KR20210148232A - 조작된 캡시드를 갖는 아데노-연관 바이러스 - Google Patents

조작된 캡시드를 갖는 아데노-연관 바이러스 Download PDF

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KR20210148232A
KR20210148232A KR1020217035010A KR20217035010A KR20210148232A KR 20210148232 A KR20210148232 A KR 20210148232A KR 1020217035010 A KR1020217035010 A KR 1020217035010A KR 20217035010 A KR20217035010 A KR 20217035010A KR 20210148232 A KR20210148232 A KR 20210148232A
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seq
capsid protein
cardiac
raav virion
raav
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크리스토퍼 에이. 레이드
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테나야 테라퓨틱스, 인코포레이티드
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KR1020217035010A 2019-04-01 2020-03-31 조작된 캡시드를 갖는 아데노-연관 바이러스 Ceased KR20210148232A (ko)

Applications Claiming Priority (5)

Application Number Priority Date Filing Date Title
US201962827576P 2019-04-01 2019-04-01
US62/827,576 2019-04-01
US202062984197P 2020-03-02 2020-03-02
US62/984,197 2020-03-02
PCT/US2020/026009 WO2020205889A1 (en) 2019-04-01 2020-03-31 Adeno-associated virus with engineered capsid

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KR20210148232A true KR20210148232A (ko) 2021-12-07

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KR1020217035010A Ceased KR20210148232A (ko) 2019-04-01 2020-03-31 조작된 캡시드를 갖는 아데노-연관 바이러스

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US (3) US20220154217A1 (https=)
EP (1) EP3947700A4 (https=)
JP (1) JP7630176B2 (https=)
KR (1) KR20210148232A (https=)
CN (1) CN114450411A (https=)
AU (1) AU2020253435A1 (https=)
CA (1) CA3135609A1 (https=)
IL (1) IL286831A (https=)
SG (1) SG11202110607WA (https=)
WO (1) WO2020205889A1 (https=)

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TW202246505A (zh) * 2021-03-05 2022-12-01 俄羅斯聯邦商亞那拜恩有限公司 編碼凝血因子ｉｘ蛋白的密碼子優化的核酸及其用途
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TW202400798A (zh) * 2022-04-11 2024-01-01 美商特納亞治療股份有限公司 斑菲素蛋白—２（ｐｌａｋｏｐｈｉｌｌｉｎ—２）基因療法之治療方法
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