UA95099C2 - Применение деферипрона при лечении железо-индуцированного повреждения митохондрий, который является следствием атаксии фридрейха - Google Patents
Применение деферипрона при лечении железо-индуцированного повреждения митохондрий, который является следствием атаксии фридрейхаInfo
- Publication number
- UA95099C2 UA95099C2 UAA200810608A UAA200810608A UA95099C2 UA 95099 C2 UA95099 C2 UA 95099C2 UA A200810608 A UAA200810608 A UA A200810608A UA A200810608 A UAA200810608 A UA A200810608A UA 95099 C2 UA95099 C2 UA 95099C2
- Authority
- UA
- Ukraine
- Prior art keywords
- iron
- deferiprone
- friedreich ataxia
- ataxia resulting
- treat friedreich
- Prior art date
Links
Classifications
-
- A—HUMAN NECESSITIES
- A61—MEDICAL OR VETERINARY SCIENCE; HYGIENE
- A61K—PREPARATIONS FOR MEDICAL, DENTAL OR TOILETRY PURPOSES
- A61K31/00—Medicinal preparations containing organic active ingredients
- A61K31/33—Heterocyclic compounds
- A61K31/395—Heterocyclic compounds having nitrogen as a ring hetero atom, e.g. guanethidine or rifamycins
- A61K31/435—Heterocyclic compounds having nitrogen as a ring hetero atom, e.g. guanethidine or rifamycins having six-membered rings with one nitrogen as the only ring hetero atom
- A61K31/44—Non condensed pyridines; Hydrogenated derivatives thereof
- A61K31/4412—Non condensed pyridines; Hydrogenated derivatives thereof having oxo groups directly attached to the heterocyclic ring
-
- A—HUMAN NECESSITIES
- A61—MEDICAL OR VETERINARY SCIENCE; HYGIENE
- A61K—PREPARATIONS FOR MEDICAL, DENTAL OR TOILETRY PURPOSES
- A61K31/00—Medicinal preparations containing organic active ingredients
- A61K31/185—Acids; Anhydrides, halides or salts thereof, e.g. sulfur acids, imidic, hydrazonic or hydroximic acids
- A61K31/19—Carboxylic acids, e.g. valproic acid
- A61K31/195—Carboxylic acids, e.g. valproic acid having an amino group
-
- A—HUMAN NECESSITIES
- A61—MEDICAL OR VETERINARY SCIENCE; HYGIENE
- A61K—PREPARATIONS FOR MEDICAL, DENTAL OR TOILETRY PURPOSES
- A61K31/00—Medicinal preparations containing organic active ingredients
- A61K31/33—Heterocyclic compounds
- A61K31/395—Heterocyclic compounds having nitrogen as a ring hetero atom, e.g. guanethidine or rifamycins
- A61K31/41—Heterocyclic compounds having nitrogen as a ring hetero atom, e.g. guanethidine or rifamycins having five-membered rings with two or more ring hetero atoms, at least one of which being nitrogen, e.g. tetrazole
- A61K31/4196—1,2,4-Triazoles
-
- A—HUMAN NECESSITIES
- A61—MEDICAL OR VETERINARY SCIENCE; HYGIENE
- A61P—SPECIFIC THERAPEUTIC ACTIVITY OF CHEMICAL COMPOUNDS OR MEDICINAL PREPARATIONS
- A61P25/00—Drugs for disorders of the nervous system
-
- A—HUMAN NECESSITIES
- A61—MEDICAL OR VETERINARY SCIENCE; HYGIENE
- A61P—SPECIFIC THERAPEUTIC ACTIVITY OF CHEMICAL COMPOUNDS OR MEDICINAL PREPARATIONS
- A61P25/00—Drugs for disorders of the nervous system
- A61P25/28—Drugs for disorders of the nervous system for treating neurodegenerative disorders of the central nervous system, e.g. nootropic agents, cognition enhancers, drugs for treating Alzheimer's disease or other forms of dementia
-
- A—HUMAN NECESSITIES
- A61—MEDICAL OR VETERINARY SCIENCE; HYGIENE
- A61P—SPECIFIC THERAPEUTIC ACTIVITY OF CHEMICAL COMPOUNDS OR MEDICINAL PREPARATIONS
- A61P39/00—General protective or antinoxious agents
- A61P39/04—Chelating agents
Landscapes
- Health & Medical Sciences (AREA)
- Animal Behavior & Ethology (AREA)
- Chemical & Material Sciences (AREA)
- Veterinary Medicine (AREA)
- Public Health (AREA)
- Medicinal Chemistry (AREA)
- General Health & Medical Sciences (AREA)
- Pharmacology & Pharmacy (AREA)
- Life Sciences & Earth Sciences (AREA)
- Epidemiology (AREA)
- Nuclear Medicine, Radiotherapy & Molecular Imaging (AREA)
- Neurosurgery (AREA)
- General Chemical & Material Sciences (AREA)
- Chemical Kinetics & Catalysis (AREA)
- Engineering & Computer Science (AREA)
- Bioinformatics & Cheminformatics (AREA)
- Biomedical Technology (AREA)
- Organic Chemistry (AREA)
- Neurology (AREA)
- Hospice & Palliative Care (AREA)
- Psychiatry (AREA)
- Toxicology (AREA)
- Pharmaceuticals Containing Other Organic And Inorganic Compounds (AREA)
- Acyclic And Carbocyclic Compounds In Medicinal Compositions (AREA)
- Medicines That Contain Protein Lipid Enzymes And Other Medicines (AREA)
Abstract
Изобретение касается применения деферипрона или его физиологически приемлемой соли при лечении железо-индуцированного повреждения митохондрий, которое является следствием атаксии Фридрейха, при отсутствии общей перегрузки железа у пациента путем ежедневного введения до 30 мг/кг деферипрона.
Applications Claiming Priority (1)
Application Number | Priority Date | Filing Date | Title |
---|---|---|---|
US77532006P | 2006-02-22 | 2006-02-22 |
Publications (1)
Publication Number | Publication Date |
---|---|
UA95099C2 true UA95099C2 (ru) | 2011-07-11 |
Family
ID=38436879
Family Applications (1)
Application Number | Title | Priority Date | Filing Date |
---|---|---|---|
UAA200810608A UA95099C2 (ru) | 2006-02-22 | 2007-02-21 | Применение деферипрона при лечении железо-индуцированного повреждения митохондрий, который является следствием атаксии фридрейха |
Country Status (24)
Country | Link |
---|---|
US (3) | US20090023784A1 (ru) |
EP (1) | EP1991225B1 (ru) |
JP (1) | JP5730466B2 (ru) |
KR (1) | KR20080104329A (ru) |
CN (1) | CN101420954A (ru) |
AU (1) | AU2007219009B2 (ru) |
BR (1) | BRPI0708211A2 (ru) |
CA (1) | CA2642778A1 (ru) |
DK (1) | DK1991225T3 (ru) |
ES (1) | ES2441065T3 (ru) |
IL (1) | IL193598A (ru) |
MA (1) | MA30266B1 (ru) |
MX (1) | MX2008010824A (ru) |
MY (1) | MY151412A (ru) |
NZ (1) | NZ570730A (ru) |
PL (1) | PL1991225T3 (ru) |
PT (1) | PT1991225E (ru) |
RS (1) | RS53225B (ru) |
RU (1) | RU2008137604A (ru) |
SG (1) | SG170020A1 (ru) |
SI (1) | SI1991225T1 (ru) |
TN (1) | TNSN08338A1 (ru) |
UA (1) | UA95099C2 (ru) |
WO (1) | WO2007095728A1 (ru) |
Families Citing this family (15)
Publication number | Priority date | Publication date | Assignee | Title |
---|---|---|---|---|
UA95099C2 (ru) * | 2006-02-22 | 2011-07-11 | Арнольд Мунних | Применение деферипрона при лечении железо-индуцированного повреждения митохондрий, который является следствием атаксии фридрейха |
CN101679263B (zh) | 2007-03-28 | 2014-01-15 | 阿普泰克斯科技公司 | 去铁酮的氟化衍生物 |
CA2722393A1 (en) * | 2008-04-25 | 2009-10-29 | Apotex Technologies Inc. | Liquid formulation for deferiprone with palatable taste |
MY161269A (en) * | 2009-01-26 | 2017-04-14 | Univ Pennsylvania | Use of deferiprone for treatment and prevention of iron-related eye disorders |
MA33985B1 (fr) | 2009-07-03 | 2013-02-01 | Apotex Technologies Inc | Dérivés fluorés de 3-hydroxypyridin-4-ones |
EP2456438A2 (en) | 2009-07-23 | 2012-05-30 | Novartis AG | Use of azabicycloalkyl derivatives or pyrrolidine-2-one derivatives |
TWI558398B (zh) | 2009-09-22 | 2016-11-21 | 諾華公司 | 菸鹼乙醯膽鹼受體α7活化劑之用途 |
DK2611457T3 (da) | 2010-08-30 | 2014-05-12 | Roberto Testi | Sammensætninger og fremgangsmåder til behandling af Friereichs ataxia med interferon gamma |
CN102861017A (zh) * | 2011-07-08 | 2013-01-09 | 辽宁省计划生育科学研究院 | 一种化合物在防治老年痴呆的应用 |
WO2013139931A1 (en) * | 2012-03-21 | 2013-09-26 | Icm (Institut Du Cerveau Et De La Moelle Épinière) | Composition for use in the treatment of neurodegenerative diseases with parkinsonian syndromes |
US10442779B2 (en) | 2014-09-22 | 2019-10-15 | Fratagene Therapeutics S.R.L. | Compositions and methods for treating Friedreich's ataxia |
US10426775B2 (en) | 2017-09-11 | 2019-10-01 | Fratagene Therapeutics Srl | Methods for treating Friedreich's ataxia with etravirine |
AU2018357350B2 (en) | 2017-10-25 | 2023-09-21 | Chiesi Farmaceutici S.P.A. | Delayed release deferiprone tablets and methods of using the same |
US12016850B2 (en) | 2022-04-11 | 2024-06-25 | Chiesi Farmaceutici S.P.A. | Modified release pharmaceutical formulations comprising deferiprone |
US12016851B2 (en) | 2022-04-11 | 2024-06-25 | Chiesi Farmaceutici S.P.A. | Modified release pharmaceutical formulations comprising deferiprone |
Family Cites Families (13)
Publication number | Priority date | Publication date | Assignee | Title |
---|---|---|---|---|
US5624807A (en) | 1992-07-22 | 1997-04-29 | The Mclean Hospital Corporation | Methods for detecting Alzheimer's disease by measuring ratios of calcium-activated neutral protease isoforms |
US6472378B2 (en) | 1998-08-31 | 2002-10-29 | Pro-Neuron, Inc. | Compositions and methods for treatment of mitochondrial diseases |
US6133322A (en) * | 1998-10-29 | 2000-10-17 | Institut National De La Sante Et De La Recherche Medicale (Inserm) | Quinone derivatives for treating or preventing diseases associated with iron overload |
US6933104B1 (en) * | 1999-04-23 | 2005-08-23 | Shiva Biomedical, Llc | Diagnosis and treatment of human kidney diseases |
AUPQ262499A0 (en) * | 1999-09-02 | 1999-09-23 | University Of Queensland, The | Novel iron chelators |
CA2313270C (en) * | 2000-06-30 | 2011-09-13 | Apotex Inc. | Use of deferiprone in treating and preventing iron-induced cardiac disease |
US20040101521A1 (en) * | 2002-07-12 | 2004-05-27 | The Buck Institute For Research On Aging | Iron sequestration or elimination to reduce neurodegeneration or Parkinsons disease progression |
US8058442B2 (en) * | 2002-11-07 | 2011-11-15 | Technion Research And Development Foundation Ltd. | Neuroprotective iron chelators and pharmaceutical compositions comprising them |
US9737511B2 (en) * | 2004-05-24 | 2017-08-22 | Geoffrey C. GURTNER | Method of treating or preventing pathologic effects of acute increases in hyperglycemia and/or acute increases of free fatty acid flux |
US8829051B2 (en) * | 2004-05-24 | 2014-09-09 | Geoffrey C. GURTNER | Method of treating or preventing pathologic effects of acute increases in hyperglycemia and/or acute increases of free fatty acid flux |
US7728038B2 (en) * | 2004-08-04 | 2010-06-01 | University Of Utah Research Foundation | Methods for chelation therapy |
US20070197469A1 (en) * | 2006-02-17 | 2007-08-23 | Murthy Yerramilli V | Fluoroquinolone carboxylic acid salt compositions |
UA95099C2 (ru) * | 2006-02-22 | 2011-07-11 | Арнольд Мунних | Применение деферипрона при лечении железо-индуцированного повреждения митохондрий, который является следствием атаксии фридрейха |
-
2007
- 2007-02-21 UA UAA200810608A patent/UA95099C2/ru unknown
- 2007-02-21 RS RS20140006A patent/RS53225B/en unknown
- 2007-02-21 SG SG201101266-3A patent/SG170020A1/en unknown
- 2007-02-21 US US12/279,930 patent/US20090023784A1/en not_active Abandoned
- 2007-02-21 JP JP2008555581A patent/JP5730466B2/ja not_active Expired - Fee Related
- 2007-02-21 AU AU2007219009A patent/AU2007219009B2/en not_active Ceased
- 2007-02-21 ES ES07701800.0T patent/ES2441065T3/es active Active
- 2007-02-21 MY MYPI20083186 patent/MY151412A/en unknown
- 2007-02-21 DK DK07701800.0T patent/DK1991225T3/da active
- 2007-02-21 PL PL07701800T patent/PL1991225T3/pl unknown
- 2007-02-21 RU RU2008137604/14A patent/RU2008137604A/ru not_active Application Discontinuation
- 2007-02-21 CA CA002642778A patent/CA2642778A1/en not_active Abandoned
- 2007-02-21 US US11/708,322 patent/US20070197649A1/en not_active Abandoned
- 2007-02-21 WO PCT/CA2007/000252 patent/WO2007095728A1/en active Application Filing
- 2007-02-21 KR KR1020087023077A patent/KR20080104329A/ko not_active Application Discontinuation
- 2007-02-21 NZ NZ570730A patent/NZ570730A/xx not_active IP Right Cessation
- 2007-02-21 SI SI200731386T patent/SI1991225T1/sl unknown
- 2007-02-21 CN CNA2007800132579A patent/CN101420954A/zh active Pending
- 2007-02-21 BR BRPI0708211-8A patent/BRPI0708211A2/pt not_active IP Right Cessation
- 2007-02-21 MX MX2008010824A patent/MX2008010824A/es active IP Right Grant
- 2007-02-21 PT PT77018000T patent/PT1991225E/pt unknown
- 2007-02-21 EP EP07701800.0A patent/EP1991225B1/en active Active
-
2008
- 2008-08-21 IL IL193598A patent/IL193598A/en not_active IP Right Cessation
- 2008-08-22 TN TNP2008000338A patent/TNSN08338A1/en unknown
- 2008-09-08 MA MA31216A patent/MA30266B1/fr unknown
-
2013
- 2013-01-31 US US13/755,048 patent/US20130190365A1/en not_active Abandoned
Also Published As
Publication number | Publication date |
---|---|
WO2007095728A1 (en) | 2007-08-30 |
MA30266B1 (fr) | 2009-03-02 |
AU2007219009A1 (en) | 2007-08-30 |
KR20080104329A (ko) | 2008-12-02 |
PL1991225T3 (pl) | 2014-04-30 |
NZ570730A (en) | 2013-05-31 |
DK1991225T3 (da) | 2013-12-16 |
TNSN08338A1 (en) | 2009-12-29 |
PT1991225E (pt) | 2014-02-13 |
CA2642778A1 (en) | 2007-08-30 |
SI1991225T1 (sl) | 2014-02-28 |
US20090023784A1 (en) | 2009-01-22 |
EP1991225A1 (en) | 2008-11-19 |
SG170020A1 (en) | 2011-04-29 |
EP1991225B1 (en) | 2013-11-06 |
RS53225B (en) | 2014-08-29 |
RU2008137604A (ru) | 2010-03-27 |
US20130190365A1 (en) | 2013-07-25 |
AU2007219009B2 (en) | 2012-12-20 |
US20070197649A1 (en) | 2007-08-23 |
IL193598A (en) | 2012-08-30 |
MX2008010824A (es) | 2009-06-08 |
BRPI0708211A2 (pt) | 2011-05-17 |
CN101420954A (zh) | 2009-04-29 |
MY151412A (en) | 2014-05-30 |
IL193598A0 (en) | 2009-08-03 |
EP1991225A4 (en) | 2009-07-29 |
JP2009527506A (ja) | 2009-07-30 |
JP5730466B2 (ja) | 2015-06-10 |
ES2441065T3 (es) | 2014-01-31 |
Similar Documents
Publication | Publication Date | Title |
---|---|---|
UA95099C2 (ru) | Применение деферипрона при лечении железо-индуцированного повреждения митохондрий, который является следствием атаксии фридрейха | |
PH12015502628A1 (en) | Pyrazolopyrrolidine derivatives and their use in the treatment of disease | |
MX2015016344A (es) | Derivados de imidazo-pirrolidinona y su uso en el tratamiento de enfermedades. | |
MY163516A (en) | Novel salts and polymorphs of desazadesferrithiocin polyether analogues as metal chelation agents | |
MX2009010407A (es) | Derivados fluorados de deferiprona. | |
HK1120441A1 (en) | Drugs for treatment of ovarian cancer | |
MX2015016421A (es) | Derivados de pirazolo-pirrolidin-4-ona como inhibidores de bet y su uso en el tratamiento de enfermedades. | |
EA201270221A1 (ru) | Лечение болезни крона с применением лаквинимода | |
MX339614B (es) | Uso de ave0010 para la fabricacion de un medicamento para el tratamiento de la diabetes mellitus tipo 2. | |
WO2011140232A3 (en) | Desazadesferrothiocin and desazadesferrothiocin polyether analogues as metal chelation agents | |
WO2011017054A3 (en) | Prodrugs of desazadesferrothiocin polyether analogues as metal chelation agents | |
EA200971086A1 (ru) | Фармацевтические композиции и способ лечения шизофрении | |
BR112012002246A2 (pt) | composto, composto ou sal farmaceutico aceitavel deste, composição farmaceutica, metodo para inibir, tratar e/ou reduzir o declinio cognitivol e/ou doença de akzhmer em um paciente | |
MX350195B (es) | Analogos de cistamina para el tratamiento de la enfermedad de parkinson. | |
EA201391076A1 (ru) | Комбинации | |
MX366353B (es) | Agentes terapeuticos para uso en la profilaxis y/o tratamiento de trastornos de movimiento hipercinetico. | |
HK1163526A1 (en) | A medicament for treating schizophrenia comprising cilostazol | |
CY1115632T1 (el) | Φθοριωμενα παραγωγα 3-υδροξυπυριδιν-4-ονων | |
MX2012012410A (es) | Agente terapeutico y agente preventivo para enfermedad de alzheimer. | |
BR112015008279A2 (pt) | derivado de 6-oxo-1,6-di-hidro-piridazina para uso no tratamento de carcinoma hepatocelular (hcc) | |
SA520411067B1 (ar) | تركيبات صلبة فموية من بيتا هستين ممتدة الإطلاق غير نابضة | |
CY1114714T1 (el) | Η χρηση δεφεριπρονης και μεθοδοι για την θεραπεια και/ή προληψη της αταξιας friedreich που προκυπτει απο ενδοκυτταρικη κακη διαχειριση σιδηρου | |
MX2014002919A (es) | Uso de 3-(r)-[3-(2-metoxifeniltio)-2-(s)-metilpropil] amino-3-dihidro-2h-1,5-benzoxatiepina para el tratamiento de cancer y, en particular para la prevencion y/o tratamiento de metastasis del cancer. |