KR20220004648A - Ttr 가이드 rna, 및 rna-가이드 dna 결합제를 암호화하는 폴리뉴클레오티드를 포함하는 조성물 및 방법 - Google Patents

Ttr 가이드 rna, 및 rna-가이드 dna 결합제를 암호화하는 폴리뉴클레오티드를 포함하는 조성물 및 방법 Download PDF

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KR20220004648A
KR20220004648A KR1020217035004A KR20217035004A KR20220004648A KR 20220004648 A KR20220004648 A KR 20220004648A KR 1020217035004 A KR1020217035004 A KR 1020217035004A KR 20217035004 A KR20217035004 A KR 20217035004A KR 20220004648 A KR20220004648 A KR 20220004648A
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lipid
composition
seq
rna
ttr
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Korean (ko)
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용 창
세스 씨. 알렉산더
크리스티 엠. 우드
아티 마헨드라 프라카쉬 칸졸리아
쇼부 오다테
제시카 린 시쳐
레이날드 마이클 레스카뷰
월터 스트랩스
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인텔리아 테라퓨틱스, 인크.
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KR1020217035004A 2019-03-28 2020-03-27 Ttr 가이드 rna, 및 rna-가이드 dna 결합제를 암호화하는 폴리뉴클레오티드를 포함하는 조성물 및 방법 Pending KR20220004648A (ko)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US201962825637P 2019-03-28 2019-03-28
US62/825,637 2019-03-28
PCT/US2020/025513 WO2020198697A1 (en) 2019-03-28 2020-03-27 Compositions and methods comprising a ttr guide rna and a polynucleotide encoding an rna-guided dna binding agent

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KR20220004648A true KR20220004648A (ko) 2022-01-11

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KR1020217035004A Pending KR20220004648A (ko) 2019-03-28 2020-03-27 Ttr 가이드 rna, 및 rna-가이드 dna 결합제를 암호화하는 폴리뉴클레오티드를 포함하는 조성물 및 방법

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US (2) US20230044994A1 (https=)
EP (1) EP3946598A1 (https=)
JP (2) JP7631215B2 (https=)
KR (1) KR20220004648A (https=)
CN (1) CN113874076A (https=)
AU (1) AU2020244887A1 (https=)
BR (1) BR112021019196A2 (https=)
CA (1) CA3134271A1 (https=)
CO (1) CO2021014559A2 (https=)
EA (1) EA202192636A1 (https=)
IL (1) IL286524A (https=)
MX (1) MX2021011565A (https=)
PH (1) PH12021552301A1 (https=)
SG (1) SG11202110434PA (https=)
WO (1) WO2020198697A1 (https=)

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CA3134271A1 (en) 2020-10-01
WO2020198697A1 (en) 2020-10-01
IL286524A (en) 2021-10-31
AU2020244887A1 (en) 2021-11-11
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BR112021019196A2 (pt) 2022-01-18
SG11202110434PA (en) 2021-10-28
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