KR102833376B1 - 뮤코지질증 ii형을 치료하기 위한 아데노-관련 바이러스 벡터 - Google Patents

뮤코지질증 ii형을 치료하기 위한 아데노-관련 바이러스 벡터 Download PDF

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KR102833376B1
KR102833376B1 KR1020187019970A KR20187019970A KR102833376B1 KR 102833376 B1 KR102833376 B1 KR 102833376B1 KR 1020187019970 A KR1020187019970 A KR 1020187019970A KR 20187019970 A KR20187019970 A KR 20187019970A KR 102833376 B1 KR102833376 B1 KR 102833376B1
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넬슨 유
동-규 진
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젠자임 코포레이션
사회복지법인 삼성생명공익재단
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KR1020187019970A 2015-12-15 2016-12-14 뮤코지질증 ii형을 치료하기 위한 아데노-관련 바이러스 벡터 Active KR102833376B1 (ko)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US201562267502P 2015-12-15 2015-12-15
US62/267,502 2015-12-15
PCT/US2016/066611 WO2017106313A1 (en) 2015-12-15 2016-12-14 Adeno-associated viral vectors for treating mucolipidosis type ii

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KR20180098294A KR20180098294A (ko) 2018-09-03
KR102833376B1 true KR102833376B1 (ko) 2025-07-11

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US (1) US20200261598A1 (OSRAM)
EP (1) EP3390644B1 (OSRAM)
JP (3) JP7347932B2 (OSRAM)
KR (1) KR102833376B1 (OSRAM)
CN (1) CN108603199A (OSRAM)
AU (2) AU2016372035B2 (OSRAM)
CA (1) CA3008268A1 (OSRAM)
ES (1) ES2991277T3 (OSRAM)
IL (1) IL259964B (OSRAM)
MX (1) MX2018007330A (OSRAM)
RU (1) RU2742612C2 (OSRAM)
SG (2) SG10201912935WA (OSRAM)
WO (1) WO2017106313A1 (OSRAM)

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WO2021077101A1 (en) 2019-10-18 2021-04-22 Research Institute At Nationwide Children's Hospital Materials and methods for the treatment of disorders associated mutations in the irf2bpl gene
MX2022009883A (es) * 2020-02-13 2022-10-03 Tenaya Therapeutics Inc Vectores de genoterapia para tratar enfermedades cardíacas.

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