CN117801075A - 多倍体腺相关病毒载体及其制备和使用方法 - Google Patents
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| US10550405B2 (en) | 2017-03-15 | 2020-02-04 | The University Of North Carolina At Chapel Hill | Rational polyploid adeno-associated virus vectors and methods of making and using the same |
| JP2020530307A (ja) | 2017-06-30 | 2020-10-22 | インティマ・バイオサイエンス，インコーポレーテッド | 遺伝子治療のためのアデノ随伴ウイルスベクター |
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| JP7425738B2 (ja) | 2018-04-03 | 2024-01-31 | ギンコ バイオワークス インコーポレイテッド | 眼組織を標的とするウイルスベクター |
| NZ759802A (en) * | 2018-05-07 | 2025-08-29 | Univ North Carolina Chapel Hill | Rational polyploid adeno-associated virus vectors and methods of making and using the same |
| JP2021523198A (ja) * | 2018-05-14 | 2021-09-02 | ビオマリン プハルマセウトイカル インコーポレイテッド | 幼若対象におけるａａｖベクターの安定的発現 |
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| CA3119771A1 (en) * | 2018-11-20 | 2020-05-28 | The Trustees Of The University Of Pennsylvania | Compositions and methods useful for targeting the blood-brain barrier |
| WO2020142236A1 (en) * | 2019-01-02 | 2020-07-09 | Intima Bioscience, Inc. | Modified adeno-associated viral vectors for use in genetic engineering |
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| CA3137078A1 (en) * | 2019-04-15 | 2020-10-22 | University Of Iowa Research Foundation | Methods and compositions for transgene expression |
| WO2020223236A1 (en) * | 2019-04-29 | 2020-11-05 | The Trustees Of The University Of Pennsylvania | Novel aav capsids and compositions containing same |
| KR20220083714A (ko) | 2019-10-17 | 2022-06-20 | 스트라이드바이오 인코포레이티드 | 니만-피크 질환 c형의 치료를 위한 아데노-연관 바이러스 벡터 |
| CN111349148A (zh) * | 2020-03-13 | 2020-06-30 | 辉大(上海)生物科技有限公司 | 一种腺相关病毒载体及其用途 |
| EP4125977A4 (en) * | 2020-05-05 | 2024-09-25 | Duke University | CROSS-SPECIES COMPATIBLE ADENO-ASSOCIATED VIRUS COMPOSITIONS AND METHODS OF USE THEREOF |
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