 通用医疗公司以马萨诸塞州通用医疗公司名义经营 | 预防和治疗烧伤损伤和继发性并发症的方法 |
US20120122957A1 (en) | 2009-04-17 | 2012-05-17 | The Salk Institute For Biological Studies | Regulation of aging by modulation of mitochondrial function |
WO2010132347A2 (en) | 2009-05-11 | 2010-11-18 | University Of Maryland, Baltimore | Docosahexaenoic acid for the treatment of heart failure |
CN102647994A (zh) | 2009-08-12 | 2012-08-22 | 康奈尔大学 | 预防或治疗代谢综合症的方法 |
EP2470191B1 (en) * | 2009-08-24 | 2014-05-07 | Stealth Peptides International, Inc. | Methods and compositions for preventing or treating ophthalmic conditions |
CN102711785A (zh) * | 2009-10-05 | 2012-10-03 | 康奈尔大学 | 预防或治疗心力衰竭的方法 |
WO2011082355A1 (en) | 2009-12-31 | 2011-07-07 | Edison Pharmaceuticals, Inc. | Treatment of leigh syndrome and leigh-like syndrome with tocotrienol quinones |
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US9241933B2 (en) | 2011-03-01 | 2016-01-26 | Pharnext | Compositions for treating amyotrophic lateral sclerosis |
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KR20200040924A (ko) * | 2011-10-21 | 2020-04-20 | 스템제닉스 인코포레이티드 | 생물학적 활성 분자의 세포내 전달을 위한 작용화 나노입자 |
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JP2016503397A (ja) * | 2012-10-22 | 2016-02-04 | ステルス ペプチドズ インターナショナル インコーポレイテッド | 心不全関連リスクおよびそれらと関連する因子を減少させる方法 |
CN105517533A (zh) | 2013-03-01 | 2016-04-20 | 康德生物医疗技术公司 | 治疗线粒体疾病的方法 |
DK2961420T3 (da) | 2013-03-01 | 2019-10-07 | Stealth Biotherapeutics Corp | Fremgangsmåder og sammensætninger til forebyggelsen eller behandlingen af barth syndrom |
CA2916977A1 (en) * | 2013-06-26 | 2014-12-31 | Stealth Biotherapeutics Corp | Methods and compositions for detecting and diagnosing diseases and conditions |
-
2014
- 2014-02-28 DK DK14756991.7T patent/DK2961420T3/da active
- 2014-02-28 JP JP2015560377A patent/JP6518197B2/ja active Active
- 2014-02-28 CN CN202211634590.4A patent/CN115990241A/zh active Pending
- 2014-02-28 WO PCT/US2014/019622 patent/WO2014134554A1/en active Application Filing
- 2014-02-28 EP EP14756991.7A patent/EP2961420B1/en active Active
- 2014-02-28 ES ES14756991T patent/ES2750258T3/es active Active
- 2014-02-28 EP EP19190165.1A patent/EP3626252A1/en active Pending
- 2014-02-28 CN CN201480022767.2A patent/CN105407906A/zh active Pending
- 2014-02-28 HU HUE14756991A patent/HUE046924T2/hu unknown
- 2014-02-28 CA CA2916880A patent/CA2916880C/en active Active
- 2014-02-28 CN CN202211635437.3A patent/CN115990242A/zh active Pending
- 2014-02-28 US US14/771,408 patent/US9687519B2/en active Active
-
2017
- 2017-06-19 US US15/626,255 patent/US11083771B2/en active Active
-
2019
- 2019-04-19 JP JP2019080101A patent/JP6918046B2/ja active Active
-
2020
- 2020-07-15 US US16/929,370 patent/US11083772B2/en active Active
-
2021
- 2021-02-10 JP JP2021019903A patent/JP7072692B2/ja active Active
- 2021-07-09 US US17/371,475 patent/US11771734B2/en active Active
-
2022
- 2022-05-10 JP JP2022077425A patent/JP7381652B2/ja active Active
-
2023
- 2023-08-23 US US18/454,319 patent/US20240156892A1/en active Pending
Also Published As
Publication number | Publication date |
---|---|
EP2961420A1 (en) | 2016-01-06 |
US20180147251A1 (en) | 2018-05-31 |
CN115990241A (zh) | 2023-04-21 |
JP2019147815A (ja) | 2019-09-05 |
US11083771B2 (en) | 2021-08-10 |
WO2014134554A1 (en) | 2014-09-04 |
US20160228487A1 (en) | 2016-08-11 |
JP6518197B2 (ja) | 2019-05-22 |
JP2021098704A (ja) | 2021-07-01 |
EP3626252A1 (en) | 2020-03-25 |
CA2916880A1 (en) | 2014-09-04 |
US20200345803A1 (en) | 2020-11-05 |
JP2016511259A (ja) | 2016-04-14 |
US20210401923A1 (en) | 2021-12-30 |
EP2961420B1 (en) | 2019-09-11 |
US20240156892A1 (en) | 2024-05-16 |
CN105407906A (zh) | 2016-03-16 |
US9687519B2 (en) | 2017-06-27 |
HUE046924T2 (hu) | 2020-03-30 |
JP6918046B2 (ja) | 2021-08-11 |
JP7072692B2 (ja) | 2022-05-20 |
US11083772B2 (en) | 2021-08-10 |
CN115990242A (zh) | 2023-04-21 |
JP2022116008A (ja) | 2022-08-09 |
ES2750258T3 (es) | 2020-03-25 |
JP7381652B2 (ja) | 2023-11-15 |
EP2961420A4 (en) | 2016-08-17 |
US11771734B2 (en) | 2023-10-03 |
CA2916880C (en) | 2021-02-09 |
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