BR112019021569A2 - Precursor de iduronato-2-sulfatase humana recombinante glicosilada (ids), método para tratar um sujeito humano diagnosticado com mucopolissacaridose tipo ii (mps ii) - Google Patents
Precursor de iduronato-2-sulfatase humana recombinante glicosilada (ids), método para tratar um sujeito humano diagnosticado com mucopolissacaridose tipo ii (mps ii) Download PDFInfo
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| CN105755044A (zh) | 2011-04-22 | 2016-07-13 | 加利福尼亚大学董事会 | 具有变异衣壳的腺相关病毒病毒体及其使用方法 |
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| HK1256341A1 (zh) | 2015-05-15 | 2019-09-20 | 明尼苏达大学董事会 | 用於治疗性递送到中枢神经系统的腺相关物 |
| EP3101125A1 (en) * | 2015-06-05 | 2016-12-07 | Laboratorios Del Dr. Esteve, S.A. | Adenoassociated virus vectors for the treatment of mucopolysaccharidoses |
| IL258005B2 (en) * | 2015-09-17 | 2025-01-01 | Res Inst Nationwide Childrens Hospital | Methods and materials for gene therapy for beta-4,1-N-acetylgalactosaminyltransferase 2 |
| SG10201912761UA (en) | 2016-04-15 | 2020-02-27 | The Trustees Of The Univ Of Pennsyvania | Gene therapy for treating mucopolysaccharidosis type ii |
| KR20190139951A (ko) | 2017-04-14 | 2019-12-18 | 리젠엑스바이오 인크. | 인간 뉴런 또는 신경교 세포에 의해 생성된 재조합 인간 이두로네이트-2 설파타제(ids)를 이용한 뮤코다당증 ii형의 치료 |
| BR112022015183A2 (pt) | 2020-01-29 | 2022-12-20 | Regenxbio Inc | Método para tratamento de um sujeito humano diagnosticado com mucopolissacaridose tipo ii (mps ii) |
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| CA3059441A1 (en) | 2018-10-18 |
| IL269892A (https=) | 2019-12-31 |
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| SG11201909361SA (en) | 2019-11-28 |
| KR20190139951A (ko) | 2019-12-18 |
| IL269892B2 (en) | 2024-04-01 |
| TW201903146A (zh) | 2019-01-16 |
| EP3609526A1 (en) | 2020-02-19 |
| US20250051740A1 (en) | 2025-02-13 |
| JP2023052096A (ja) | 2023-04-11 |
| EP3609526A4 (en) | 2021-01-13 |
| JP2025087702A (ja) | 2025-06-10 |
| TW202532642A (zh) | 2025-08-16 |
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