RU2742612C2 - Векторы на основе аденоассоциированного вируса для лечения муколипидоза типа ii - Google Patents

Векторы на основе аденоассоциированного вируса для лечения муколипидоза типа ii Download PDF

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RU2742612C2
RU2742612C2 RU2018124448A RU2018124448A RU2742612C2 RU 2742612 C2 RU2742612 C2 RU 2742612C2 RU 2018124448 A RU2018124448 A RU 2018124448A RU 2018124448 A RU2018124448 A RU 2018124448A RU 2742612 C2 RU2742612 C2 RU 2742612C2
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aav
raav
gnptab
nucleic acid
iii
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Нельсон ЙЮ
Донг-Киу ДЗИН
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Джензим Корпорейшн
Самсунг Лайф Паблик Уэлфэр Фаундейшн
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RU2018124448A 2015-12-15 2016-12-14 Векторы на основе аденоассоциированного вируса для лечения муколипидоза типа ii RU2742612C2 (ru)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US201562267502P 2015-12-15 2015-12-15
US62/267,502 2015-12-15
PCT/US2016/066611 WO2017106313A1 (en) 2015-12-15 2016-12-14 Adeno-associated viral vectors for treating mucolipidosis type ii

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RU2018124448A RU2018124448A (ru) 2020-01-17
RU2018124448A3 RU2018124448A3 (https=) 2020-08-14
RU2742612C2 true RU2742612C2 (ru) 2021-02-09

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US (1) US20200261598A1 (https=)
EP (1) EP3390644B1 (https=)
JP (3) JP7347932B2 (https=)
KR (1) KR102833376B1 (https=)
CN (1) CN108603199A (https=)
AU (2) AU2016372035B2 (https=)
CA (1) CA3008268A1 (https=)
ES (1) ES2991277T3 (https=)
IL (1) IL259964B (https=)
MX (1) MX2018007330A (https=)
RU (1) RU2742612C2 (https=)
SG (2) SG11201804994QA (https=)
WO (1) WO2017106313A1 (https=)

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WO2020106916A1 (en) * 2018-11-21 2020-05-28 Stridebio, Inc. Recombinant viral vectors and nucleic acids for producing the same
CA3158131A1 (en) * 2019-10-18 2021-04-22 Nicolas Sebastien Wein Materials and methods for the treatment of disorders associated mutations in the irf2bpl gene
EP4103214B1 (en) * 2020-02-13 2026-04-29 Tenaya Therapeutics, Inc. Gene therapy vectors for treating heart disease

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