CN109715801B - 用于治疗α1抗胰蛋白酶缺乏的材料和方法 - Google Patents

用于治疗α1抗胰蛋白酶缺乏的材料和方法 Download PDF

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CN109715801B
CN109715801B CN201680080398.1A CN201680080398A CN109715801B CN 109715801 B CN109715801 B CN 109715801B CN 201680080398 A CN201680080398 A CN 201680080398A CN 109715801 B CN109715801 B CN 109715801B
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nucleotides
gene
certain embodiments
sequence
cells
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CN109715801A (zh
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C.A.科万
R.L.博戈拉
J.李
A.S.伦贝里
M.J.约翰
J.W.斯特宾斯
T.T.朊
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CRISPR Therapeutics AG
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CN201680080398.1A 2015-12-01 2016-12-01 用于治疗α1抗胰蛋白酶缺乏的材料和方法 Active CN109715801B (zh)

Applications Claiming Priority (5)

Application Number Priority Date Filing Date Title
US201562261661P 2015-12-01 2015-12-01
US62/261661 2015-12-01
US201662324056P 2016-04-18 2016-04-18
US62/324056 2016-04-18
PCT/IB2016/001845 WO2017093804A2 (en) 2015-12-01 2016-12-01 Materials and methods for treatment of alpha-1 antitrypsin deficiency

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CN109715801A CN109715801A (zh) 2019-05-03
CN109715801B true CN109715801B (zh) 2022-11-01

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US (2) US11851653B2 (https=)
EP (2) EP3967758A1 (https=)
JP (2) JP6932698B2 (https=)
CN (1) CN109715801B (https=)
AU (1) AU2016364667A1 (https=)
CA (1) CA3006618A1 (https=)
WO (1) WO2017093804A2 (https=)

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