KR20200116933A - 인간 심근세포에서 디스트로핀 돌연변이를 교정하기 위한 조성물 및 방법 - Google Patents

인간 심근세포에서 디스트로핀 돌연변이를 교정하기 위한 조성물 및 방법 Download PDF

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KR20200116933A
KR20200116933A KR1020207022943A KR20207022943A KR20200116933A KR 20200116933 A KR20200116933 A KR 20200116933A KR 1020207022943 A KR1020207022943 A KR 1020207022943A KR 20207022943 A KR20207022943 A KR 20207022943A KR 20200116933 A KR20200116933 A KR 20200116933A
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에릭 엔. 올슨
쳉주 롱
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더 보드 오브 리젠츠 오브 더 유니버시티 오브 텍사스 시스템
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KR1020207022943A 2018-01-31 2019-01-31 인간 심근세포에서 디스트로핀 돌연변이를 교정하기 위한 조성물 및 방법 Ceased KR20200116933A (ko)

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US201862624748P 2018-01-31 2018-01-31
US62/624,748 2018-01-31
PCT/US2019/015988 WO2019152609A1 (en) 2018-01-31 2019-01-31 Compositions and methods for correcting dystrophin mutations in human cardiomyocytes

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US (1) US20200370042A1 (https=)
EP (1) EP3746557A1 (https=)
JP (1) JP2021511803A (https=)
KR (1) KR20200116933A (https=)
CN (1) CN111836893A (https=)
AU (1) AU2019216321A1 (https=)
BR (1) BR112020015617A2 (https=)
CA (1) CA3088547A1 (https=)
EA (1) EA202091828A1 (https=)
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