JPWO2022240778A5 - - Google Patents
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- Publication number
- JPWO2022240778A5 JPWO2022240778A5 JP2023569975A JP2023569975A JPWO2022240778A5 JP WO2022240778 A5 JPWO2022240778 A5 JP WO2022240778A5 JP 2023569975 A JP2023569975 A JP 2023569975A JP 2023569975 A JP2023569975 A JP 2023569975A JP WO2022240778 A5 JPWO2022240778 A5 JP WO2022240778A5
- Authority
- JP
- Japan
- Prior art keywords
- construct
- cells
- polynucleotide
- viral vector
- promoter
- Prior art date
- Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
- Pending
Links
Applications Claiming Priority (7)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| US202163188450P | 2021-05-13 | 2021-05-13 | |
| US63/188,450 | 2021-05-13 | ||
| US202163251025P | 2021-09-30 | 2021-09-30 | |
| US63/251,025 | 2021-09-30 | ||
| US202163277549P | 2021-11-09 | 2021-11-09 | |
| US63/277,549 | 2021-11-09 | ||
| PCT/US2022/028396 WO2022240778A1 (en) | 2021-05-13 | 2022-05-09 | Gene therapy delivery compositions and methods for treating hearing loss |
Publications (3)
| Publication Number | Publication Date |
|---|---|
| JP2024521052A JP2024521052A (ja) | 2024-05-28 |
| JPWO2022240778A5 true JPWO2022240778A5 (https=) | 2025-05-16 |
| JP2024521052A5 JP2024521052A5 (https=) | 2025-05-16 |
Family
ID=84028799
Family Applications (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2023569975A Pending JP2024521052A (ja) | 2021-05-13 | 2022-05-09 | 遺伝子治療送達組成物及び難聴を処置するための方法 |
Country Status (16)
| Country | Link |
|---|---|
| US (1) | US20250339560A1 (https=) |
| EP (1) | EP4337226A4 (https=) |
| JP (1) | JP2024521052A (https=) |
| KR (1) | KR20240021799A (https=) |
| AU (1) | AU2022271727A1 (https=) |
| CA (1) | CA3218877A1 (https=) |
| CL (1) | CL2023003364A1 (https=) |
| CO (1) | CO2023017148A2 (https=) |
| CR (1) | CR20230577A (https=) |
| DO (1) | DOP2023000248A (https=) |
| EC (1) | ECSP23093588A (https=) |
| IL (1) | IL308396A (https=) |
| JO (1) | JOP20230289A1 (https=) |
| MX (1) | MX2023013394A (https=) |
| PE (1) | PE20240240A1 (https=) |
| WO (1) | WO2022240778A1 (https=) |
Families Citing this family (4)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| MX2020006435A (es) | 2017-12-19 | 2021-02-09 | Akouos Inc | Administracion de anticuerpos terapeuticos mediada por vector de virus adenoasociado (aav) en el oido interno. |
| JP2023541443A (ja) * | 2020-09-14 | 2023-10-02 | プレジデント アンド フェローズ オブ ハーバード カレッジ | ＧＪＢ２をコードする組換えアデノ随伴ウイルス（ｒＡＡＶ）およびその使用。 |
| IL303317A (en) | 2020-12-01 | 2023-07-01 | Akouos Inc | ANTI-NATURAL ANTIBODY STRUCTURES AND RELATED METHODS FOR THE TREATMENT OF SYMPTOMS ASSOCIATED WITH VESTIBULAR SWANNOMA |
| KR20250175321A (ko) * | 2023-03-28 | 2025-12-16 | 센소리온 | 커넥신 26을 암호화하는 아데노-연관 바이러스 벡터 및 이의 용도 |
Family Cites Families (12)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| ATE360066T1 (de) * | 1997-08-05 | 2007-05-15 | Hoffmann La Roche | Aus einer menschlichen glial zelllinie- abgeleiteter promotor eines neurotrophischen faktors, diesen enthaltende vektoren und methoden zum screenen von verbindungen damit |
| AU2003241299A1 (en) * | 2002-04-19 | 2003-11-03 | Schering Aktiengesellschaft | Novel prostate tumor-specific promoter |
| PL2002003T3 (pl) * | 2005-05-27 | 2016-06-30 | Ospedale San Raffaele Srl | Wektor genetyczny zawierający mi-RNA |
| US20070161031A1 (en) * | 2005-12-16 | 2007-07-12 | The Board Of Trustees Of The Leland Stanford Junior University | Functional arrays for high throughput characterization of gene expression regulatory elements |
| US20150051267A1 (en) * | 2013-08-16 | 2015-02-19 | Purdue Research Foundation | BICISTRONIC GENE TRANSFER TOOLS FOR DELIVERY OF miRNAS AND PROTEIN CODING SEQUENCES |
| AU2016363830C1 (en) * | 2015-12-04 | 2022-03-24 | Centre National De La Recherche Scientifique | Promoters and uses thereof |
| AU2018344883B2 (en) * | 2017-10-02 | 2024-03-07 | Scientist Of Fortune S.A. | Cellular transport system for transferring a sulfonic acid construct carrying a cargo into the cytoplasm of a cell |
| US12054724B2 (en) * | 2018-04-10 | 2024-08-06 | President And Fellows Of Harvard College | AAV vectors encoding clarin-1 or GJB2 and uses thereof |
| CA3115810A1 (en) * | 2018-10-11 | 2020-04-16 | Decibel Therapeutics, Inc. | Aav1 vectors and uses thereof for treatment of otic indications |
| US20220396806A1 (en) * | 2019-07-26 | 2022-12-15 | Akouos, Inc. | Methods of treating hearing loss using a secreted target protein |
| CA3153133A1 (en) * | 2019-09-30 | 2021-04-08 | Chris Bartolome | Adeno-associated virus (aav) systems for treatment of genetic hearing loss |
| EP4164695A4 (en) * | 2020-05-13 | 2024-06-05 | Akouos, Inc. | COMPOSITIONS AND METHODS FOR TREATING GJB2-ASSOCIATED HEARING LOSS |
-
2022
- 2022-05-09 US US18/560,064 patent/US20250339560A1/en active Pending
- 2022-05-09 WO PCT/US2022/028396 patent/WO2022240778A1/en not_active Ceased
- 2022-05-09 KR KR1020237042840A patent/KR20240021799A/ko active Pending
- 2022-05-09 PE PE2023003052A patent/PE20240240A1/es unknown
- 2022-05-09 IL IL308396A patent/IL308396A/en unknown
- 2022-05-09 JP JP2023569975A patent/JP2024521052A/ja active Pending
- 2022-05-09 MX MX2023013394A patent/MX2023013394A/es unknown
- 2022-05-09 AU AU2022271727A patent/AU2022271727A1/en not_active Abandoned
- 2022-05-09 CA CA3218877A patent/CA3218877A1/en active Pending
- 2022-05-09 EP EP22808141.0A patent/EP4337226A4/en active Pending
- 2022-05-09 CR CR20230577A patent/CR20230577A/es unknown
-
2023
- 2023-11-10 CL CL2023003364A patent/CL2023003364A1/es unknown
- 2023-11-10 DO DO2023000248A patent/DOP2023000248A/es unknown
- 2023-11-12 JO JOJO/P/2023/0289A patent/JOP20230289A1/ar unknown
- 2023-12-11 CO CONC2023/0017148A patent/CO2023017148A2/es unknown
- 2023-12-13 EC ECSENADI202393588A patent/ECSP23093588A/es unknown
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