SG10201912907PA - Gene editing of deep intronic mutations - Google Patents

Gene editing of deep intronic mutations

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Publication number
SG10201912907PA
SG10201912907PA SG10201912907PA SG10201912907PA SG10201912907PA SG 10201912907P A SG10201912907P A SG 10201912907PA SG 10201912907P A SG10201912907P A SG 10201912907PA SG 10201912907P A SG10201912907P A SG 10201912907PA SG 10201912907P A SG10201912907P A SG 10201912907PA
Authority
SG
Singapore
Prior art keywords
gene editing
deep intronic
intronic mutations
mutations
deep
Prior art date
Application number
SG10201912907PA
Inventor
Guoxiang Ruan
Abraham Scaria
Original Assignee
Genzyme Corp
Priority date (The priority date is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the date listed.)
Filing date
Publication date
Application filed by Genzyme Corp filed Critical Genzyme Corp
Publication of SG10201912907PA publication Critical patent/SG10201912907PA/en

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SG10201912907PA 2015-05-16 2016-04-15 Gene editing of deep intronic mutations SG10201912907PA (en)

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US9359599B2 (en) 2013-08-22 2016-06-07 President And Fellows Of Harvard College Engineered transcription activator-like effector (TALE) domains and uses thereof
US9526784B2 (en) 2013-09-06 2016-12-27 President And Fellows Of Harvard College Delivery system for functional nucleases
US9228207B2 (en) 2013-09-06 2016-01-05 President And Fellows Of Harvard College Switchable gRNAs comprising aptamers
US9322037B2 (en) 2013-09-06 2016-04-26 President And Fellows Of Harvard College Cas9-FokI fusion proteins and uses thereof
US11053481B2 (en) 2013-12-12 2021-07-06 President And Fellows Of Harvard College Fusions of Cas9 domains and nucleic acid-editing domains
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