KR20210127206A - 유전성 질환의 치료를 위한 것을 포함하는, 아데노신 데아미나제 염기 편집기를 사용하여 질환-관련 유전자를 편집하는 방법 - Google Patents

유전성 질환의 치료를 위한 것을 포함하는, 아데노신 데아미나제 염기 편집기를 사용하여 질환-관련 유전자를 편집하는 방법 Download PDF

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KR20210127206A
KR20210127206A KR1020217029268A KR20217029268A KR20210127206A KR 20210127206 A KR20210127206 A KR 20210127206A KR 1020217029268 A KR1020217029268 A KR 1020217029268A KR 20217029268 A KR20217029268 A KR 20217029268A KR 20210127206 A KR20210127206 A KR 20210127206A
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South Korea
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base editor
gene
adenosine
disease
nucleic acid
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KR1020217029268A
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Korean (ko)
Inventor
이안 슬레이메이커
니콜 가우델리
이 유
베른트 제츠체
데이비드 에이. 본
승주 이
마이클 페커
제이슨 마이클 게르케
나탈리 페트로시안
엔젤리카 메사나
샤우나 베르코비치
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빔 테라퓨틱스, 인크.
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KR1020217029268A 2019-02-13 2020-02-13 유전성 질환의 치료를 위한 것을 포함하는, 아데노신 데아미나제 염기 편집기를 사용하여 질환-관련 유전자를 편집하는 방법 Pending KR20210127206A (ko)

Applications Claiming Priority (19)

Application Number Priority Date Filing Date Title
US201962805271P 2019-02-13 2019-02-13
US62/805,271 2019-02-13
US201962850919P 2019-05-21 2019-05-21
US62/850,919 2019-05-21
US201962852224P 2019-05-23 2019-05-23
US201962852228P 2019-05-23 2019-05-23
US62/852,228 2019-05-23
US62/852,224 2019-05-23
US201962873138P 2019-07-11 2019-07-11
US62/873,138 2019-07-11
US201962888867P 2019-08-19 2019-08-19
US62/888,867 2019-08-19
US201962931722P 2019-11-06 2019-11-06
US62/931,722 2019-11-06
US201962941569P 2019-11-27 2019-11-27
US62/941,569 2019-11-27
US202062966526P 2020-01-27 2020-01-27
US62/966,526 2020-01-27
PCT/US2020/018073 WO2020168051A1 (en) 2019-02-13 2020-02-13 Methods of editing a disease-associated gene using adenosine deaminase base editors, including for the treatment of genetic disease

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KR20210127206A true KR20210127206A (ko) 2021-10-21

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KR1020217029268A Pending KR20210127206A (ko) 2019-02-13 2020-02-13 유전성 질환의 치료를 위한 것을 포함하는, 아데노신 데아미나제 염기 편집기를 사용하여 질환-관련 유전자를 편집하는 방법

Country Status (8)

Country Link
US (1) US20230140953A1 (https=)
EP (1) EP3924484A4 (https=)
JP (2) JP7586601B2 (https=)
KR (1) KR20210127206A (https=)
CN (2) CN119280261A (https=)
AU (1) AU2020223306A1 (https=)
CA (1) CA3128876A1 (https=)
WO (1) WO2020168051A1 (https=)

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