KR102526506B1 - Rdh12가 연루된 장애 및 질환의 치료를 위한 방법 및 조성물 - Google Patents

Rdh12가 연루된 장애 및 질환의 치료를 위한 방법 및 조성물 Download PDF

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KR102526506B1
KR102526506B1 KR1020197003500A KR20197003500A KR102526506B1 KR 102526506 B1 KR102526506 B1 KR 102526506B1 KR 1020197003500 A KR1020197003500 A KR 1020197003500A KR 20197003500 A KR20197003500 A KR 20197003500A KR 102526506 B1 KR102526506 B1 KR 102526506B1
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rdh12
aav
sequence
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eye
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KR20190034221A (ko
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진 베네트
준웨이 순
비디울라다 바시레디
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더 트러스티스 오브 더 유니버시티 오브 펜실베니아
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KR1020197003500A 2016-07-08 2017-07-07 Rdh12가 연루된 장애 및 질환의 치료를 위한 방법 및 조성물 Active KR102526506B1 (ko)

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KR1020237013817A KR102799528B1 (ko) 2016-07-08 2017-07-07 Rdh12가 연루된 장애 및 질환의 치료를 위한 방법 및 조성물

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US201662359777P 2016-07-08 2016-07-08
US62/359,777 2016-07-08
PCT/US2017/041122 WO2018009814A1 (en) 2016-07-08 2017-07-07 Methods and compositions for treatment of disorders and diseases involving rdh12

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KR1020237013817A Division KR102799528B1 (ko) 2016-07-08 2017-07-07 Rdh12가 연루된 장애 및 질환의 치료를 위한 방법 및 조성물

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KR20190034221A KR20190034221A (ko) 2019-04-01
KR102526506B1 true KR102526506B1 (ko) 2023-05-03

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KR1020197003500A Active KR102526506B1 (ko) 2016-07-08 2017-07-07 Rdh12가 연루된 장애 및 질환의 치료를 위한 방법 및 조성물
KR1020237013817A Active KR102799528B1 (ko) 2016-07-08 2017-07-07 Rdh12가 연루된 장애 및 질환의 치료를 위한 방법 및 조성물

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US (4) US11197936B2 (enExample)
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CN (1) CN110191954B (enExample)
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IL (3) IL264070B2 (enExample)
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Families Citing this family (9)

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IL258024B2 (en) * 2015-09-24 2023-03-01 Univ Pennsylvania A preparation and method for the treatment of a complement-mediated disease
IL264070B2 (en) 2016-07-08 2023-03-01 Univ Pennsylvania Methods and preparations for the treatment of disorders and diseases involving rdh12
EP3619019A4 (en) 2017-05-04 2021-01-20 Lehigh University ADDITIVE MANUFACTURING SYSTEM WITH ADJUSTABLE MATERIAL PROPERTIES
WO2019099696A1 (en) 2017-11-15 2019-05-23 The Regents Of The University Of Michigan Viral vectors comprising rdh12 coding regions and methods of treating retinal dystrophies
CA3209779A1 (en) 2021-02-01 2022-08-04 Regenxbio Inc. Gene therapy for neuronal ceroid lipofuscinoses
TR2021022284A2 (tr) * 2021-12-31 2022-01-21 T C Ueskuedar Ueniversitesi Retinitis pigmentosa (rp) hastalığının tedavisinde kullanılmak üzere retinol dehidrojenaz 12 (rdh12) gen mutasyonlarına yönelik crıspr-pe sistemi.
CN115725659A (zh) * 2022-04-01 2023-03-03 首都医科大学附属北京同仁医院 一种应用视网膜原位基因编辑制作非人灵长类动物先天性黑矇模型的方法
JP7168814B1 (ja) 2022-07-01 2022-11-09 東洋インキＳｃホールディングス株式会社 積層体の分離回収方法
CN118453915A (zh) * 2024-04-29 2024-08-09 中国医学科学院北京协和医院 一种针对rdh12突变的基因治疗药物

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