CN113271982B - 通过靶向肌营养相关蛋白基因来治疗肌营养不良的方法 - Google Patents

通过靶向肌营养相关蛋白基因来治疗肌营养不良的方法 Download PDF

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CN113271982B
CN113271982B CN201980075173.0A CN201980075173A CN113271982B CN 113271982 B CN113271982 B CN 113271982B CN 201980075173 A CN201980075173 A CN 201980075173A CN 113271982 B CN113271982 B CN 113271982B
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CN113271982A (zh
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吉见英治
吉冈克郎
山形哲也
秦元宝
伊恩·罗伯特·汤普生
尼德西·康纳
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Morris Medical Co ltd
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Astellas Pharma Inc
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CN201980075173.0A 2018-11-16 2019-11-15 通过靶向肌营养相关蛋白基因来治疗肌营养不良的方法 Active CN113271982B (zh)

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Application Number Priority Date Filing Date Title
US201862768474P 2018-11-16 2018-11-16
US62/768,474 2018-11-16
US201962861039P 2019-06-13 2019-06-13
US62/861,039 2019-06-13
US201962931925P 2019-11-07 2019-11-07
US62/931,925 2019-11-07
PCT/JP2019/045716 WO2020101042A1 (en) 2018-11-16 2019-11-15 Method for treating muscular dystrophy by targeting utrophin gene

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CN113271982B true CN113271982B (zh) 2024-07-30

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WO2021230385A1 (en) 2020-05-15 2021-11-18 Astellas Pharma Inc. Method for treating muscular dystrophy by targeting utrophin gene
EP4222263A1 (en) 2020-09-29 2023-08-09 Genethon Enhancing utrophin expression in cell by inducing mutations within utrophin regulatory elements and therapeutic use thereof
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