KR20260048369A - 알부민 좌위로부터 트랜스진을 발현하기 위한 조성물 및 방법 - Google Patents

알부민 좌위로부터 트랜스진을 발현하기 위한 조성물 및 방법

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Publication number
KR20260048369A
KR20260048369A KR1020267010209A KR20267010209A KR20260048369A KR 20260048369 A KR20260048369 A KR 20260048369A KR 1020267010209 A KR1020267010209 A KR 1020267010209A KR 20267010209 A KR20267010209 A KR 20267010209A KR 20260048369 A KR20260048369 A KR 20260048369A
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South Korea
Prior art keywords
sequence
seq
nucleic acid
rna
guide rna
Prior art date
Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
Pending
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KR1020267010209A
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English (en)
Korean (ko)
Inventor
조나단 더글라스 핀
혼-렌 황
모이트리 로이
케디 라이
레이첼 새틀러
크리스토스 카이랏사우스
청 왕
Original Assignee
인텔리아 테라퓨틱스, 인크.
리제너론 파마슈티칼스 인코포레이티드
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Application filed by 인텔리아 테라퓨틱스, 인크., 리제너론 파마슈티칼스 인코포레이티드 filed Critical 인텔리아 테라퓨틱스, 인크.
Publication of KR20260048369A publication Critical patent/KR20260048369A/ko
Pending legal-status Critical Current

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    • A61K48/0025—Medicinal preparations containing genetic material which is inserted into cells of the living body to treat genetic diseases; Gene therapy characterised by an aspect of the 'non-active' part of the composition delivered, e.g. wherein such 'non-active' part is not delivered simultaneously with the 'active' part of the composition wherein the non-active part clearly interacts with the delivered nucleic acid
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    • A—HUMAN NECESSITIES
    • A01—AGRICULTURE; FORESTRY; ANIMAL HUSBANDRY; HUNTING; TRAPPING; FISHING
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    • A01K2207/15—Humanized animals
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KR1020267010209A 2018-10-18 2019-10-18 알부민 좌위로부터 트랜스진을 발현하기 위한 조성물 및 방법 Pending KR20260048369A (ko)

Applications Claiming Priority (6)

Application Number Priority Date Filing Date Title
US201862747402P 2018-10-18 2018-10-18
US62/747,402 2018-10-18
US201962840346P 2019-04-29 2019-04-29
US62/840,346 2019-04-29
PCT/US2019/057086 WO2020082042A2 (en) 2018-10-18 2019-10-18 Compositions and methods for transgene expression from an albumin locus
KR1020217014887A KR102949204B1 (ko) 2018-10-18 2019-10-18 알부민 좌위로부터 트랜스진을 발현하기 위한 조성물 및 방법

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KR1020217014887A Division KR102949204B1 (ko) 2018-10-18 2019-10-18 알부민 좌위로부터 트랜스진을 발현하기 위한 조성물 및 방법

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KR20260048369A true KR20260048369A (ko) 2026-04-09

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KR1020267010209A Pending KR20260048369A (ko) 2018-10-18 2019-10-18 알부민 좌위로부터 트랜스진을 발현하기 위한 조성물 및 방법
KR1020217014887A Active KR102949204B1 (ko) 2018-10-18 2019-10-18 알부민 좌위로부터 트랜스진을 발현하기 위한 조성물 및 방법

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US (3) US20200270617A1 (enExample)
EP (1) EP3867381A2 (enExample)
JP (2) JP7472121B2 (enExample)
KR (2) KR20260048369A (enExample)
CN (1) CN114207130A (enExample)
AU (2) AU2019361203B2 (enExample)
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