RU2764920C2 - Способы и композиции для лечения нарушений и заболеваний, связанных с rdh12 - Google Patents

Способы и композиции для лечения нарушений и заболеваний, связанных с rdh12 Download PDF

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RU2764920C2
RU2764920C2 RU2019103488A RU2019103488A RU2764920C2 RU 2764920 C2 RU2764920 C2 RU 2764920C2 RU 2019103488 A RU2019103488 A RU 2019103488A RU 2019103488 A RU2019103488 A RU 2019103488A RU 2764920 C2 RU2764920 C2 RU 2764920C2
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rdh12
aav
sequences
expression
protein
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RU2019103488A
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RU2019103488A3 (enExample
RU2019103488A (ru
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Джин БЕННЕТТ
Цзюньвей СУНЬ
Видиуллата ВАСИРЕДДИ
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Зе Трастис Оф Зе Юниверсити Оф Пенсильвания
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RU2019103488A 2016-07-08 2017-07-07 Способы и композиции для лечения нарушений и заболеваний, связанных с rdh12 RU2764920C2 (ru)

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Application Number Priority Date Filing Date Title
US201662359777P 2016-07-08 2016-07-08
US62/359,777 2016-07-08
PCT/US2017/041122 WO2018009814A1 (en) 2016-07-08 2017-07-07 Methods and compositions for treatment of disorders and diseases involving rdh12

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RU2019103488A RU2019103488A (ru) 2020-08-10
RU2019103488A3 RU2019103488A3 (enExample) 2021-02-04
RU2764920C2 true RU2764920C2 (ru) 2022-01-24

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US (4) US11197936B2 (enExample)
EP (1) EP3481958B1 (enExample)
JP (2) JP7101656B2 (enExample)
KR (2) KR102799528B1 (enExample)
CN (1) CN110191954B (enExample)
AU (2) AU2017292010B2 (enExample)
BR (1) BR112019000171A2 (enExample)
CA (1) CA3029646A1 (enExample)
ES (1) ES3069917T3 (enExample)
IL (3) IL264070B2 (enExample)
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EP3359663A4 (en) * 2015-09-24 2019-08-14 The Trustees of The University of Pennsylvania COMPOSITION AND METHOD FOR THE TREATMENT OF A COMPLEMENT-MEDIATED DISEASE
US11197936B2 (en) * 2016-07-08 2021-12-14 The Trustees Of The University Of Pennsylvania Methods and compositions for treatment of disorders and diseases involving RDH12
CA3099004C (en) 2017-05-04 2024-11-12 Lehigh University ADDITIVE MANUFACTURING SYSTEM WITH ADJUSTABLE MATERIAL PROPERTIES
SMT202400321T1 (it) * 2017-11-15 2024-11-15 Univ Michigan Regents Vettori virali comprendenti regioni codificanti rdh12 e metodi di trattamento di distrofie retiniche
MX2023008826A (es) 2021-02-01 2023-09-15 Regenxbio Inc Terapia génica para lipofuscinosis neuronal ceroidea.
EP4457347A4 (en) * 2021-12-31 2026-07-01 T C Uskudar Univ CRISPR-PE SYSTEM FOR RETINOL DEHYDROGENASE 12 (RDH12) GENE MUTATIONS FOR THE TREATMENT OF RETINITIS PIGMENTARIAN (RP)
TR2021022284A2 (tr) * 2021-12-31 2022-01-21 T C Ueskuedar Ueniversitesi Retinitis pigmentosa (rp) hastalığının tedavisinde kullanılmak üzere retinol dehidrojenaz 12 (rdh12) gen mutasyonlarına yönelik crıspr-pe sistemi.
CN115725659A (zh) * 2022-04-01 2023-03-03 首都医科大学附属北京同仁医院 一种应用视网膜原位基因编辑制作非人灵长类动物先天性黑矇模型的方法
JP7168814B1 (ja) 2022-07-01 2022-11-09 東洋インキＳｃホールディングス株式会社 積層体の分離回収方法
CN118453915A (zh) * 2024-04-29 2024-08-09 中国医学科学院北京协和医院 一种针对rdh12突变的基因治疗药物

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