CA3040483A1 - Aav capsid designs - Google Patents

Aav capsid designs Download PDF

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Publication number
CA3040483A1
CA3040483A1 CA3040483A CA3040483A CA3040483A1 CA 3040483 A1 CA3040483 A1 CA 3040483A1 CA 3040483 A CA3040483 A CA 3040483A CA 3040483 A CA3040483 A CA 3040483A CA 3040483 A1 CA3040483 A1 CA 3040483A1
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CA
Canada
Prior art keywords
hsa
mir
aav
promoter
nucleic acid
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Pending
Application number
CA3040483A
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English (en)
French (fr)
Inventor
Guangping Gao
Guangchao XU
Phillip TAI
Yuquan Wei
Li Luo
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University of Massachusetts Amherst
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University of Massachusetts Amherst
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Publication of CA3040483A1 publication Critical patent/CA3040483A1/en
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CA3040483A 2016-10-13 2017-10-13 Aav capsid designs Pending CA3040483A1 (en)

Applications Claiming Priority (7)

Application Number Priority Date Filing Date Title
US201662408022P 2016-10-13 2016-10-13
US62/408,022 2016-10-13
US201662417756P 2016-11-04 2016-11-04
US62/417,756 2016-11-04
US201762486642P 2017-04-18 2017-04-18
US62/486,642 2017-04-18
PCT/US2017/056614 WO2018071831A1 (en) 2016-10-13 2017-10-13 Aav capsid designs

Publications (1)

Publication Number Publication Date
CA3040483A1 true CA3040483A1 (en) 2018-04-19

Family

ID=61906092

Family Applications (1)

Application Number Title Priority Date Filing Date
CA3040483A Pending CA3040483A1 (en) 2016-10-13 2017-10-13 Aav capsid designs

Country Status (8)

Country Link
US (2) US11578340B2 (https=)
EP (1) EP3526333A4 (https=)
JP (2) JP7577291B6 (https=)
KR (2) KR20240173209A (https=)
CN (1) CN110506119A (https=)
AU (2) AU2017341849B2 (https=)
CA (1) CA3040483A1 (https=)
WO (1) WO2018071831A1 (https=)

Cited By (1)

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CN115976106A (zh) * 2022-12-14 2023-04-18 中国人民解放军海军军医大学第一附属医院 一种携带人spink1基因的重组腺相关病毒载体及其防治胰腺炎的应用

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CN107073051B (zh) 2014-10-21 2021-08-24 马萨诸塞大学 重组aav变体及其用途
GB201508026D0 (en) 2015-05-11 2015-06-24 Ucl Business Plc Capsid
US20200316221A1 (en) * 2016-10-13 2020-10-08 University Of Massachusetts Aav capsid designs
AU2017341849B2 (en) 2016-10-13 2024-03-21 University Of Massachusetts AAV capsid designs
WO2018119330A2 (en) * 2016-12-22 2018-06-28 Oregon Health & Science University Adeno associated viral vectors
EP3575398A4 (en) * 2017-01-30 2020-11-11 Nippon Medical School Foundation ADENO-ASSOCIATED VIRUS (AAV) CAPSIDE PROTEIN MUTANT
US10898585B2 (en) 2017-04-14 2021-01-26 Ptc Therapeutics .Inc. Gene therapy for AADC deficiency
SG11202009854XA (en) * 2018-02-15 2020-11-27 Bjoerklund Tomas Modified viral capsids
AU2019227910B2 (en) 2018-02-28 2025-07-17 The Regents Of The University Of California A modular system for gene and protein delivery based on AAV
CA3100006A1 (en) * 2018-05-11 2019-11-14 Massachusetts Eye And Ear Infirmary Altering tissue tropism of adeno-associated viruses
CN113966399A (zh) 2018-09-26 2022-01-21 加州理工学院 用于靶向基因疗法的腺相关病毒组合物
US20220073905A1 (en) * 2018-12-28 2022-03-10 University Of Pittsburgh - Of The Commonwealth System Of Higher Education Methods and materials for single cell transcriptome-based development of aav vectors and promoters
JP2022530457A (ja) 2019-04-26 2022-06-29 サンガモ セラピューティクス， インコーポレイテッド 遺伝子操作ａａｖ
EP3963083A1 (en) * 2019-04-29 2022-03-09 Voyager Therapeutics, Inc. Compositions and methods for the treatment of tauopathy
AU2020299026A1 (en) * 2019-07-04 2022-01-20 Children's Medical Research Institute Methods and AAV vectors for in vivo transduction
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