CN118879692A - 深内含子突变的基因编辑 - Google Patents

深内含子突变的基因编辑 Download PDF

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CN118879692A
CN118879692A CN202410714061.8A CN202410714061A CN118879692A CN 118879692 A CN118879692 A CN 118879692A CN 202410714061 A CN202410714061 A CN 202410714061A CN 118879692 A CN118879692 A CN 118879692A
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guide rna
cas
vector
sequence
promoter
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CN202410714061.8A
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Chinese (zh)
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G·阮
A·斯盖利亚
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Genzyme Corp
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Genzyme Corp
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CN202410714061.8A 2015-05-16 2016-04-15 深内含子突变的基因编辑 Pending CN118879692A (zh)

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Application Number Priority Date Filing Date Title
US201562162720P 2015-05-16 2015-05-16
US62/162,720 2015-05-16
PCT/US2016/027987 WO2016186772A2 (en) 2015-05-16 2016-04-15 Gene editing of deep intronic mutations
CN201680041691.7A CN107849547B (zh) 2015-05-16 2016-04-15 深内含子突变的基因编辑

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CN202210293007.1A Pending CN114657180A (zh) 2015-05-16 2016-04-15 深内含子突变的基因编辑
CN202410714061.8A Pending CN118879692A (zh) 2015-05-16 2016-04-15 深内含子突变的基因编辑

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CN202210293007.1A Pending CN114657180A (zh) 2015-05-16 2016-04-15 深内含子突变的基因编辑

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