BR112014028666B1 - Uso de uma partícula de raav2, composição farmacêutica e kit - Google Patents
Uso de uma partícula de raav2, composição farmacêutica e kit Download PDFInfo
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| PCT/US2013/031725 WO2013172964A1 (en) | 2012-05-18 | 2013-03-14 | Methods and compositions for treating amyloid deposits |
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| BR112014028666A2 BR112014028666A2 (pt) | 2017-06-27 |
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| CN112410339A (zh) | 2014-11-14 | 2021-02-26 | 沃雅戈治疗公司 | 调节性多核苷酸 |
| US11027024B2 (en) | 2015-05-29 | 2021-06-08 | University Of Iowa Research Foundation | Methods of delivery of transgenes for treating brain diseases |
| EP3307391A1 (en) * | 2015-06-12 | 2018-04-18 | INSERM (Institut National de la Santé et de la Recherche Médicale) | Methods and pharmaceutical composition for the treatment of alzheimer's disease |
| KR20180134373A (ko) * | 2016-04-14 | 2018-12-18 | 타오 헬스 라이프 파마 가부시키가이샤 | 아밀로스페로이드(aspd)형 구조체 및 의약 조성물 |
| CA3252099A1 (en) | 2016-05-18 | 2025-06-05 | Voyager Therapeutics, Inc. | MODULATING POLYNUCLEOTIDES |
| AU2017306558B2 (en) * | 2016-08-03 | 2024-09-19 | University Of South Florida | Reelin compositions for treatment of neurological disorders |
| MX2019002518A (es) * | 2016-09-02 | 2019-07-18 | Spark Therapeutics Inc | Metodos y vectores para el tratamiento de trastornos del snc. |
| EP3309550A1 (en) * | 2016-10-12 | 2018-04-18 | sphingotec GmbH | Method for the detection of apolipoprotein e4 |
| KR102709597B1 (ko) | 2017-10-03 | 2024-09-26 | 프리베일 테라퓨틱스, 인크. | 리소좀 장애를 위한 유전자 요법 |
| CN111465691A (zh) | 2017-10-03 | 2020-07-28 | 普利维尔治疗公司 | 用于溶酶体障碍的基因疗法 |
| CA3121211A1 (en) * | 2018-11-28 | 2020-06-04 | Prevail Therapeutics, Inc. | Gene therapies for neurodegenerative disease |
| MX2022004524A (es) * | 2019-10-16 | 2022-07-21 | Univ Cornell | Tratamiento génico para la enfermedad de alzheimer. |
| KR20230020946A (ko) * | 2020-03-31 | 2023-02-13 | 누오-베타 파마슈티컬 테크놀로지 (상하이) 씨오., 엘티디. | 중수소화 옥소페닐아르신 화합물 및 이의 용도 |
| US20230405149A1 (en) * | 2020-11-25 | 2023-12-21 | Prevail Therapeutics, Inc. | Gene therapies for neurodegenerative disease |
| CN120187407A (zh) * | 2021-12-15 | 2025-06-20 | 健达九州(北京)生物科技有限公司 | 重组aav载体及其用途 |
| CN116063405B (zh) * | 2022-09-27 | 2025-08-29 | 广州译码基因科技有限公司 | 可提高AAV病毒包装能力的衣壳蛋白突变体MutC及其应用 |
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| US5589154A (en) * | 1994-11-22 | 1996-12-31 | Rutgers, The State University Of New Jersey | Methods for the prevention or treatment of vascular hemorrhaging and Alzheimer's disease |
| US6436996B1 (en) * | 1997-09-30 | 2002-08-20 | Duke University | Modulation of nitric oxide production |
| US6468524B1 (en) * | 2000-03-22 | 2002-10-22 | The United States Of America, As Represented By The Secretary Of The Department Of Health And Human Services | AAV4 vector and uses thereof |
| US6855314B1 (en) | 2000-03-22 | 2005-02-15 | The United States Of America As Represented By The Department Of Health And Human Services | AAV5 vector for transducing brain cells and lung cells |
| GB0322645D0 (en) * | 2003-09-26 | 2003-10-29 | Melacure Therapeutics Ab | Use of antisecretory factor peptides |
| EP1828390B1 (en) * | 2004-12-15 | 2012-06-13 | The University Of North Carolina At Chapel Hill | Chimeric vectors |
| PL1879623T3 (pl) * | 2005-05-02 | 2013-03-29 | Genzyme Corp | Terapia genowa zaburzeń rdzenia kręgowego |
| CN101610793B (zh) * | 2006-09-14 | 2012-10-24 | 迈德詹尼克斯医疗以色列有限公司 | 长效药物制剂 |
| HUE027278T2 (en) * | 2007-05-16 | 2016-11-28 | Brigham & Womens Hospital Inc | Treatment of synucleinopathies |
| EP2561075B1 (en) * | 2010-04-23 | 2018-06-27 | University of Massachusetts | Aav-based treatment of cholesterol-related disorders |
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2013
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- 2013-03-14 IN IN2672KON2014 patent/IN2014KN02672A/en unknown
- 2013-03-14 CN CN202011133829.0A patent/CN112574964A/zh active Pending
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- 2013-03-14 AU AU2013263346A patent/AU2013263346B2/en active Active
- 2013-03-14 US US14/402,064 patent/US20150183850A1/en not_active Abandoned
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- 2013-03-14 WO PCT/US2013/031725 patent/WO2013172964A1/en not_active Ceased
- 2013-03-14 JP JP2015512644A patent/JP6469000B2/ja active Active
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2018
- 2018-11-02 JP JP2018207331A patent/JP2019031564A/ja active Pending
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| EP2850195B1 (en) | 2020-01-22 |
| CN104540952A (zh) | 2015-04-22 |
| HK1207109A1 (en) | 2016-01-22 |
| JP2019031564A (ja) | 2019-02-28 |
| ES2786078T3 (es) | 2020-10-08 |
| RU2673484C2 (ru) | 2018-11-27 |
| JP6469000B2 (ja) | 2019-02-13 |
| AU2013263346B2 (en) | 2018-08-23 |
| CN112574964A (zh) | 2021-03-30 |
| IN2014KN02672A (enExample) | 2015-05-08 |
| JP2015520161A (ja) | 2015-07-16 |
| EP2850195A1 (en) | 2015-03-25 |
| RU2014151218A (ru) | 2016-07-10 |
| WO2013172964A1 (en) | 2013-11-21 |
| AU2013263346A1 (en) | 2014-12-04 |
| CA2873890A1 (en) | 2013-11-21 |
| BR112014028666A2 (pt) | 2017-06-27 |
| US20150183850A1 (en) | 2015-07-02 |
| EP2850195A4 (en) | 2015-12-09 |
| CA2873890C (en) | 2022-12-06 |
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