MX2019005588A - Metodos para modular corte y empalme de arn. - Google Patents

Metodos para modular corte y empalme de arn.

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Publication number
MX2019005588A
MX2019005588A MX2019005588A MX2019005588A MX2019005588A MX 2019005588 A MX2019005588 A MX 2019005588A MX 2019005588 A MX2019005588 A MX 2019005588A MX 2019005588 A MX2019005588 A MX 2019005588A MX 2019005588 A MX2019005588 A MX 2019005588A
Authority
MX
Mexico
Prior art keywords
methods
gene
another aspect
intronic
rna transcript
Prior art date
Application number
MX2019005588A
Other languages
English (en)
Spanish (es)
Inventor
Dakka Amal
Bhattacharyya Anuradha
EFFENBERGER Kerstin
Gabbeta Vijayalakshmi
Li Wencheng
Naryshkin Nikolai
Trotta Christopher
WIEDINGER Kari
Original Assignee
Ptc Therapeutics Inc
Priority date (The priority date is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the date listed.)
Filing date
Publication date
Application filed by Ptc Therapeutics Inc filed Critical Ptc Therapeutics Inc
Publication of MX2019005588A publication Critical patent/MX2019005588A/es

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MX2019005588A 2016-11-28 2017-11-27 Metodos para modular corte y empalme de arn. MX2019005588A (es)

Applications Claiming Priority (2)

Application Number Priority Date Filing Date Title
US201662426619P 2016-11-28 2016-11-28
PCT/US2017/063323 WO2018098446A1 (en) 2016-11-28 2017-11-27 Methods for modulating rna splicing

Publications (1)

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MX2019005588A true MX2019005588A (es) 2019-10-15

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US (2) US11702646B2 (cg-RX-API-DMAC7.html)
EP (1) EP3544435A4 (cg-RX-API-DMAC7.html)
JP (2) JP2019535789A (cg-RX-API-DMAC7.html)
CN (1) CN110352007A (cg-RX-API-DMAC7.html)
AU (1) AU2017363369A1 (cg-RX-API-DMAC7.html)
CA (1) CA3043755A1 (cg-RX-API-DMAC7.html)
EA (1) EA201991309A1 (cg-RX-API-DMAC7.html)
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EP4249472A3 (en) 2015-05-30 2023-12-13 PTC Therapeutics, Inc. Methods for modulating rna splicing
CN110352007A (zh) 2016-11-28 2019-10-18 Ptc医疗公司 用于调节rna剪接的方法
CN111372611A (zh) 2017-06-14 2020-07-03 Ptc医疗公司 修饰rna剪接的方法
IL272413B (en) 2017-08-04 2022-09-01 Skyhawk Therapeutics Inc Methods and compositions for modulating splicing
EP3833357A4 (en) * 2018-08-07 2022-06-08 The Children's Hospital of Philadelphia REGULATION OF GENE EXPRESSION BY ALTERNATIVE SPLICING, AND THERAPEUTIC METHODS
WO2020076892A1 (en) * 2018-10-09 2020-04-16 The University Of North Carolina At Chapel Hill Regulated gene editing system
CN114007613A (zh) 2019-02-05 2022-02-01 斯基霍克疗法公司 用于调节剪接的方法和组合物
EP3920928A4 (en) 2019-02-06 2022-09-28 Skyhawk Therapeutics, Inc. METHODS AND COMPOSITIONS FOR MODULATION OF SPLICING
US11129829B2 (en) 2019-06-17 2021-09-28 Skyhawk Therapeutics, Inc. Methods for modulating splicing
US20220307053A1 (en) 2019-07-25 2022-09-29 Novartis Ag Regulatable expression systems
WO2021034985A1 (en) * 2019-08-19 2021-02-25 Stoke Therapeutics, Inc. Compositions and methods for modulating splicing and protein expression
IL293340A (en) 2019-12-02 2022-07-01 Storm Therapeutics Ltd Polyheterocyclic compounds as mettl3 inhibitors
AU2021218807A1 (en) * 2020-02-12 2022-09-15 The Children's Hospital Of Philadelphia Compositions and methods for inducible alternative splicing regulation of gene expression
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