JPWO2022040447A5 - - Google Patents

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Publication number
JPWO2022040447A5
JPWO2022040447A5 JP2023512428A JP2023512428A JPWO2022040447A5 JP WO2022040447 A5 JPWO2022040447 A5 JP WO2022040447A5 JP 2023512428 A JP2023512428 A JP 2023512428A JP 2023512428 A JP2023512428 A JP 2023512428A JP WO2022040447 A5 JPWO2022040447 A5 JP WO2022040447A5
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JP
Japan
Prior art keywords
gsi
pharmaceutical product
semagacestat
human patient
mucus
Prior art date
Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
Pending
Application number
JP2023512428A
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English (en)
Japanese (ja)
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JP2023538125A (ja
JP2023538125A5 (https=
Publication date
Application filed filed Critical
Priority claimed from PCT/US2021/046742 external-priority patent/WO2022040447A2/en
Publication of JP2023538125A publication Critical patent/JP2023538125A/ja
Publication of JPWO2022040447A5 publication Critical patent/JPWO2022040447A5/ja
Publication of JP2023538125A5 publication Critical patent/JP2023538125A5/ja
Pending legal-status Critical Current

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JP2023512428A 2020-08-20 2021-08-19 粘液過剰分泌を特徴とする呼吸器疾患を処置するための方法 Pending JP2023538125A (ja)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US202063068235P 2020-08-20 2020-08-20
US63/068,235 2020-08-20
PCT/US2021/046742 WO2022040447A2 (en) 2020-08-20 2021-08-19 Methods for treating respiratory diseases characterized by mucus hypersecretion

Publications (3)

Publication Number Publication Date
JP2023538125A JP2023538125A (ja) 2023-09-06
JPWO2022040447A5 true JPWO2022040447A5 (https=) 2024-08-20
JP2023538125A5 JP2023538125A5 (https=) 2024-08-20

Family

ID=80323184

Family Applications (1)

Application Number Title Priority Date Filing Date
JP2023512428A Pending JP2023538125A (ja) 2020-08-20 2021-08-19 粘液過剰分泌を特徴とする呼吸器疾患を処置するための方法

Country Status (11)

Country Link
US (1) US20230277550A1 (https=)
EP (1) EP4199914A4 (https=)
JP (1) JP2023538125A (https=)
KR (1) KR20230052954A (https=)
CN (1) CN116033895A (https=)
AU (1) AU2021329507A1 (https=)
BR (1) BR112023002651A2 (https=)
CA (1) CA3188234A1 (https=)
IL (1) IL300405A (https=)
MX (1) MX2023001993A (https=)
WO (1) WO2022040447A2 (https=)

Families Citing this family (2)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
EP4268824A1 (en) * 2022-04-26 2023-11-01 Manros Therapeutics Imidazo[2,1-f][1,2,4]triazine derivatives useful as a medicament
WO2024112356A1 (en) * 2022-11-23 2024-05-30 The Board Of Trustees Of The Leland Stanford Junior University Methods for treating respiratory diseases characterized by mucus hypersecretion

Family Cites Families (26)

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Publication number Priority date Publication date Assignee Title
US7468365B2 (en) 2000-11-17 2008-12-23 Eli Lilly And Company Lactam compound
SE0101004D0 (sv) 2001-03-21 2001-03-21 Astrazeneca Ab New measuring technique
RS56037B1 (sr) 2004-06-24 2017-09-29 Vertex Pharma Modulatori atp-vezujućih kasetnih transportera
EP3219705B1 (en) 2005-12-28 2020-03-11 Vertex Pharmaceuticals Incorporated Pharmaceutical compositions of the amorphous form of n-[2,4-bis(1,1-dimethylethyl)-5-hydroxyphenyl]-1,4-dihydro-4-oxoquinoline-3-carboxamide
CA2644136A1 (en) * 2006-02-27 2007-09-07 The Johns Hopkins University Cancer treatment with gamma-secretase inhibitors
US7645789B2 (en) 2006-04-07 2010-01-12 Vertex Pharmaceuticals Incorporated Indole derivatives as CFTR modulators
EP2674428B1 (en) 2006-04-07 2016-04-06 Vertex Pharmaceuticals Incorporated Modulators of ATP-binding cassette transporters
EP3683218B1 (en) 2007-12-07 2024-09-18 Vertex Pharmaceuticals Incorporated Solid forms of 3-(6-(1-(2,2-difluorobenzo[d][1,3]dioxol-5-yl) cyclopropanecarboxamido)-3-methylpyridin-2-yl) benzoic acid
US8299059B2 (en) 2009-10-30 2012-10-30 Eli Lilly And Company Crystalline compound and a process for its preparation
PT3030568T (pt) 2013-08-08 2018-12-24 Galapagos Nv Tieno[2,3-c]piranos como moduladores de cftr
EP2932966A1 (en) 2014-04-16 2015-10-21 Novartis AG Gamma secretase inhibitors for treating respiratory diseases
MA41051B1 (fr) 2014-10-06 2020-11-30 Vertex Pharma Modulateurs du régulateur de conductance transmembranaire de la mucoviscidose
US10392378B2 (en) 2014-12-23 2019-08-27 Proteostasis Therapeutics, Inc. Derivatives of 5-phenyl- or 5-heteroarylathiazol-2-carboxylic amide useful for the treatment of inter alia cystic fibrosis
US10548878B2 (en) 2015-07-24 2020-02-04 Proteostasis Therapeutics, Inc. Compounds, compositions, and methods of increasing CFTR activity
BR112018007021B1 (pt) 2015-10-06 2024-01-09 Proteostasis Therapeutics, Inc Composto, composição compreendendo os ditos compostos e uso dos mesmos para tratar fibrose cística
US9890149B2 (en) 2015-10-07 2018-02-13 NuBridge BioSciences Isothiazole derivatives as CFTR modulators
BR112018007161B1 (pt) 2015-10-09 2024-01-16 Galapagos Nv COMPOSTOS PIRAZOLO[3,4-b]PIRIDIN-6-CARBOXAMIDA N-SULFONILADA, COMPOSIÇÃO FARMACÊUTICA CONTENDO OS DITOS COMPOSTOS E USOS DOS MESMOS PARA TRATAR FIBROSE CÍSTICA
AU2017256172A1 (en) 2016-04-26 2018-09-06 AbbVie S.à.r.l. Modulators of cystic fibrosis transmembrane conductance regulator protein
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TW201811766A (zh) 2016-08-29 2018-04-01 瑞士商諾華公司 N-(吡啶-2-基)吡啶-磺醯胺衍生物及其用於疾病治療之用途
US10399940B2 (en) 2016-10-07 2019-09-03 Abbvie S.Á.R.L. Substituted pyrrolidines and methods of use
MX387203B (es) 2016-11-18 2025-03-18 Cystic Fibrosis Found Pirrolopirimidinas como potenciadores de cftr.
SG10201911076QA (en) 2016-12-16 2020-01-30 Cystic Fibrosis Found Bycyclic heteroaryl derivatives as cftr potentiators
IL268349B2 (en) * 2017-02-17 2024-08-01 Hutchinson Fred Cancer Res Combination therapies for treatment of bcma-related cancers and autoimmune disorders
TW201831471A (zh) 2017-02-24 2018-09-01 盧森堡商艾伯維公司 囊腫纖化症跨膜傳導調節蛋白的調節劑及其使用方法
KR20250030524A (ko) 2019-08-09 2025-03-05 화이자 인코포레이티드 (s)-2-(((s)-6,8-디플루오로-1,2,3,4-테트라하이드로나프탈렌-2-일)아미노)-n-(1-(2-메틸-1-(네오펜틸아미노)프로판-2-일)-1h-이미다졸-4-일)펜탄아미드의고체 상태 형태 및 이의 용도

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