RU2764920C2 - Способы и композиции для лечения нарушений и заболеваний, связанных с rdh12 - Google Patents

Способы и композиции для лечения нарушений и заболеваний, связанных с rdh12 Download PDF

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RU2764920C2
RU2764920C2 RU2019103488A RU2019103488A RU2764920C2 RU 2764920 C2 RU2764920 C2 RU 2764920C2 RU 2019103488 A RU2019103488 A RU 2019103488A RU 2019103488 A RU2019103488 A RU 2019103488A RU 2764920 C2 RU2764920 C2 RU 2764920C2
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rdh12
aav
sequences
expression
protein
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RU2019103488A
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RU2019103488A3 (enExample
RU2019103488A (ru
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Джин БЕННЕТТ
Цзюньвей СУНЬ
Видиуллата ВАСИРЕДДИ
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Зе Трастис Оф Зе Юниверсити Оф Пенсильвания
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RU2019103488A 2016-07-08 2017-07-07 Способы и композиции для лечения нарушений и заболеваний, связанных с rdh12 RU2764920C2 (ru)

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US201662359777P 2016-07-08 2016-07-08
US62/359,777 2016-07-08
PCT/US2017/041122 WO2018009814A1 (en) 2016-07-08 2017-07-07 Methods and compositions for treatment of disorders and diseases involving rdh12

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RU2019103488A RU2019103488A (ru) 2020-08-10
RU2019103488A3 RU2019103488A3 (enExample) 2021-02-04
RU2764920C2 true RU2764920C2 (ru) 2022-01-24

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US (4) US11197936B2 (enExample)
EP (1) EP3481958A4 (enExample)
JP (2) JP7101656B2 (enExample)
KR (2) KR102526506B1 (enExample)
CN (1) CN110191954B (enExample)
AU (2) AU2017292010B2 (enExample)
BR (1) BR112019000171A2 (enExample)
CA (1) CA3029646A1 (enExample)
IL (3) IL320533A (enExample)
RU (1) RU2764920C2 (enExample)
WO (1) WO2018009814A1 (enExample)

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RU2727411C2 (ru) * 2015-09-24 2020-07-21 Дзе Трастиз Оф Дзе Юниверсити Оф Пенсильвания Композиция и способ для лечения заболевания, опосредованного комплементом
EP3481958A4 (en) * 2016-07-08 2019-12-25 The Trustees of The University of Pennsylvania METHOD AND COMPOSITIONS FOR TREATING DISTURBANCES AND DISEASES WITH RDH12
CA3099004C (en) 2017-05-04 2024-11-12 Univ Lehigh ADDITIVE MANUFACTURING SYSTEM WITH ADJUSTABLE MATERIAL PROPERTIES
AU2018367606B2 (en) 2017-11-15 2024-08-29 The Regents Of The University Of Michigan Viral vectors comprising RDH12 coding regions and methods of treating retinal dystrophies
EP4284335A1 (en) 2021-02-01 2023-12-06 RegenxBio Inc. Gene therapy for neuronal ceroid lipofuscinoses
TR2021022284A2 (tr) * 2021-12-31 2022-01-21 T C Ueskuedar Ueniversitesi Retinitis pigmentosa (rp) hastalığının tedavisinde kullanılmak üzere retinol dehidrojenaz 12 (rdh12) gen mutasyonlarına yönelik crıspr-pe sistemi.
CN115725659A (zh) * 2022-04-01 2023-03-03 首都医科大学附属北京同仁医院 一种应用视网膜原位基因编辑制作非人灵长类动物先天性黑矇模型的方法
JP7168814B1 (ja) 2022-07-01 2022-11-09 東洋インキＳｃホールディングス株式会社 積層体の分離回収方法
CN118453915A (zh) * 2024-04-29 2024-08-09 中国医学科学院北京协和医院 一种针对rdh12突变的基因治疗药物

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