RU2742612C2 - Векторы на основе аденоассоциированного вируса для лечения муколипидоза типа ii - Google Patents

Векторы на основе аденоассоциированного вируса для лечения муколипидоза типа ii Download PDF

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RU2742612C2
RU2742612C2 RU2018124448A RU2018124448A RU2742612C2 RU 2742612 C2 RU2742612 C2 RU 2742612C2 RU 2018124448 A RU2018124448 A RU 2018124448A RU 2018124448 A RU2018124448 A RU 2018124448A RU 2742612 C2 RU2742612 C2 RU 2742612C2
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aav
raav
gnptab
nucleic acid
iii
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RU2018124448A3 (OSRAM
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Нельсон ЙЮ
Донг-Киу ДЗИН
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Джензим Корпорейшн
Самсунг Лайф Паблик Уэлфэр Фаундейшн
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RU2018124448A 2015-12-15 2016-12-14 Векторы на основе аденоассоциированного вируса для лечения муколипидоза типа ii RU2742612C2 (ru)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US201562267502P 2015-12-15 2015-12-15
US62/267,502 2015-12-15
PCT/US2016/066611 WO2017106313A1 (en) 2015-12-15 2016-12-14 Adeno-associated viral vectors for treating mucolipidosis type ii

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RU2018124448A RU2018124448A (ru) 2020-01-17
RU2018124448A3 RU2018124448A3 (OSRAM) 2020-08-14
RU2742612C2 true RU2742612C2 (ru) 2021-02-09

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US (1) US20200261598A1 (OSRAM)
EP (1) EP3390644B1 (OSRAM)
JP (3) JP7347932B2 (OSRAM)
KR (1) KR102833376B1 (OSRAM)
CN (1) CN108603199A (OSRAM)
AU (2) AU2016372035B2 (OSRAM)
CA (1) CA3008268A1 (OSRAM)
ES (1) ES2991277T3 (OSRAM)
IL (1) IL259964B (OSRAM)
MX (1) MX2018007330A (OSRAM)
RU (1) RU2742612C2 (OSRAM)
SG (2) SG10201912935WA (OSRAM)
WO (1) WO2017106313A1 (OSRAM)

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AU2019385506A1 (en) * 2018-11-21 2021-06-03 Takeda Pharmaceutical Company Limited Recombinant viral vectors and nucleic acids for producing the same
WO2021077101A1 (en) 2019-10-18 2021-04-22 Research Institute At Nationwide Children's Hospital Materials and methods for the treatment of disorders associated mutations in the irf2bpl gene
MX2022009883A (es) * 2020-02-13 2022-10-03 Tenaya Therapeutics Inc Vectores de genoterapia para tratar enfermedades cardíacas.

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* Cited by examiner, † Cited by third party
Title
https://www.ncbi.nlm.nih.gov/gene/79158 от 05.09.2009 (согласно интернет архиву Wayback Machine) [Найдено в интернет 14.08.2020]. DataBasa GenBank: AHD72821.1 от 23.12.2013 [Найдено в интернет 14.08.2020]. *

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