RU2763319C2 - Реагенты для лечения окулофарингеальной мышечной дистрофии (офмд) и их применение - Google Patents

Реагенты для лечения окулофарингеальной мышечной дистрофии (офмд) и их применение Download PDF

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RU2763319C2
RU2763319C2 RU2019121950A RU2019121950A RU2763319C2 RU 2763319 C2 RU2763319 C2 RU 2763319C2 RU 2019121950 A RU2019121950 A RU 2019121950A RU 2019121950 A RU2019121950 A RU 2019121950A RU 2763319 C2 RU2763319 C2 RU 2763319C2
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sequence
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RU2019121950A3 (enExample
RU2019121950A (ru
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Ванесса СТРИНГЗ-УФОМБАХ
Дэвид СЬЮХИ
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Бенитек АйПи Холдингз Инк.
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RU2019121950A 2016-12-14 2017-12-14 Реагенты для лечения окулофарингеальной мышечной дистрофии (офмд) и их применение RU2763319C2 (ru)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US201662434312P 2016-12-14 2016-12-14
US62/434,312 2016-12-14
PCT/AU2017/051385 WO2018107228A1 (en) 2016-12-14 2017-12-14 Reagents for treatment of oculopharyngeal muscular dystrophy (opmd) and use thereof

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RU2019121950A3 RU2019121950A3 (enExample) 2021-01-18
RU2019121950A RU2019121950A (ru) 2021-01-18
RU2763319C2 true RU2763319C2 (ru) 2021-12-28

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US (2) US11142765B2 (enExample)
EP (1) EP3555294A4 (enExample)
JP (2) JP7233149B2 (enExample)
KR (2) KR102495222B1 (enExample)
CN (2) CN110382698B (enExample)
AU (2) AU2017377661B2 (enExample)
CA (1) CA3047154A1 (enExample)
IL (2) IL267353B2 (enExample)
MX (2) MX2019007110A (enExample)
RU (1) RU2763319C2 (enExample)
WO (1) WO2018107228A1 (enExample)
ZA (1) ZA202106827B (enExample)

Families Citing this family (5)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
KR102495222B1 (ko) 2016-12-14 2023-02-09 베니텍 아이피 홀딩스 아이엔씨. 안구인두근위축증 (opmd)의 치료제 및 이의 사용
EP3866859A4 (en) * 2018-10-17 2023-08-09 Benitec IP Holdings Inc. METHODS OF TREATMENT FOR OCULOPHARYNGEAL MUSCULAR DYSTROPHY (OPMD)
CA3130221A1 (en) 2019-02-28 2020-09-03 Benitec IP Holdings Inc. Compositions and methods for treating oculopharyngeal muscular dystrophy (opmd)
AU2020414441A1 (en) * 2019-12-23 2022-08-18 Versameb Ag Compositions and methods for simultaneously modulating expression of genes
WO2026011009A1 (en) * 2024-07-02 2026-01-08 Kate Therapeutics, Inc. Compositions and methods for muscle disorders

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WO2008150897A2 (en) * 2007-05-31 2008-12-11 University Of Iowa Research Foundation Reduction of off-target rna interference toxicity
RU2659423C2 (ru) * 2012-02-16 2018-07-02 ЭйТИР ФАРМА, ИНК. ГИСТИДИЛ-тРНК-СИНТЕТАЗЫ ДЛЯ ЛЕЧЕНИЯ АУТОИММУННЫХ И ВОСПАЛИТЕЛЬНЫХ ЗАБОЛЕВАНИЙ

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EP1783645A1 (en) * 2005-11-08 2007-05-09 Actigenics Methods for the identification of microRNA and their applications in research and human health
WO2008092935A2 (en) * 2007-01-31 2008-08-07 Basf Plant Science Gmbh Plants having enhanced yield-related traits and/or increased abiotic stress resistance, and a method for making the same
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AU2017250017B2 (en) * 2016-04-14 2022-12-22 Benitec IP Holdings Inc. Reagents for treatment of oculopharyngeal muscular dystrophy (OPMD) and use thereof
KR102495222B1 (ko) * 2016-12-14 2023-02-09 베니텍 아이피 홀딩스 아이엔씨. 안구인두근위축증 (opmd)의 치료제 및 이의 사용

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WO2008150897A2 (en) * 2007-05-31 2008-12-11 University Of Iowa Research Foundation Reduction of off-target rna interference toxicity
RU2659423C2 (ru) * 2012-02-16 2018-07-02 ЭйТИР ФАРМА, ИНК. ГИСТИДИЛ-тРНК-СИНТЕТАЗЫ ДЛЯ ЛЕЧЕНИЯ АУТОИММУННЫХ И ВОСПАЛИТЕЛЬНЫХ ЗАБОЛЕВАНИЙ

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AU2017377661A1 (en) 2019-07-18
IL267353B1 (en) 2023-08-01
CN110382698A (zh) 2019-10-25
JP7233149B2 (ja) 2023-03-06
AU2023222827A1 (en) 2023-09-14
IL267353B2 (en) 2023-12-01
BR112019012312A8 (pt) 2023-02-28
EP3555294A4 (en) 2020-08-26
IL304674A (en) 2023-09-01
US11142765B2 (en) 2021-10-12
AU2023222827B2 (en) 2025-02-27
IL267353A (en) 2019-08-29
MX2019007110A (es) 2019-12-05
ZA202106827B (en) 2022-07-27
KR102495222B1 (ko) 2023-02-09
US11932852B2 (en) 2024-03-19
IL304674B1 (en) 2024-07-01
CN118421624A (zh) 2024-08-02
AU2017377661B2 (en) 2023-07-27
US20190330629A1 (en) 2019-10-31
JP7431359B2 (ja) 2024-02-14
KR20190104151A (ko) 2019-09-06
RU2019121950A3 (enExample) 2021-01-18
KR20230020586A (ko) 2023-02-10
KR102667867B1 (ko) 2024-05-29
CN110382698B (zh) 2024-05-10
MX2024003643A (es) 2024-04-15
WO2018107228A1 (en) 2018-06-21
BR112019012312A2 (pt) 2020-02-11
JP2020503014A (ja) 2020-01-30
JP2023062092A (ja) 2023-05-02
EP3555294A1 (en) 2019-10-23
RU2019121950A (ru) 2021-01-18
CA3047154A1 (en) 2018-06-21
US20220056446A1 (en) 2022-02-24
IL304674B2 (en) 2024-11-01

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