KR20240151726A - 판코니 빈혈 환자를 위한 유전자 치료 - Google Patents

판코니 빈혈 환자를 위한 유전자 치료 Download PDF

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KR20240151726A
KR20240151726A KR1020247018425A KR20247018425A KR20240151726A KR 20240151726 A KR20240151726 A KR 20240151726A KR 1020247018425 A KR1020247018425 A KR 1020247018425A KR 20247018425 A KR20247018425 A KR 20247018425A KR 20240151726 A KR20240151726 A KR 20240151726A
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cells
sequence
cell
fanca
vector
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Korean (ko)
Inventor
후안 에이. 부에렌
파울라 리오
수산나 나바로
줄리안 세빌라
호세 카를로스 세고비아
아프리카 곤잘레스
호세 안토니오 카사도
기예르모 구네셰아
Original Assignee
센트로 데 인베스띠가씨오네스 에너제티까스 메디오암비엔딸레스 와이 테크놀로지까스, 오.에이., 엠.피.
푼다시안 인스티튜토 데 인베스티카시온 사니타리아 푼다시안 시메네스 디아즈
콘소르시오 센트로 데 인베스티카시온 비오메디카 엔 레드
푼다시온 파라 라 인베스티게시온 바이오메디카 델 호스피탈 인판틸 유니베르시타리오 니노 지저스
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Application filed by 센트로 데 인베스띠가씨오네스 에너제티까스 메디오암비엔딸레스 와이 테크놀로지까스, 오.에이., 엠.피., 푼다시안 인스티튜토 데 인베스티카시온 사니타리아 푼다시안 시메네스 디아즈, 콘소르시오 센트로 데 인베스티카시온 비오메디카 엔 레드, 푼다시온 파라 라 인베스티게시온 바이오메디카 델 호스피탈 인판틸 유니베르시타리오 니노 지저스 filed Critical 센트로 데 인베스띠가씨오네스 에너제티까스 메디오암비엔딸레스 와이 테크놀로지까스, 오.에이., 엠.피.
Publication of KR20240151726A publication Critical patent/KR20240151726A/ko
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KR1020247018425A 2016-09-08 2017-09-08 판코니 빈혈 환자를 위한 유전자 치료 Ceased KR20240151726A (ko)

Applications Claiming Priority (6)

Application Number Priority Date Filing Date Title
US201662385185P 2016-09-08 2016-09-08
US62/385,185 2016-09-08
US201662412028P 2016-10-24 2016-10-24
US62/412,028 2016-10-24
PCT/US2017/050837 WO2018049273A1 (en) 2016-09-08 2017-09-08 Gene therapy for patients with fanconi anemia
KR1020197009772A KR102672636B1 (ko) 2016-09-08 2017-09-08 판코니 빈혈 환자를 위한 유전자 치료

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US (2) US20190203225A1 (enExample)
EP (1) EP3510162A4 (enExample)
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CN (1) CN110536966A (enExample)
AU (3) AU2017322511B2 (enExample)
CA (1) CA3035605A1 (enExample)
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