BR112023025999A2 - Métodos de purificação de coluna de vetor de aav - Google Patents

Métodos de purificação de coluna de vetor de aav

Info

Publication number
BR112023025999A2
BR112023025999A2 BR112023025999A BR112023025999A BR112023025999A2 BR 112023025999 A2 BR112023025999 A2 BR 112023025999A2 BR 112023025999 A BR112023025999 A BR 112023025999A BR 112023025999 A BR112023025999 A BR 112023025999A BR 112023025999 A2 BR112023025999 A2 BR 112023025999A2
Authority
BR
Brazil
Prior art keywords
aav vector
column purification
purification methods
vector column
complete
Prior art date
Application number
BR112023025999A
Other languages
English (en)
Portuguese (pt)
Inventor
Mi Jin
Ohnmar Khanal
Vijesh Kumar
Original Assignee
Spark Therapeutics Inc
Priority date (The priority date is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the date listed.)
Filing date
Publication date
Application filed by Spark Therapeutics Inc filed Critical Spark Therapeutics Inc
Publication of BR112023025999A2 publication Critical patent/BR112023025999A2/pt

Links

Classifications

    • CCHEMISTRY; METALLURGY
    • C12BIOCHEMISTRY; BEER; SPIRITS; WINE; VINEGAR; MICROBIOLOGY; ENZYMOLOGY; MUTATION OR GENETIC ENGINEERING
    • C12NMICROORGANISMS OR ENZYMES; COMPOSITIONS THEREOF; PROPAGATING, PRESERVING, OR MAINTAINING MICROORGANISMS; MUTATION OR GENETIC ENGINEERING; CULTURE MEDIA
    • C12N15/00Mutation or genetic engineering; DNA or RNA concerning genetic engineering, vectors, e.g. plasmids, or their isolation, preparation or purification; Use of hosts therefor
    • C12N15/09Recombinant DNA-technology
    • C12N15/63Introduction of foreign genetic material using vectors; Vectors; Use of hosts therefor; Regulation of expression
    • C12N15/79Vectors or expression systems specially adapted for eukaryotic hosts
    • C12N15/85Vectors or expression systems specially adapted for eukaryotic hosts for animal cells
    • C12N15/86Viral vectors
    • BPERFORMING OPERATIONS; TRANSPORTING
    • B01PHYSICAL OR CHEMICAL PROCESSES OR APPARATUS IN GENERAL
    • B01DSEPARATION
    • B01D15/00Separating processes involving the treatment of liquids with solid sorbents; Apparatus therefor
    • B01D15/08Selective adsorption, e.g. chromatography
    • B01D15/26Selective adsorption, e.g. chromatography characterised by the separation mechanism
    • B01D15/36Selective adsorption, e.g. chromatography characterised by the separation mechanism involving ionic interaction, e.g. ion-exchange, ion-pair, ion-suppression or ion-exclusion
    • B01D15/361Ion-exchange
    • B01D15/363Anion-exchange
    • BPERFORMING OPERATIONS; TRANSPORTING
    • B01PHYSICAL OR CHEMICAL PROCESSES OR APPARATUS IN GENERAL
    • B01DSEPARATION
    • B01D15/00Separating processes involving the treatment of liquids with solid sorbents; Apparatus therefor
    • B01D15/08Selective adsorption, e.g. chromatography
    • B01D15/42Selective adsorption, e.g. chromatography characterised by the development mode, e.g. by displacement or by elution
    • B01D15/422Displacement mode
    • CCHEMISTRY; METALLURGY
    • C12BIOCHEMISTRY; BEER; SPIRITS; WINE; VINEGAR; MICROBIOLOGY; ENZYMOLOGY; MUTATION OR GENETIC ENGINEERING
    • C12NMICROORGANISMS OR ENZYMES; COMPOSITIONS THEREOF; PROPAGATING, PRESERVING, OR MAINTAINING MICROORGANISMS; MUTATION OR GENETIC ENGINEERING; CULTURE MEDIA
    • C12N2750/00MICROORGANISMS OR ENZYMES; COMPOSITIONS THEREOF; PROPAGATING, PRESERVING, OR MAINTAINING MICROORGANISMS; MUTATION OR GENETIC ENGINEERING; CULTURE MEDIA ssDNA viruses
    • C12N2750/00011Details
    • C12N2750/14011Parvoviridae
    • C12N2750/14111Dependovirus, e.g. adenoassociated viruses
    • C12N2750/14141Use of virus, viral particle or viral elements as a vector
    • C12N2750/14143Use of virus, viral particle or viral elements as a vector viral genome or elements thereof as genetic vector
    • CCHEMISTRY; METALLURGY
    • C12BIOCHEMISTRY; BEER; SPIRITS; WINE; VINEGAR; MICROBIOLOGY; ENZYMOLOGY; MUTATION OR GENETIC ENGINEERING
    • C12NMICROORGANISMS OR ENZYMES; COMPOSITIONS THEREOF; PROPAGATING, PRESERVING, OR MAINTAINING MICROORGANISMS; MUTATION OR GENETIC ENGINEERING; CULTURE MEDIA
    • C12N2750/00MICROORGANISMS OR ENZYMES; COMPOSITIONS THEREOF; PROPAGATING, PRESERVING, OR MAINTAINING MICROORGANISMS; MUTATION OR GENETIC ENGINEERING; CULTURE MEDIA ssDNA viruses
    • C12N2750/00011Details
    • C12N2750/14011Parvoviridae
    • C12N2750/14111Dependovirus, e.g. adenoassociated viruses
    • C12N2750/14151Methods of production or purification of viral material

Landscapes

  • Chemical & Material Sciences (AREA)
  • Health & Medical Sciences (AREA)
  • Life Sciences & Earth Sciences (AREA)
  • Genetics & Genomics (AREA)
  • Engineering & Computer Science (AREA)
  • General Engineering & Computer Science (AREA)
  • Bioinformatics & Cheminformatics (AREA)
  • Organic Chemistry (AREA)
  • Chemical Kinetics & Catalysis (AREA)
  • Biomedical Technology (AREA)
  • Zoology (AREA)
  • Biotechnology (AREA)
  • Analytical Chemistry (AREA)
  • Wood Science & Technology (AREA)
  • Biophysics (AREA)
  • Plant Pathology (AREA)
  • Microbiology (AREA)
  • Molecular Biology (AREA)
  • Virology (AREA)
  • Biochemistry (AREA)
  • General Health & Medical Sciences (AREA)
  • Physics & Mathematics (AREA)
  • Micro-Organisms Or Cultivation Processes Thereof (AREA)
  • Nitrogen And Oxygen Or Sulfur-Condensed Heterocyclic Ring Systems (AREA)
  • Treatment Of Liquids With Adsorbents In General (AREA)
BR112023025999A 2021-06-11 2022-06-10 Métodos de purificação de coluna de vetor de aav BR112023025999A2 (pt)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US202163209680P 2021-06-11 2021-06-11
US202263366094P 2022-06-09 2022-06-09
PCT/US2022/072859 WO2022261663A1 (en) 2021-06-11 2022-06-10 Aav vector column purification methods

Publications (1)

Publication Number Publication Date
BR112023025999A2 true BR112023025999A2 (pt) 2024-02-27

Family

ID=84426294

Family Applications (1)

Application Number Title Priority Date Filing Date
BR112023025999A BR112023025999A2 (pt) 2021-06-11 2022-06-10 Métodos de purificação de coluna de vetor de aav

Country Status (13)

Country Link
US (1) US20240271159A1 (https=)
EP (1) EP4351755A4 (https=)
JP (1) JP2024525142A (https=)
KR (1) KR20240021231A (https=)
AU (1) AU2022289035A1 (https=)
BR (1) BR112023025999A2 (https=)
CA (1) CA3221540A1 (https=)
CL (1) CL2023003646A1 (https=)
CO (1) CO2023018191A2 (https=)
IL (1) IL309070A (https=)
MX (1) MX2023014809A (https=)
PE (1) PE20240359A1 (https=)
WO (1) WO2022261663A1 (https=)

Families Citing this family (3)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
WO2024036251A1 (en) * 2022-08-12 2024-02-15 Ultragenyx Pharmaceutical Inc. Novel anion-exchange chromatography methods for separation of empty from full recombinant adeno-associated virus particles
EP4670812A1 (en) * 2024-06-27 2025-12-31 Sartorius Stedim Biotech GmbH CONTINUOUS POLISHING OF VIRAL CAPSIDES
WO2026064763A1 (en) * 2024-09-23 2026-03-26 Regeneron Pharmaceuticals, Inc. Partitioning anion exchange chromatography for purification of recombinant adeno-associated virus (raav)

Family Cites Families (5)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
DE602004030327D1 (de) * 2003-05-21 2011-01-13 Genzyme Corp Verfahren zur herstellung von präparationen rekombinanter aav-virionen, die weitgehend frei von leeren capsiden sind
US20120093775A1 (en) * 2009-03-27 2012-04-19 Proyecto De Biomedicina Cima, S.L. Methods and compositions for the treatment of cirrhosis and liver fibrosis
MY207534A (en) * 2017-06-30 2025-03-03 Spark Therapeutics Inc Aav vector column purification methods
US20230183659A1 (en) * 2021-10-29 2023-06-15 Homology Medicines, Inc. Methods and compositions for the purification of adeno-associated virus
EP4602172A1 (en) * 2022-10-11 2025-08-20 MeiraGTx UK II Limited Chromatography methods for purification of aav capsids

Also Published As

Publication number Publication date
JP2024525142A (ja) 2024-07-10
IL309070A (en) 2024-02-01
US20240271159A1 (en) 2024-08-15
CO2023018191A2 (es) 2024-01-25
WO2022261663A1 (en) 2022-12-15
EP4351755A4 (en) 2025-04-23
EP4351755A1 (en) 2024-04-17
AU2022289035A1 (en) 2024-01-04
PE20240359A1 (es) 2024-02-27
KR20240021231A (ko) 2024-02-16
CL2023003646A1 (es) 2024-10-25
CA3221540A1 (en) 2022-12-15
MX2023014809A (es) 2024-01-29

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