KR20230088393A - 재조합 아데노 연관 바이러스 조성물 및 이의 제조 방법 - Google Patents
재조합 아데노 연관 바이러스 조성물 및 이의 제조 방법 Download PDFInfo
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- C12N2750/00011—Details
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- C12N2750/14111—Dependovirus, e.g. adenoassociated viruses
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| PCT/US2021/055243 WO2022082017A2 (en) | 2020-10-15 | 2021-10-15 | Recombinant adeno-associated virus compositions and methods for producing same |
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| EP4615981A1 (en) | 2022-11-11 | 2025-09-17 | Eli Lilly and Company | Synthetic nucleic acids including astrocyte-directed promoter constructs and methods of using the same |
| CN116350801A (zh) * | 2022-11-22 | 2023-06-30 | 四川至善唯新生物科技有限公司 | 一种重组腺相关病毒载体的药物组合物及其用途 |
| TW202432839A (zh) * | 2022-12-06 | 2024-08-16 | 美商再生元醫藥公司 | 用於確定病毒載體基因體滴度之液滴式數位ｐｃｒ分析 |
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| WO2026043765A1 (en) | 2024-08-21 | 2026-02-26 | Eli Lilly And Company | Engineered regulatory splice elements for gene therapies |
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| WO2007084773A2 (en) * | 2006-01-20 | 2007-07-26 | University Of North Carolina At Chapel Hill | Enhanced production of infectious parvovirus vectors in insect cells |
| EP3387138B1 (en) * | 2015-12-11 | 2022-01-26 | The Trustees Of The University Of Pennsylvania | Scalable purification method for aav9 |
| CN106916793B (zh) * | 2015-12-24 | 2019-01-15 | 中国科学院武汉物理与数学研究所 | 一种重组腺相关病毒的制备方法及重组杆状病毒 |
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| BR112020006671A2 (pt) | 2017-10-03 | 2020-12-01 | Prevail Therapeutics, Inc. | terapias genéticas para distúrbios lisossômicos |
| KR102709597B1 (ko) * | 2017-10-03 | 2024-09-26 | 프리베일 테라퓨틱스, 인크. | 리소좀 장애를 위한 유전자 요법 |
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| MX2020004830A (es) * | 2017-11-08 | 2020-11-11 | Avexis Inc | Medios y metodo para preparar vectores virales y usos de los mismos. |
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| AU2021359852A1 (en) | 2023-06-08 |
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