TW202221123A - 調節ｓｃｎ２ａ之化合物及方法 - Google Patents
調節ｓｃｎ２ａ之化合物及方法 Download PDFInfo
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| JP2023544162A (ja) * | 2020-10-01 | 2023-10-20 | アイオーニス ファーマシューティカルズ， インコーポレーテッド | Ｃｈｍｐ７を調節するための化合物 |
| JP2024518788A (ja) * | 2021-05-10 | 2024-05-02 | キュー－ステート バイオサイエンシーズ， インコーポレイテッド | ナトリウムチャネル１．６を標的とする組成物 |
| WO2023192885A2 (en) * | 2022-03-28 | 2023-10-05 | Praxis Precision Medicines, Inc. | Methods of using oligomeric compounds to treat scn2a-related disorders |
| AU2023348346A1 (en) * | 2022-09-30 | 2025-03-27 | Contera Pharma A/S | Antisense oligonucleotides for the treatment of canavan disease |
| AU2024343201A1 (en) * | 2023-09-15 | 2026-03-26 | Praxis Precision Medicines, Inc. | Elsunersen / prax-222 for use in the treatment of scn2a-related disorders |
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- 2021-08-06 WO PCT/US2021/044887 patent/WO2022032060A2/en not_active Ceased
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| ECSP23008455A (es) | 2023-05-31 |
| US12227746B2 (en) | 2025-02-18 |
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| CN116322707A (zh) | 2023-06-23 |
| US20240102012A1 (en) | 2024-03-28 |
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| CN116322707B (zh) | 2026-02-03 |
| IL300258A (en) | 2023-03-01 |
| AU2021320384A1 (en) | 2023-02-16 |
| CO2023002128A2 (es) | 2023-03-07 |
| KR20230048052A (ko) | 2023-04-10 |
| BR112023002034A2 (pt) | 2023-04-04 |
| CL2024000541A1 (es) | 2024-08-30 |
| JP2023536994A (ja) | 2023-08-30 |
| US20240026353A1 (en) | 2024-01-25 |
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