CN110536966A - 用于范可尼贫血患者的基因疗法 - Google Patents

用于范可尼贫血患者的基因疗法 Download PDF

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Publication number
CN110536966A
CN110536966A CN201780068686.XA CN201780068686A CN110536966A CN 110536966 A CN110536966 A CN 110536966A CN 201780068686 A CN201780068686 A CN 201780068686A CN 110536966 A CN110536966 A CN 110536966A
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sequence
cells
cell
fanca
leu
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J·A·布埃伦
P·里奥
S·纳瓦罗
J·塞维拉
J·C·塞格维亚
A·冈萨雷兹
J·A·卡萨多
G·古奈查
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Biomedical Network Research Consortium Center MP
Fundacion Para La Investigacion Biomedica Del Hospital Infantil Universitario Nino Jesus
Centro de Investigaciones Energeticas Medioambientales y Tecnologicas CIEMAT
Instituto de Investigacion Sanitaria Fundacion Jimenez Diaz
Original Assignee
Biomedical Network Research Consortium Center MP
Fundacion Para La Investigacion Biomedica Del Hospital Infantil Universitario Nino Jesus
Centro de Investigaciones Energeticas Medioambientales y Tecnologicas CIEMAT
Instituto de Investigacion Sanitaria Fundacion Jimenez Diaz
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Publication of CN110536966A publication Critical patent/CN110536966A/zh
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CN201780068686.XA 2016-09-08 2017-09-08 用于范可尼贫血患者的基因疗法 Pending CN110536966A (zh)

Applications Claiming Priority (5)

Application Number Priority Date Filing Date Title
US201662385185P 2016-09-08 2016-09-08
US62/385,185 2016-09-08
US201662412028P 2016-10-24 2016-10-24
US62/412,028 2016-10-24
PCT/US2017/050837 WO2018049273A1 (en) 2016-09-08 2017-09-08 Gene therapy for patients with fanconi anemia

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CN110536966A true CN110536966A (zh) 2019-12-03

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US (1) US20190203225A1 (enExample)
EP (1) EP3510162A4 (enExample)
JP (3) JP7197466B2 (enExample)
KR (2) KR102672636B1 (enExample)
CN (1) CN110536966A (enExample)
AU (3) AU2017322511B2 (enExample)
CA (1) CA3035605A1 (enExample)
IL (2) IL320371A (enExample)
MX (1) MX2019002699A (enExample)
SG (1) SG11201901718VA (enExample)
WO (1) WO2018049273A1 (enExample)

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CN111163810B (zh) 2017-10-16 2024-09-10 能源环境和技术研究中心O.A.,M.P. 用于递送pklr以治疗丙酮酸激酶缺乏症的慢病毒载体
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CN110904102A (zh) * 2018-09-18 2020-03-24 中国科学院上海生命科学研究院 一种用于重组蛋白质表达的启动子
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CA3185267A1 (en) 2020-08-07 2022-02-10 Spacecraft Seven, Llc Plakophilin-2 (pkp2) gene therapy using aav vector
CA3213792A1 (en) 2021-04-26 2022-11-03 Jonathan Thon Compositions and methods related to megakaryocyte-derived extracellular vesicles for fanconi anemia
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